Trial Outcomes & Findings for Atezolizumab in Combination With Carboplatin Plus Pemetrexed in Chemotherapy-naïve Patients With Asymptomatic Brain Metastasis (NCT NCT03526900)

NCT ID: NCT03526900

Last Updated: 2024-10-09

Results Overview

Percentage of subjects without disease progression (intracranial or systemic) at 12 weeks after enrollment. Determined by the investigator according to RANO and RECIST v1.1 criteria for brain and systemic disease respectively. Response Evaluation Criteria In Solid Tumors (RECIST v1.1) for target lesions and assessed by MRI:Complete Response(CR),Disappearance of all target lesions; Partial Response (PR) ≥30% decrease in the sum of the longest diameter of target lesions; Progressive disease (PD) ≥20% increase in the sum of diameters of target lesions. Reponse Evaluation criteria in brain metastasis (RANO) for target lesions assessed by MRI: Complete Response (CR) Disappearance of all CNS target lesions without use of corticosteroids, Partial response (PR) ≥30% decrease in the sum longest diameter of CNS target lesions;Progessive disease (PD) ≥20% increase in the sum longest diameter of CNS target lesions

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

40 participants

Primary outcome timeframe

12 weeks after enrollment

Results posted on

2024-10-09

Participant Flow

Screening details:Patients who are chemotherapy naïve and have Stage IV non-squamous NSCLC with untreated brain metastases will be enrolled in this study. Study enrollment was completed between November 2018 and December 2019.

Participant milestones

Participant milestones
Measure
Atezolizumab
Induction phase: atezolizumab will be given intravenously (iv) at a dose of 1200 mg for 60 minutes on day 1 of each cycle. Subsequent atezolizumab cycles may be administered for 30 minutes, if there were no perfusion-related toxicity. Pemetrexed will be administered at a dose of 500 mg/m2 IV for 15 minutes on day 1 of each cycle. In addition, folic acid, vitamin B12, and dexamethasone 4 mg will be given the day before and the day after treatment with pemetrexed. Carboplatin will be given at a dose with an area under the 5 curve for 30 minutes on day 1 of each cycle, approximately 30 minutes after the pemetrexed infusion is complete. After completing 4 to 6 cycles of Carboplatino plus pemetrexed and atezolizumab, patients will continue with pemetrexed in combination with atezolizumab (maintenance phase) until they have an unacceptable toxicity, progression of the disease, decision of the patient/physician or have Completed 2 years of treatment. Atezolizumab: - Induction (four or six 21-day cycles) : Atezolizumab 1200 mg / iv + carboplatin 5 AUCs + pemetrexed 500 mg/m2 -Maintenance (21-day cycles): atezolizumab 1200 mg/iv + pemetrexed 500 mg/m2.
Overall Study
STARTED
40
Overall Study
COMPLETED
40
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Atezolizumab in Combination With Carboplatin Plus Pemetrexed in Chemotherapy-naïve Patients With Asymptomatic Brain Metastasis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Atezolizumab
n=40 Participants
