Trial Outcomes & Findings for A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) (NCT NCT03439670)

NCT ID: NCT03439670

Last Updated: 2023-03-09

Results Overview

Vamorolone at 6.0mg/kg/day vs. placebo group in change from baseline to the Week 24 assessment

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

121 participants

Primary outcome timeframe

24 weeks

Results posted on

2023-03-09

Participant Flow

Participant milestones

Participant milestones
Measure
Treatment Group 1
Patients enrolled in Treatment Group 1 (experimental group) will receive vamorolone 2.0 mg/kg/day for 24 weeks followed by vamorolone 2.0mg/kg/day for 20 weeks.
Treatment Group 2
Patients enrolled in Treatment Group 2 (experimental group) will receive vamorolone 6.0 mg/kg/day for 24 weeks followed by vamorolone 6.0mg/kg/day for 20 weeks.
Treatment Group 3
Patients enrolled in Treatment Group 3 (active comparator group) will receive prednisone 0.75 mg/kg/day for 24 weeks followed by vamorolone 2.0mg/kg/day for 20 weeks.
Treatment Group 4
Patients enrolled in Treatment Group 4 (active comparator group) will receive prednisone 0.75 mg/kg/day for 24 weeks followed by vamorolone 6.0mg/kg/day for 20 weeks.
Treatment Group 5
Patients enrolled in Treatment Group 5 will receive placebo for 24 weeks followed by vamorolone 2mg/kg/day for 20 weeks.
Treatment Group 6
Patients enrolled in Treatment Group 6 will receive placebo for 24 weeks followed by vamorolone 6mg/kg/day for 20 weeks.
Overall Study
STARTED
30
30
15
16
15
15
Overall Study
COMPLETED
28
26
15
15
14
14
Overall Study
NOT COMPLETED
2
4
0
1
1
1

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Treatment Group 1
n=28 Participants
Patients enrolled in Treatment Group 1 (experimental group) will receive vamorolone 2.0 mg/kg/day for 24 weeks followed by vamorolone 2.0mg/kg/day for 20 weeks.
Treatment Group 2
n=28 Participants
Patients enrolled in Treatment Group 2 (experimental group) will receive vamorolone 6.0 mg/kg/day for 24 weeks followed by vamorolone 6.0mg/kg/day for 20 weeks.
Treatment Group 3
n=15 Participants
Patients enrolled in Treatment Group 3 (active comparator group) will receive prednisone 0.75 mg/kg/day for 24 weeks followed by vamorolone 2.0mg/kg/day for 20 weeks.
Treatment Group 4
n=15 Participants
Patients enrolled in Treatment Group 4 (active comparator group) will receive prednisone 0.75 mg/kg/day for 24 weeks followed by vamorolone 6.0mg/kg/day for 20 weeks.
Treatment Group 5
n=14 Participants
Patients enrolled in Treatment Group 5 will receive placebo for 24 weeks followed by vamorolone 2mg/kg/day for 20 weeks.
Treatment Group 6
n=14 Participants
Patients enrolled in Treatment Group 6 will receive placebo for 24 weeks followed by vamorolone 6mg/kg/day for 20 weeks.
Total
n=114 Participants
Total of all reporting groups
Age, Categorical
<=18 years
28 Participants
n=99 Participants
28 Participants
n=107 Participants
15 Participants
n=206 Participants
15 Participants
n=7 Participants
14 Participants
n=31 Participants
14 Participants
n=30 Participants
114 Participants
n=3 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
0 Participants
n=31 Participants
0 Participants
n=30 Participants
0 Participants
n=3 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
0 Participants
n=31 Participants
0 Participants
n=30 Participants
0 Participants
n=3 Participants
Sex: Female, Male
Female
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
0 Participants
n=31 Participants
0 Participants
n=30 Participants
0 Participants
n=3 Participants
Sex: Female, Male
Male
28 Participants
n=99 Participants
28 Participants
n=107 Participants
15 Participants
n=206 Participants
15 Participants
n=7 Participants
14 Participants
n=31 Participants
14 Participants
n=30 Participants
114 Participants
n=3 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
1 Participants
n=7 Participants
0 Participants
n=31 Participants
0 Participants
n=30 Participants
1 Participants
n=3 Participants
Race (NIH/OMB)
Asian
4 Participants
n=99 Participants
3 Participants
n=107 Participants
2 Participants
n=206 Participants
1 Participants
n=7 Participants
1 Participants
n=31 Participants
1 Participants
n=30 Participants
12 Participants
n=3 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
0 Participants
n=31 Participants
0 Participants
n=30 Participants
0 Participants
n=3 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=99 Participants
1 Participants
n=107 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
0 Participants
n=31 Participants
0 Participants
n=30 Participants
2 Participants
n=3 Participants
Race (NIH/OMB)
White
23 Participants
n=99 Participants
23 Participants
n=107 Participants
12 Participants
n=206 Participants
12 Participants
n=7 Participants
11 Participants
n=31 Participants
13 Participants
n=30 Participants
94 Participants
n=3 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
1 Participants
n=107 Participants
1 Participants
n=206 Participants
1 Participants
n=7 Participants
1 Participants
n=31 Participants
0 Participants
n=30 Participants
4 Participants
n=3 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
0 Participants
n=7 Participants
1 Participants
n=31 Participants
0 Participants
n=30 Participants
1 Participants
n=3 Participants
TTSTAND (seconds)
6.01 Seconds
STANDARD_DEVIATION 2.406 • n=99 Participants
5.97 Seconds
STANDARD_DEVIATION 1.991 • n=107 Participants
5.36 Seconds
STANDARD_DEVIATION 1.948 • n=206 Participants
4.53 Seconds
STANDARD_DEVIATION 0.808 • n=7 Participants
5.51 Seconds
STANDARD_DEVIATION 1.578 • n=31 Participants
5.58 Seconds
STANDARD_DEVIATION 2.288 • n=30 Participants
5.560 Seconds
STANDARD_DEVIATION 1.9498 • n=3 Participants

