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Lifetime Impact of Achondroplasia Study in Europe-LIAISE

NCT03449368 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 196

Last updated 2021-04-05

No results posted yet for this study

Summary

Observational study looking at the burden of illness in achondroplasia subjects aged 5-70. The study will include a 5 year review of historical clinical data as well as a single point collection of questionnaire data to look at the impact on the following in individuals with achondroplasia versus a normative population:

* Quality of life
* Clinical burden
* Healthcare resource use
* Socio-economic burden
* Psychosocial burden

Up to 300 subjects will be included in sites in Germany, Spain, Italy, Sweden, Austria and Denmark

Conditions

Sponsors & Collaborators

Principal Investigators

  • Medical Director · BioMarin Pharmaceutical

Eligibility

Min Age
5 Years
Max Age
70 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2017-12-17
Primary Completion
2020-04-29
Completion
2020-04-29

Countries

  • Austria
  • Denmark
  • Germany
  • Italy
  • Spain
  • Sweden

Study Locations

More Related Trials

Entities

Diseases
Companies

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT03449368 on ClinicalTrials.gov