Induction phase: atezolizumab will be given intravenously (iv) at a dose of 1200 mg for 60 minutes on day 1 of each cycle. Subsequent atezolizumab cycles may be administered for 30 minutes, if there were no perfusion-related toxicity. Pemetrexed will be administered at a dose of 500 mg/m2 IV for 15 minutes on day 1 of each cycle. In addition, folic acid, vitamin B12, and dexamethasone 4 mg will be given the day before and the day after treatment with pemetrexed. Carboplatin will be given at a dose with an area under the 5 curve for 30 minutes on day 1 of each cycle, approximately 30 minutes after the pemetrexed infusion is complete. After completing 4 to 6 cycles of Carboplatino plus pemetrexed and atezolizumab, patients will continue with pemetrexed in combination with atezolizumab (maintenance phase) until they have an unacceptable toxicity, progression of the disease, decision of the patient/physician or have Completed 2 years of treatment. Atezolizumab: - Induction (four or six 21-day cycles) : Atezolizumab 1200 mg / iv + carboplatin 5 AUCs + pemetrexed 500 mg/m2 -Maintenance (21-day cycles): atezolizumab 1200 mg/iv + pemetrexed 500 mg/m2.
Age, Continuous
66.75 years
STANDARD_DEVIATION 14.2 • n=99 Participants
Sex: Female, Male
Female
11 Participants
n=99 Participants
Sex: Female, Male
Male
29 Participants
n=99 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
Race (NIH/OMB)
Asian
0 Participants
n=99 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=99 Participants
Race (NIH/OMB)
White
40 Participants
n=99 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
Region of Enrollment
Spain
40 participants
n=99 Participants
Performance Status
ECOG 0
14 participants
n=99 Participants
Performance Status
ECOG 1
26 participants
n=99 Participants
Performance Status
ECOG 2
0 participants
n=99 Participants
Performance Status
ECOG 3
0 participants
n=99 Participants
Performance Status
ECOG 4
0 participants
n=99 Participants
Cigarrette Smoking History
Never Smoke
6 Participants
n=99 Participants
Cigarrette Smoking History
Former Smoke
11 Participants
n=99 Participants
Cigarrette Smoking History
Smoker
23 Participants
n=99 Participants
Histology
Adenocarcinoma
39 Participants
n=99 Participants
Histology
Adenosquamous
0 Participants
n=99 Participants
Histology
Squamous
0 Participants
n=99 Participants
Histology
Large Cell Carcinoma
0 Participants
n=99 Participants
Histology
NOS/Undifferentiated
1 Participants
n=99 Participants
PD-L1 expression
≥ 50%
10 Participants
n=99 Participants
PD-L1 expression
1%-49 %
10 Participants
n=99 Participants
PD-L1 expression
0 %
18 Participants
n=99 Participants
PD-L1 expression
Unknown
2 Participants
n=99 Participants
Baseline corticosteroids
Yes
22 Participants
n=99 Participants
Baseline corticosteroids
No
18 Participants
n=99 Participants
Diagnosis of brain metastases
Synchronous
37 Participants
n=99 Participants
Diagnosis of brain metastases
Metachronous
3 Participants
n=99 Participants
Total number of brain lesions per patient
5 Number of lesions
n=99 Participants
Total number of target brain lesions per patient
1 Number of lesions
n=99 Participants