PRIMARY outcome

Timeframe: 24 weeks

Population: Per the protocol, the primary clinical efficacy endpoint was "comparison of the vamorolone 6.0 mg/kg/day dose level group versus the placebo group in change from baseline to the Week 24 assessment."

Vamorolone at 6.0mg/kg/day vs. placebo group in change from baseline to the Week 24 assessment

Outcome measures

Outcome measures
Measure
Treatment Group 1
n=28 Participants
Patients enrolled in Treatment Group 1 (placebo comparator group) will receive placebo for 24 weeks.
Treatment Group 2
n=27 Participants
Patients enrolled in Treatment Group 2 (experimental group) will receive vamorolone 6.0 mg/kg/day for 24 weeks
Efficacy Measured by Time to Stand Test (TTSTAND) Velocity in Rises/Second Change From Baseline
-.007 Rises/Seconds
Standard Deviation 0.0628
0.054 Rises/Seconds
Standard Deviation 0.0666

Adverse Events

Treatment Group 1

Serious events: 1 serious events
Other events: 26 other events
Deaths: 0 deaths

Treatment Group 2

Serious events: 2 serious events
Other events: 26 other events
Deaths: 0 deaths

Treatment Group 3

Serious events: 0 serious events
Other events: 15 other events
Deaths: 0 deaths

Treatment Group 4

Serious events: 0 serious events
Other events: 13 other events
Deaths: 0 deaths

Treatment Group 5

Serious events: 0 serious events
Other events: 12 other events
Deaths: 0 deaths

Treatment Group 6

Serious events: 0 serious events
Other events: 14 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Treatment Group 1
n=28 participants at risk
Patients enrolled in Treatment Group 1 (experimental group) will receive vamorolone 2.0 mg/kg/day for 24 weeks followed by vamorolone 2.0mg/kg/day for 20 weeks.
Treatment Group 2
n=28 participants at risk
Patients enrolled in Treatment Group 2 (experimental group) will receive vamorolone 6.0 mg/kg/day for 24 weeks followed by vamorolone 6.0mg/kg/day for 20 weeks.
Treatment Group 3
n=15 participants at risk
Patients enrolled in Treatment Group 3 (active comparator group) will receive prednisone 0.75 mg/kg/day for 24 weeks followed by vamorolone 2.0mg/kg/day for 20 weeks
Treatment Group 4
n=15 participants at risk
Patients enrolled in Treatment Group 4 (active comparator group) will receive prednisone 0.75 mg/kg/day for 24 weeks followed by vamorolone 6.0mg/kg/day for 20 weeks.
Treatment Group 5
n=14 participants at risk
Patients enrolled in Treatment Group 5 will receive placebo for 24 weeks followed by vamorolone 2mg/kg/day for 20 weeks.
Treatment Group 6
n=14 participants at risk
Patients enrolled in Treatment Group 6 will receive placebo for 24 weeks followed by vamorolone 6mg/kg/day for 20 weeks.
Infections and infestations
Gastroenteritis viral/viral gasteroenteritis
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Appendicitis
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Respiratory, thoracic and mediastinal disorders
Asthma
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks

Other adverse events

Other adverse events
Measure
Treatment Group 1
n=28 participants at risk
Patients enrolled in Treatment Group 1 (experimental group) will receive vamorolone 2.0 mg/kg/day for 24 weeks followed by vamorolone 2.0mg/kg/day for 20 weeks.
Treatment Group 2
n=28 participants at risk
Patients enrolled in Treatment Group 2 (experimental group) will receive vamorolone 6.0 mg/kg/day for 24 weeks followed by vamorolone 6.0mg/kg/day for 20 weeks.
Treatment Group 3
n=15 participants at risk
Patients enrolled in Treatment Group 3 (active comparator group) will receive prednisone 0.75 mg/kg/day for 24 weeks followed by vamorolone 2.0mg/kg/day for 20 weeks
Treatment Group 4
n=15 participants at risk
Patients enrolled in Treatment Group 4 (active comparator group) will receive prednisone 0.75 mg/kg/day for 24 weeks followed by vamorolone 6.0mg/kg/day for 20 weeks.
Treatment Group 5
n=14 participants at risk
Patients enrolled in Treatment Group 5 will receive placebo for 24 weeks followed by vamorolone 2mg/kg/day for 20 weeks.
Treatment Group 6
n=14 participants at risk
Patients enrolled in Treatment Group 6 will receive placebo for 24 weeks followed by vamorolone 6mg/kg/day for 20 weeks.
Nervous system disorders
Seizure
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Nervous system disorders
Syncope
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Vascular disorders
Hot flush
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Vascular disorders
Peripheral coldness
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Ear and labyrinth disorders
Ear pain
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Ear and labyrinth disorders
Tympanic membrane perforation
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Hepatobiliary disorders
Hepatomegaly
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Blood and lymphatic system disorders
Leukopenia
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Skin papilloma
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Gastrointestinal disorders
Abdominal Pain
10.7%
3/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
14.3%
2/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Gastrointestinal disorders
Abdominal Pain upper
3.6%
1/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
20.0%
3/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Gastrointestinal disorders
Constipation
10.7%
3/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Gastrointestinal disorders
Diarrhoea
10.7%
3/28 • Up to 48 weeks
17.9%
5/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Gastrointestinal disorders
Vomiting
21.4%
6/28 • Up to 48 weeks
21.4%
6/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
21.4%
3/14 • Up to 48 weeks
General disorders
Pyrexia
25.0%
7/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
20.0%
3/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
21.4%
3/14 • Up to 48 weeks
21.4%
3/14 • Up to 48 weeks
Infections and infestations
Gasteroenteritis
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Infections and infestations
Nasopharyngitis
7.1%
2/28 • Up to 48 weeks
14.3%
4/28 • Up to 48 weeks
20.0%
3/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
14.3%
2/14 • Up to 48 weeks
Infections and infestations
Upper respiratory tract infection
35.7%
10/28 • Up to 48 weeks
14.3%
4/28 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
20.0%
3/15 • Up to 48 weeks
21.4%
3/14 • Up to 48 weeks
14.3%
2/14 • Up to 48 weeks
Infections and infestations
Rhinitis
7.1%
2/28 • Up to 48 weeks
14.3%
4/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
14.3%
2/14 • Up to 48 weeks
Injury, poisoning and procedural complications
Arthropod bite
3.6%
1/28 • Up to 48 weeks
7.1%
2/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Injury, poisoning and procedural complications
Contusion
7.1%
2/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Injury, poisoning and procedural complications
Fall
7.1%
2/28 • Up to 48 weeks
14.3%
4/28 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
20.0%
3/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Investigations
Blood uric acid increased
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Investigations
Protein Urine Present
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
20.0%
3/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Investigations
Weight increased
3.6%
1/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Metabolism and nutrition disorders
Increased appetite
3.6%
1/28 • Up to 48 weeks
7.1%
2/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Metabolism and nutrition disorders
Vitamin D Deficiency
7.1%
2/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Pain in extremity
7.1%
2/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
26.7%
4/15 • Up to 48 weeks
26.7%
4/15 • Up to 48 weeks
14.3%
2/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Nervous system disorders
Headache
10.7%
3/28 • Up to 48 weeks
7.1%
2/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
21.4%
3/14 • Up to 48 weeks
Nervous system disorders
Psychomotor hyperactivity
7.1%
2/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Abnormal behaviour
7.1%
2/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Psychiatric disorders
Aggression
7.1%
2/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Irritability
0.00%
0/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Respiratory, thoracic and mediastinal disorders
Cough
17.9%
5/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
26.7%
4/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
14.3%
2/14 • Up to 48 weeks
Respiratory, thoracic and mediastinal disorders
Nasal congestion
0.00%
0/28 • Up to 48 weeks
7.1%
2/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Hypertrichosis
3.6%
1/28 • Up to 48 weeks
10.7%
3/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Rash
7.1%
2/28 • Up to 48 weeks
7.1%
2/28 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
14.3%
2/14 • Up to 48 weeks
Gastrointestinal disorders
Mouth Ulceration
0.00%
0/28 • Up to 48 weeks
7.1%
2/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Gastrointestinal disorders
Toothache
3.6%
1/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Gastrointestinal disorders
Diarrhoea haemorrhagic
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Gastrointestinal disorders
Flatulance
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Enterobiasis
3.6%
1/28 • Up to 48 weeks
7.1%
2/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Conjunctivitis
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Infections and infestations
Ear Infection
3.6%
1/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Infections and infestations
Gastroenteritis
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Infections and infestations
Tonsilitis
3.6%
1/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
14.3%
2/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Viral Infection
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
COVID-19
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Infections and infestations
