Trial Outcomes & Findings for Study Evaluating Subjects With Distal Renal Tubular Acidosis (NCT NCT03644706)

NCT ID: NCT03644706

Last Updated: 2026-06-03

Results Overview

Blood bicarbonate levels were measured at the begininning (day 1) and end (day 6) of the withdrawal period, and change in blood bicarbonate levels was calculated as value at day 6 minus value at day 1

Recruitment status

TERMINATED

Study phase

PHASE3

Target enrollment

3 participants

Primary outcome timeframe

day 1, day 6

Results posted on

2026-06-03

Participant Flow

Patients were recruited by the study site teams.

Study was terminated due to Covid-19

Participant milestones

Participant milestones
Measure
Enrolled to Study
Enrolled, tested and established on ADV7103 in the open label titration and stabilization phase
Randomized to ADV7103
Patients continue to receive ADV7103 twice a day at their open label dose over 6 days
Randomized to Placebo
Patients receive matched placebo twice a day until they reach a bicarbonate level of 18mEq/L
Titration
STARTED
3
0
0
Titration
COMPLETED
3
0
0
Titration
NOT COMPLETED
0
0
0
Randomization/Withdrawal
STARTED
0
1
0
Randomization/Withdrawal
COMPLETED
0
1
0
Randomization/Withdrawal
NOT COMPLETED
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Study Evaluating Subjects With Distal Renal Tubular Acidosis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
All Participants
n=3 Participants
Baseline data collected at enrollment
Age, Categorical
<=18 years
1 Participants
n=20 Participants
Age, Categorical
Between 18 and 65 years
2 Participants
n=20 Participants
Age, Categorical
>=65 years
0 Participants
n=20 Participants
Sex: Female, Male
Female
2 Participants
n=20 Participants
Sex: Female, Male
Male
1 Participants
n=20 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=20 Participants
Race (NIH/OMB)
Asian
0 Participants
n=20 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=20 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=20 Participants
Race (NIH/OMB)
White
3 Participants
n=20 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=20 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=20 Participants

PRIMARY outcome

Timeframe: day 1, day 6

Population: 3 patients entered the study. Only 1 patient entered period 2 - withdrawal. The small sample size and premature termination of the study limited the assessment of efficacy of ADV7103 versus placebo.

Blood bicarbonate levels were measured at the begininning (day 1) and end (day 6) of the withdrawal period, and change in blood bicarbonate levels was calculated as value at day 6 minus value at day 1

Outcome measures

Outcome measures
Measure
ADV7103
n=1 Participants
Patients continue to receive ADV7103 twice a day at their open label dose over 6 days
Placebo Comparator
Patients receive matched placebo twice a day until they reach a bicarbonate level of 18mEq/L
Change in Blood Bicarbonate Levels During Withdrawal Period
27 mmol/l
Standard Deviation NA
SD not calculable for 1 participant

Adverse Events

ADV7103

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Placebo Comparator

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Dr Adrian Hepner, Acting CMO Advicenne S.A.

Advicenne Pharma

Phone: +1 949 874 1617

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place