PRIMARY outcome

Timeframe: 12 weeks after enrollment

Population: Intention-to-treat population cohort of 40 patients

Percentage of subjects without disease progression (intracranial or systemic) at 12 weeks after enrollment. Determined by the investigator according to RANO and RECIST v1.1 criteria for brain and systemic disease respectively. Response Evaluation Criteria In Solid Tumors (RECIST v1.1) for target lesions and assessed by MRI:Complete Response(CR),Disappearance of all target lesions; Partial Response (PR) ≥30% decrease in the sum of the longest diameter of target lesions; Progressive disease (PD) ≥20% increase in the sum of diameters of target lesions. Reponse Evaluation criteria in brain metastasis (RANO) for target lesions assessed by MRI: Complete Response (CR) Disappearance of all CNS target lesions without use of corticosteroids, Partial response (PR) ≥30% decrease in the sum longest diameter of CNS target lesions;Progessive disease (PD) ≥20% increase in the sum longest diameter of CNS target lesions

Outcome measures

Outcome measures
Measure
Atezolizumab
n=40 Participants
Induction phase: atezolizumab will be given intravenously (iv) at a dose of 1200 mg for 60 minutes on day 1 of each cycle. Subsequent atezolizumab cycles may be administered for 30 minutes, if there were no perfusion-related toxicity. Pemetrexed will be administered at a dose of 500 mg/m2 IV for 15 minutes on day 1 of each cycle. In addition, folic acid, vitamin B12, and dexamethasone 4 mg will be given the day before and the day after treatment with pemetrexed. Carboplatin will be given at a dose with an area under the 5 curve for 30 minutes on day 1 of each cycle, approximately 30 minutes after the pemetrexed infusion is complete. After completing 4 to 6 cycles of Carboplatino plus pemetrexed and atezolizumab, patients will continue with pemetrexed in combination with atezolizumab (maintenance phase) until they have an unacceptable toxicity, progression of the disease, decision of the patient/physician or have Completed 2 years of treatment. Atezolizumab: - Induction (four or six 21-day cycles) : Atezolizumab 1200 mg / iv + carboplatin 5 AUCs + pemetrexed 500 mg/m2 -Maintenance (21-day cycles): atezolizumab 1200 mg/iv + pemetrexed 500 mg/m2.
Efficacy of Atezolizumab + CBDCA + Pemetrexed by Evaluating PFS Rate
62.2 percentage of participants
Interval 47.1 to 76.2

SECONDARY outcome

Timeframe: Two consecutive evaluations 6 weeks apart

Objective response defined as a complete response or partial response on two consecutive evaluations 6 weeks apart, as determined by the investigator according to RANO and RECIST v1.1 criteria for brain and systemic disease respectively. Response Evaluation Criteria In Solid Tumors (RECIST v1.1) for target lesions and assessed by MRI: Complete Response(CR), Disappearance of all target lesions; Partial Response (PR) ≥30% decrease in the sum of the longest diameter of target lesions; Progressive disease (PD) ≥20% increase in the sum of diameters of target lesions. Reponse Evaluation criteria in brain metastasis (RANO) for target lesions assessed by MRI: Complete Response (CR), Disappearance of all CNS target lesions without use of corticosteroids, Partial response (PR) ≥30% decrease in the sum longest diameter of CNS target lesions; Progessive disease (PD) ≥20% increase in the sum longest diameter of CNS target lesions or the appearance of new lesions

Outcome measures

Outcome measures
Measure
Atezolizumab
n=40 Participants
Induction phase: atezolizumab will be given intravenously (iv) at a dose of 1200 mg for 60 minutes on day 1 of each cycle. Subsequent atezolizumab cycles may be administered for 30 minutes, if there were no perfusion-related toxicity. Pemetrexed will be administered at a dose of 500 mg/m2 IV for 15 minutes on day 1 of each cycle. In addition, folic acid, vitamin B12, and dexamethasone 4 mg will be given the day before and the day after treatment with pemetrexed. Carboplatin will be given at a dose with an area under the 5 curve for 30 minutes on day 1 of each cycle, approximately 30 minutes after the pemetrexed infusion is complete. After completing 4 to 6 cycles of Carboplatino plus pemetrexed and atezolizumab, patients will continue with pemetrexed in combination with atezolizumab (maintenance phase) until they have an unacceptable toxicity, progression of the disease, decision of the patient/physician or have Completed 2 years of treatment. Atezolizumab: - Induction (four or six 21-day cycles) : Atezolizumab 1200 mg / iv + carboplatin 5 AUCs + pemetrexed 500 mg/m2 -Maintenance (21-day cycles): atezolizumab 1200 mg/iv + pemetrexed 500 mg/m2.
Efficacy of Atezolizumab + CBDCA + Pemetrexed by Measuring Objective Response.
18 Participants

OTHER_PRE_SPECIFIED outcome

Timeframe: From the date of randomization until the date of first documented progression or date of death from any cause, whichever came first, assessed up to 48 months.

Population: Intention to treat

To record the number of patients best response with steroid vs without steroid. Response Evaluation criteria in brain metastasis (RANO-BM) for target lesions and assessed by MRI: Complete Response (CR) Disappearance of all CNS target lesions, Partial response (PR) ≥30% decrease in the sum longest diameter of CNS target lesions; Overall Response (OR) = CR + PR. Progessive disease (PD) ≥20% increase in the sum longest diameter of CNS target lesions or a measurable increase in a non-target lesion, or the appearance of new lesions

Outcome measures

Outcome measures
Measure
Atezolizumab
n=38 Participants
Induction phase: atezolizumab will be given intravenously (iv) at a dose of 1200 mg for 60 minutes on day 1 of each cycle. Subsequent atezolizumab cycles may be administered for 30 minutes, if there were no perfusion-related toxicity. Pemetrexed will be administered at a dose of 500 mg/m2 IV for 15 minutes on day 1 of each cycle. In addition, folic acid, vitamin B12, and dexamethasone 4 mg will be given the day before and the day after treatment with pemetrexed. Carboplatin will be given at a dose with an area under the 5 curve for 30 minutes on day 1 of each cycle, approximately 30 minutes after the pemetrexed infusion is complete. After completing 4 to 6 cycles of Carboplatino plus pemetrexed and atezolizumab, patients will continue with pemetrexed in combination with atezolizumab (maintenance phase) until they have an unacceptable toxicity, progression of the disease, decision of the patient/physician or have Completed 2 years of treatment. Atezolizumab: - Induction (four or six 21-day cycles) : Atezolizumab 1200 mg / iv + carboplatin 5 AUCs + pemetrexed 500 mg/m2 -Maintenance (21-day cycles): atezolizumab 1200 mg/iv + pemetrexed 500 mg/m2.
Overall Response by RANO Criteria and Steroids
No steroids Stable disease or progression
11 Participants
Overall Response by RANO Criteria and Steroids
No steroids Complete response or partial response
7 Participants
Overall Response by RANO Criteria and Steroids
Yes steroids Stable disease or progression
10 Participants
Overall Response by RANO Criteria and Steroids
Yes steroids Complete response or partial
10 Participants

OTHER_PRE_SPECIFIED outcome

Timeframe: From date of randomization until the date of first needed salvage therapy, assessed up to 48 months.

Population: Per protocol population

Register the median time to needed brain radiotherapy (WBRT or SRS).

Outcome measures

Outcome measures
Measure
Atezolizumab
n=24 Participants
Induction phase: atezolizumab will be given intravenously (iv) at a dose of 1200 mg for 60 minutes on day 1 of each cycle. Subsequent atezolizumab cycles may be administered for 30 minutes, if there were no perfusion-related toxicity. Pemetrexed will be administered at a dose of 500 mg/m2 IV for 15 minutes on day 1 of each cycle. In addition, folic acid, vitamin B12, and dexamethasone 4 mg will be given the day before and the day after treatment with pemetrexed. Carboplatin will be given at a dose with an area under the 5 curve for 30 minutes on day 1 of each cycle, approximately 30 minutes after the pemetrexed infusion is complete. After completing 4 to 6 cycles of Carboplatino plus pemetrexed and atezolizumab, patients will continue with pemetrexed in combination with atezolizumab (maintenance phase) until they have an unacceptable toxicity, progression of the disease, decision of the patient/physician or have Completed 2 years of treatment. Atezolizumab: - Induction (four or six 21-day cycles) : Atezolizumab 1200 mg / iv + carboplatin 5 AUCs + pemetrexed 500 mg/m2 -Maintenance (21-day cycles): atezolizumab 1200 mg/iv + pemetrexed 500 mg/m2.
Median Time to Brain Radiotherapy (WBRT or SRS)
10.9 months
Interval 7.8 to 15.9

Adverse Events

Atezolizumab

Serious events: 7 serious events
Other events: 28 other events
Deaths: 1 deaths

Serious adverse events

Serious adverse events
Measure
Atezolizumab
n=40 participants at risk
Induction phase: atezolizumab will be given intravenously (iv) at a dose of 1200 mg for 60 minutes on day 1 of each cycle. Subsequent atezolizumab cycles may be administered for 30 minutes, if there were no perfusion-related toxicity. Pemetrexed will be administered at a dose of 500 mg/m2 IV for 15 minutes on day 1 of each cycle. In addition, folic acid, vitamin B12, and dexamethasone 4 mg will be given the day before and the day after treatment with pemetrexed. Carboplatin will be given at a dose with an area under the 5 curve for 30 minutes on day 1 of each cycle, approximately 30 minutes after the pemetrexed infusion is complete. After completing 4 to 6 cycles of Carboplatino plus pemetrexed and atezolizumab, patients will continue with pemetrexed in combination with atezolizumab (maintenance phase) until they have an unacceptable toxicity, progression of the disease, decision of the patient/physician or have Completed 2 years of treatment. Atezolizumab: - Induction (four or six 21-day cycles) : Atezolizumab 1200 mg / iv + carboplatin 5 AUCs + pemetrexed 500 mg/m2 -Maintenance (21-day cycles): atezolizumab 1200 mg/iv + pemetrexed 500 mg/m2.
Renal and urinary disorders
Nephritis
2.5%
1/40 • Number of events 1 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Respiratory, thoracic and mediastinal disorders
Pneumonitis
5.0%
2/40 • Number of events 2 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Renal and urinary disorders
Acute kidney injury
5.0%
2/40 • Number of events 2 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Vascular disorders
Pulmonary embolism
2.5%
1/40 • Number of events 1 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Blood and lymphatic system disorders
Febrile neutropenia
2.5%
1/40 • Number of events 1 • 48 months
The severity of AE will be determined using CTCAE version 4.03

Other adverse events

Other adverse events
Measure
Atezolizumab
n=40 participants at risk
Induction phase: atezolizumab will be given intravenously (iv) at a dose of 1200 mg for 60 minutes on day 1 of each cycle. Subsequent atezolizumab cycles may be administered for 30 minutes, if there were no perfusion-related toxicity. Pemetrexed will be administered at a dose of 500 mg/m2 IV for 15 minutes on day 1 of each cycle. In addition, folic acid, vitamin B12, and dexamethasone 4 mg will be given the day before and the day after treatment with pemetrexed. Carboplatin will be given at a dose with an area under the 5 curve for 30 minutes on day 1 of each cycle, approximately 30 minutes after the pemetrexed infusion is complete. After completing 4 to 6 cycles of Carboplatino plus pemetrexed and atezolizumab, patients will continue with pemetrexed in combination with atezolizumab (maintenance phase) until they have an unacceptable toxicity, progression of the disease, decision of the patient/physician or have Completed 2 years of treatment. Atezolizumab: - Induction (four or six 21-day cycles) : Atezolizumab 1200 mg / iv + carboplatin 5 AUCs + pemetrexed 500 mg/m2 -Maintenance (21-day cycles): atezolizumab 1200 mg/iv + pemetrexed 500 mg/m2.
General disorders
Anemia
20.0%
8/40 • Number of events 8 • 48 months
The severity of AE will be determined using CTCAE version 4.03
General disorders
Fatigue
37.5%
15/40 • Number of events 15 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Gastrointestinal disorders
Diarrhea
10.0%
4/40 • Number of events 4 • 48 months
The severity of AE will be determined using CTCAE version 4.03
General disorders
Anorexia
10.0%
4/40 • Number of events 4 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Blood and lymphatic system disorders
Platelet count decreased
7.5%
3/40 • Number of events 3 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Hepatobiliary disorders
Alanine aminotransferase increased
5.0%
2/40 • Number of events 2 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Blood and lymphatic system disorders
Neutrophil count decreased
5.0%
2/40 • Number of events 2 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Respiratory, thoracic and mediastinal disorders
Upper respiratory infection
5.0%
2/40 • Number of events 2 • 48 months
The severity of AE will be determined using CTCAE version 4.03
Hepatobiliary disorders
Lipase increased
5.0%
2/40 • Number of events 2 • 48 months
The severity of AE will be determined using CTCAE version 4.03

Additional Information

Eva Pereira

Fundación GECP

Phone: +34934302006

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place