Cystitis
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Fungal Infection
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Gastroenteritis viral/viral gasteroenteritis
10.7%
3/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Hand-foot-and-mouth disease
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Infections and infestations
Impetigo
7.1%
2/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Influenza
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
14.3%
2/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Moluscum contagiosum
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Infections and infestations
Otitis media bacterial
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Pharyngitis streptococcal
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Infections and infestations
Pneumonia
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Respiratory track infection viral
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Steptococcal infection
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Tooth infection
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Infections and infestations
Viral upper respiratory tract infection
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Endocrine disorders
Cushingoid
14.3%
4/28 • Up to 48 weeks
32.1%
9/28 • Up to 48 weeks
26.7%
4/15 • Up to 48 weeks
26.7%
4/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Endocrine disorders
Growth hormone deficiency
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Injury, poisoning and procedural complications
Ligament strain
3.6%
1/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Injury, poisoning and procedural complications
Back injury
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Injury, poisoning and procedural complications
Muscle strain
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Injury, poisoning and procedural complications
Vaccination complication
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Back pain
3.6%
1/28 • Up to 48 weeks
7.1%
2/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Athralgia
3.6%
1/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Muscle spasms
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Myalgia
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Costrochondritis
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Joint contracture
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Joint swelling
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Muscle atrophy
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Muscular weakness
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Musculoskeletal pain
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Musculoskeletal stiffness
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Vertebral wedging
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Musculoskeletal and connective tissue disorders
Agitation
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Sleep disorder
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Anger
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Dysphemia
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Emotional disorder
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Enuresis
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Initial insomnia
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Insomnia
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Psychiatric disorders
Mood swings
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Oppositional defiant disorder
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Personality change
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Trichotillomania
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Epistaxis
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Respiratory, thoracic and mediastinal disorders
Rhinorrhoea
3.6%
1/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Respiratory, thoracic and mediastinal disorders
Oropharyngeal pain
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Eczema
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Perioral dermatitis
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Pruritis
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Dry skin
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Erythema
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Psychiatric disorders
Night sweats
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Rash macropapular
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Urticaria
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Skin and subcutaneous tissue disorders
Viral rash
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Investigations
Cortisol decreased
3.6%
1/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Investigations
Bacterial test postive
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Investigations
Blood pressure increased
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Investigations
Blood triglycerides increased
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Investigations
Electrocardiogram abnormal
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Investigations
Glycosylated haemoglobin increased
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Investigations
Lipase decreased
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Investigations
Urine analysis abnormal
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Investigations
Weight decreased
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Metabolism and nutrition disorders
Decreased appetite
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Metabolism and nutrition disorders
Hypertriglyceridaemia
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Metabolism and nutrition disorders
Overweight
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Metabolism and nutrition disorders
Polydipsia
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
General disorders
Asthenia
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
General disorders
Fatigue
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
13.3%
2/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
General disorders
Impaired healing
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
General disorders
Thirst
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Renal and urinary disorders
Chromaturia
0.00%
0/28 • Up to 48 weeks
3.6%
1/28 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
Renal and urinary disorders
Proteinuria
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Nervous system disorders
Dizziness
0.00%
0/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
7.1%
1/14 • Up to 48 weeks
Nervous system disorders
Poor quality sleep
3.6%
1/28 • Up to 48 weeks
0.00%
0/28 • Up to 48 weeks
0.00%
0/15 • Up to 48 weeks
6.7%
1/15 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks
0.00%
0/14 • Up to 48 weeks

Additional Information

Dr. Eric Hoffman

ReveraGen BioPharma Inc.

Phone: 301-762-7980

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place