Trial Outcomes & Findings for An Observational Study of the Safety of Direct-acting Antivirals in Patients With Hepatitis C (NCT NCT03423641)

NCT ID: NCT03423641

Last Updated: 2019-08-07

Results Overview

Inpatient encounter with an ICD-9 diagnosis code of 410.xx or ICD-10 diagnosis code of I21.xx.

Recruitment status

COMPLETED

Target enrollment

33808 participants

Primary outcome timeframe

Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Results posted on

2019-08-07

Participant Flow

This is a retrospective observational study, thus patients are not assigned and no one is excluded from the study after they become eligible.

Participant milestones

Participant milestones
Measure
Direct Acting Antivirals
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Overall Study
STARTED
15524
18284
Overall Study
COMPLETED
15193
10210
Overall Study
NOT COMPLETED
331
8074

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

There is no difference between the baseline population and the analysis population.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Direct Acting Antivirals
n=15524 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=18284 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Total
n=33808 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=99 Participants • There is no difference between the baseline population and the analysis population.
0 Participants
n=107 Participants • There is no difference between the baseline population and the analysis population.
0 Participants
n=206 Participants • There is no difference between the baseline population and the analysis population.
Age, Categorical
Between 18 and 65 years
12349 Participants
n=99 Participants • There is no difference between the baseline population and the analysis population.
14638 Participants
n=107 Participants • There is no difference between the baseline population and the analysis population.
26987 Participants
n=206 Participants • There is no difference between the baseline population and the analysis population.
Age, Categorical
>=65 years
3175 Participants
n=99 Participants • There is no difference between the baseline population and the analysis population.
3646 Participants
n=107 Participants • There is no difference between the baseline population and the analysis population.
6821 Participants
n=206 Participants • There is no difference between the baseline population and the analysis population.
Sex: Female, Male
Female
6092 Participants
n=99 Participants
6962 Participants
n=107 Participants
13054 Participants
n=206 Participants
Sex: Female, Male
Male
9432 Participants
n=99 Participants
11322 Participants
n=107 Participants
20754 Participants
n=206 Participants
Race (NIH/OMB)
American Indian or Alaska Native
112 Participants
n=99 Participants
116 Participants
n=107 Participants
228 Participants
n=206 Participants
Race (NIH/OMB)
Asian
891 Participants
n=99 Participants
772 Participants
n=107 Participants
1663 Participants
n=206 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
49 Participants
n=99 Participants
51 Participants
n=107 Participants
100 Participants
n=206 Participants
Race (NIH/OMB)
Black or African American
2699 Participants
n=99 Participants
3838 Participants
n=107 Participants
6537 Participants
n=206 Participants
Race (NIH/OMB)
White
8670 Participants
n=99 Participants
9892 Participants
n=107 Participants
18562 Participants
n=206 Participants
Race (NIH/OMB)
More than one race
700 Participants
n=99 Participants
720 Participants
n=107 Participants
1420 Participants
n=206 Participants
Race (NIH/OMB)
Unknown or Not Reported
2403 Participants
n=99 Participants
2895 Participants
n=107 Participants
5298 Participants
n=206 Participants
Region of Enrollment
United States
15524 Participants
n=99 Participants
18284 Participants
n=107 Participants
33808 Participants
n=206 Participants

PRIMARY outcome

Timeframe: Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients without a prior diagnosis of MI.

Inpatient encounter with an ICD-9 diagnosis code of 410.xx or ICD-10 diagnosis code of I21.xx.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=14959 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=17421 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Acute Myocardial Infarction (AMI)
3.3 Events per 1000 person years
Interval 2.0 to 4.7
5.2 Events per 1000 person years
Interval 4.6 to 5.8

PRIMARY outcome

Timeframe: Labs and diagnoses collected from clinical encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients with MELD scores less than 15 at baseline.

An acute change in MELD (model for end stage liver disease) score of 5 or more and the change is deemed to have persisted (defined as meeting one of the following criteria: MELD continues to be elevated 3 months later, liver transplant, death). The minimum value for the MELD is 6.43, but there is no maximum value. Higher scores mean a worse outcome.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=13321 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=13716 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Acute on Chronic Liver Failure
16.5 Events per 1000 person years
Interval 13.3 to 19.7
24.1 Events per 1000 person years
Interval 22.8 to 25.5

PRIMARY outcome

Timeframe: Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients without a prior diagnosis of AKF.

Encounters with an ICD-9 diagnosis code of 584.xx or ICD-10 diagnosis code of N17.xx.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=14321 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=16926 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Acute Kidney Failure (AKF)
24.2 Events per 1000 person years
Interval 20.5 to 28.0
33.7 Events per 1000 person years
Interval 32.2 to 35.2

PRIMARY outcome

Timeframe: Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients without a prior diagnosis of MODS.

Inpatient encounters with ICD-9 diagnosis code of 995.92, 995.94, 785.52 or ICD-10 code of R65.11 or R65.2x.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=15107 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=17763 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Multiple Organ Dysfunction Syndrome (MODS)
9.7 Events per 1000 person years
Interval 7.4 to 12.0
17.2 Events per 1000 person years
Interval 16.2 to 18.3

PRIMARY outcome

Timeframe: Death dates will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population is equivalent to the baseline population.

Date of death in one or more records. Death data comes from medical records, Social Security, or state databases.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=15524 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=18284 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Death
10.7 Events per 1000 person years
Interval 8.3 to 13.1
33.7 Events per 1000 person years
Interval 32.3 to 35.1

PRIMARY outcome

Timeframe: Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients without a prior diagnosis of a stroke.

Inpatient encounters with ICD-9 diagnosis code of 433.xx, 434.xx or ICD-10 code of I63.xx, I65.xx.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=14758 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=17142 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Ischemic Stroke
3.6 Events per 1000 person years
Interval 2.2 to 5.1
5.8 Events per 1000 person years
Interval 5.1 to 6.4

PRIMARY outcome

Timeframe: Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients without a prior diagnosis of a stroke.

Inpatient encounters with ICD-9 diagnosis code of 430.xx-432.xx or ICD-10 code of I60.xx-I62.xx

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=14802 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=17098 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Hemorrhagic Stroke
1.5 Events per 1000 person years
Interval 0.6 to 2.3
3.1 Events per 1000 person years
Interval 2.6 to 3.5

PRIMARY outcome

Timeframe: Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients without prior diagnosis of jaundice, ascites, hemorrhagic varices or medication dispense of lactulose or rifaximin.

A patient will be characterized as having decompensated cirrhosis from an encounter indicating jaundice (ICD-9 diagnosis code of 782.4 or ICD-10 code of R17), ascites (ICD-9 diagnosis code of 789.5, 789.51, 789.59 or ICD-10 diagnosis code of R18.0, R18.8, K71.51, K70.11, or K70.31), or varices (ICD-9 diagnosis code of 456.0, 456.20 or ICD-10 diagnosis code of I85.01 or I85.11, or a medication dispense of lactulose or rifaximin along with a diagnosis of cirrhosis.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=13496 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=16465 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Decompensated Cirrhosis
23.8 Events per 1000 person years
Interval 20.0 to 27.7
38.6 Events per 1000 person years
Interval 37.0 to 40.2

PRIMARY outcome

Timeframe: Hospitalizations will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population is the same as the baseline population.

An encounter in which the place of service is an inpatient hospitalization.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=15524 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=18284 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Rate of Hospitalizations
162.8 Events per 1000 person years
Interval 157.9 to 167.7
325.0 Events per 1000 person years
Interval 320.6 to 329.4

PRIMARY outcome

Timeframe: ED visits will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population is the same as the baseline population.

An encounter in which the place of service is an emergency department or urgent care center.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=15524 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=18284 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Rate of Emergency Department Visits
551.2 Events per 1000 person years
Interval 542.3 to 560.2
853.4 Events per 1000 person years
Interval 846.2 to 860.5

PRIMARY outcome

Timeframe: Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients without a past diagnosis of arrhythmia.

Inpatient encounters with an ICD-9 diagnosis code of 427.1, 427.42, 427.5, 427.9 or an ICD-10 diagnosis code of I47.2, I49.01, I49.02, I46.9, I49.9.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=13396 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=15272 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Arrhythmia
3.2 Events per 1000 person years
Interval 1.8 to 4.5
4.7 Events per 1000 person years
Interval 4.1 to 5.2

PRIMARY outcome

Timeframe: Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients without a prior diagnosis of liver cancer.

Encounters with ICD-9 diagnosis code of 155.xx or ICD-10 code of C22.xx.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=14905 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=17989 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Liver Cancer
9.3 Events per 1000 person years
Interval 7.0 to 11.5
14.9 Events per 1000 person years
Interval 13.9 to 15.8

PRIMARY outcome

Timeframe: Patient diagnoses collected from encounters will be examined through study completion, or up to 180 days from the day the patient initiated a DAA.

Population: The analysis population consists of the subset of patients without a prior diagnosis of cancer.

Encounters with ICD-9 codes 140.xx through 208.xx, except 155.xx or ICD-10 coes C00-C97 except C22.xx.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=13254 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
n=16689 Participants
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of Cancers Other Than Liver Cancer
20.7 Events per 1000 person years
Interval 17.1 to 24.3
26.4 Events per 1000 person years
Interval 25.0 to 27.7

PRIMARY outcome

Timeframe: Labs will be for up to 180 days following the initiation of a DAA.

Population: At the time of initiating DAA therapy, at least one of the following had to be true (1) Hepatitis B core antibody (HBcAb) positive and Hepatitis B surface antigen (HBsAg) negative (2) Hepatitis B core antibody (HBcAb) positive and undetectable levels of HBV DNA; (3) numerical HBV DNA result

We identified HBV reactivations in three different ways \[Di Bisceglie et al., 2015; Yanny et al., 2018\]: (1) patients who had a history of Hepatitis B core antibody (HBcAb) positive and were Hepatitis B surface antigen (HBsAg) negative at the time of initiating DAA therapy who became HBsAg positive within 180 days after receiving a DAA; (2) patients with undetectable levels of HBV DNA at the time of initiating DAA therapy who had a numerical result within 180 days after receiving a DAA; (3) patients with a numerical HBV DNA result at the time of initiating DAA therapy whose viral load increased by a factor of 10 within 180 days after receiving a DAA. For all methods of detecting a reactivation, we required that the reactivations be clinically significant: bilirubin at least 3, aspartate aminotransferase (AST) at least 400, or alanine aminotransferase (ALT) at least 500.

Outcome measures

Outcome measures
Measure
Direct Acting Antivirals
n=2308 Participants
Patients who receive a direct acting antiviral enter the DAA cohort at the time of initiation of the drug. Direct Acting Antivirals: The time period during which a patient is dispensed the medication and for up to 180 days after initiation of the medication.
Comparison
The exposure time of patients who have not received a direct acting antiviral (patients can change from the comparison to the DAA group once they receive the medication)
Incidence of HBV Reactivation
1 Participants

Adverse Events

Direct Acting Antivirals

Serious events: 0 serious events
Other events: 0 other events
Deaths: 77 deaths

Comparison

Serious events: 0 serious events
Other events: 0 other events
Deaths: 2186 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Elizabeth McGlynn, Ph.D.

Kaiser Permanente

Phone: 6265643807

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place