EAP_GS010_single Patient

A Single Intravitreal Injection of rAAV2-ND4 for the Treatment of Leber's Hereditary Optic Neuropathy

NCT03153293 ·Status: UNKNOWN ·Phase: PHASE2/PHASE3

Gene Therapy Clinical Trial for the Treatment of Leber's Hereditary Optic Neuropathy Associated With ND4 Mutations

NCT05293626 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE1/PHASE2

Study of Efficacy and Safety of Voretigene Neparvovec in Japanese Patients With Biallelic RPE65 Mutation-associated Retinal Dystrophy

NCT04516369 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE3

Dose-escalation Study to Evaluate the Safety and Tolerability of GS030 in Subjects With Retinitis Pigmentosa

NCT03326336 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE1/PHASE2

Long-term Follow-up Study in Subjects Who Received Voretigene Neparvovec-rzyl (AAV2-hRPE65v2)

NCT03602820 ·Status: ACTIVE_NOT_RECRUITING

Safety Study in Subjects With Leber Congenital Amaurosis

NCT00516477 ·Status: COMPLETED ·Phase: PHASE1

Study of NGM621 in Participants With Geographic Atrophy

NCT04014777 ·Status: COMPLETED ·Phase: PHASE1

A Study of NGM621 in Participants With Geographic Atrophy

NCT04465955 ·Status: COMPLETED ·Phase: PHASE2

Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis

NCT00999609 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE3

Safety and Effects of a Single Intravitreal Injection of vMCO-010 Optogenetic Therapy in Subjects With Stargardt Disease

NCT05417126 ·Status: COMPLETED ·Phase: PHASE2

A Long-term Extension Study of JNJ-81201887 (AAVCAGsCD59) Parent Studies in Participants With Geographic Atrophy (GA) Secondary to Age-related Macular Degeneration (AMD)

NCT06635148 ·Status: RECRUITING ·Phase: PHASE2

Phase I/II Study of SKG0106 Intravitreal Injection in Patients With Neovascular Age-related Macular Degeneration (nAMD)

NCT05986864 ·Status: RECRUITING ·Phase: PHASE1/PHASE2

UGX202 Injection in Patients With Advanced Retinitis Pigmentosa

NCT07311863 ·Status: NOT_YET_RECRUITING ·Phase: EARLY_PHASE1

Gene Therapy Clinical Trial for the Treatment Of Leber's HereDitary Optic Neuropathy

NCT04912843 ·Status: RECRUITING ·Phase: PHASE2/PHASE3

Study to Evaluate the Efficacy and Safety of VGR-R01 Gene Therapy in Patients With Bietti Crystalline Dystrophy

NCT06699108 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE3

Safety and Efficacy Study in Patients With Retinitis Pigmentosa Due to Mutations in PDE6B Gene

NCT03328130 ·Status: TERMINATED ·Phase: PHASE1/PHASE2

A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US

NCT03597399 ·Status: COMPLETED

A Study of Encapsulated Cell Technology (ECT) Implant for Participants With Early Stage Retinitis Pigmentosa

NCT00447980 ·Status: COMPLETED ·Phase: PHASE2

Study of SAR421869 in Participants With Retinitis Pigmentosa Associated With Usher Syndrome Type 1B

NCT01505062 ·Status: TERMINATED ·Phase: PHASE1/PHASE2

Efficacy and Safety of MCO-010 Optogenetic Therapy in Adults With Retinitis Pigmentosa [RESTORE]

NCT04945772 ·Status: COMPLETED ·Phase: PHASE2

Safety And Tolerability Study Of RN6G In Subjects With Advanced Dry, Age-Related Macular Degeneration Including Geographic Atrophy

NCT01003691 ·Status: COMPLETED ·Phase: PHASE1

Safety and Efficacy Trial of AAV Gene Therapy in Patients With CNGB3 Achromatopsia (A Clarity Clinical Trial)

NCT02599922 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE1/PHASE2

Gene Therapy for Gyrate Atrophy

NCT00001735 ·Status: COMPLETED ·Phase: PHASE1

A Safety and Efficacy Study of a One-time Intravitreal Injection of SAR446597 in Participants With Geographic Atrophy Secondary to Age-related Macular Degeneration

NCT07215234 ·Status: RECRUITING ·Phase: PHASE1/PHASE2

Safety and Tolerability of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations

NCT06196827 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE1