Study of ORL-1B in Patients With Biotinidase Deficiency
NCT03269045 · Status: COMPLETED · Phase: PHASE1/PHASE2 · Type: INTERVENTIONAL · Enrollment: 20
Last updated 2018-01-17
Summary
An Open-label, Single-arm, Phase 2 Study of Biotin in Patients With Biotinidase Deficiency.
Conditions
- Biotinidase Deficiency
Interventions
- DRUG
-
ORL-1B
Oral ORL-1B
Sponsors & Collaborators
-
Orpha Labs
lead INDUSTRY
Study Design
- Allocation
- NA
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Max Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2013-08-31
- Primary Completion
- 2018-01-01
- Completion
- 2018-01-01
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