Trial Outcomes & Findings for Focused Ultrasound and Pembrolizumab in Metastatic Breast Cancer (NCT NCT03237572)

NCT ID: NCT03237572

Last Updated: 2026-02-09

Results Overview

How many of the immune cells inside a tumor are a specific type of "killer" T cell

Recruitment status

TERMINATED

Study phase

PHASE1

Target enrollment

13 participants

Primary outcome timeframe

baseline and week 4

Results posted on

2026-02-09

Participant Flow

Participant milestones

Participant milestones
Measure
Arm A: 1st Dose of Pembrolizumab After HIFU
Pembrolizumab (200 mg) administered intravenously, days 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Arm B: 1st Dose of Pembrolizumab Before HIFU
Pembrolizumab (200 mg) intravenously, days 1, 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Overall Study
NOT COMPLETED
0
0
Overall Study
STARTED
6
7
Overall Study
COMPLETED
6
7

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Focused Ultrasound and Pembrolizumab in Metastatic Breast Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Arm A: 1st Dose of Pembrolizumab After HIFU
n=6 Participants
Pembrolizumab (200 mg) administered intravenously, days 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Arm B: 1st Dose of Pembrolizumab Before HIFU
n=7 Participants
Pembrolizumab (200 mg) intravenously, days 1, 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Total
n=13 Participants
Total of all reporting groups
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=41 Participants
0 Participants
n=1581 Participants
0 Participants
n=4626 Participants
Age, Customized
47.7 years
STANDARD_DEVIATION 10.3 • n=41 Participants
57.9 years
STANDARD_DEVIATION 9.63 • n=1581 Participants
53.2 years
STANDARD_DEVIATION 10.9 • n=4626 Participants
Sex: Female, Male
Female
6 Participants
n=41 Participants
7 Participants
n=1581 Participants
13 Participants
n=4626 Participants
Sex: Female, Male
Male
0 Participants
n=41 Participants
0 Participants
n=1581 Participants
0 Participants
n=4626 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
1 Participants
n=41 Participants
0 Participants
n=1581 Participants
1 Participants
n=4626 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
5 Participants
n=41 Participants
7 Participants
n=1581 Participants
12 Participants
n=4626 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=41 Participants
0 Participants
n=1581 Participants
0 Participants
n=4626 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=41 Participants
0 Participants
n=1581 Participants
0 Participants
n=4626 Participants
Race (NIH/OMB)
Asian
0 Participants
n=41 Participants
0 Participants
n=1581 Participants
0 Participants
n=4626 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=41 Participants
0 Participants
n=1581 Participants
0 Participants
n=4626 Participants
Race (NIH/OMB)
Black or African American
2 Participants
n=41 Participants
3 Participants
n=1581 Participants
5 Participants
n=4626 Participants
Race (NIH/OMB)
White
3 Participants
n=41 Participants
4 Participants
n=1581 Participants
7 Participants
n=4626 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=41 Participants
0 Participants
n=1581 Participants
1 Participants
n=4626 Participants
Region of Enrollment
United States
6 participants
n=41 Participants
7 participants
n=1581 Participants
13 participants
n=4626 Participants
Eastern Cooperative Oncology Group (ECOG) Performance Status
1.2 units on a scale
n=41 Participants
1.3 units on a scale
n=1581 Participants
1.2 units on a scale
n=4626 Participants

PRIMARY outcome

Timeframe: baseline and week 4

Population: The ratio of CD8/CD4 in the periablated zone around the tumor is described as mean of the ratios of CD8/CD4 in each patient collected by ultrasound guided needle biopsy in the peri-ablated tumor area (within 10mm of ablation margin)

How many of the immune cells inside a tumor are a specific type of "killer" T cell

Outcome measures

Outcome measures
Measure
Arm A: 1st Dose of Pembrolizumab After HIFU
n=6 Participants
Pembrolizumab (200 mg) administered intravenously, days 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Arm B: 1st Dose of Pembrolizumab Before HIFU
n=7 Participants
Pembrolizumab (200 mg) intravenously, days 1, 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Change in Proportion of CD8+ Tumor Infiltrating Lymphocytes
35.98 ratio of CD8 to CD4
Standard Deviation 64.38
126.39 ratio of CD8 to CD4
Standard Deviation 216.16

Adverse Events

Arm A: 1st Dose of Pembrolizumab After HIFU

Serious events: 1 serious events
Other events: 6 other events
Deaths: 0 deaths

Arm B: 1st Dose of Pembrolizumab Before HIFU

Serious events: 3 serious events
Other events: 7 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Arm A: 1st Dose of Pembrolizumab After HIFU
n=6 participants at risk
Pembrolizumab (200 mg) administered intravenously, days 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Arm B: 1st Dose of Pembrolizumab Before HIFU
n=7 participants at risk
Pembrolizumab (200 mg) intravenously, days 1, 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Investigations
Blood Bilirubin Increased
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Endocrine disorders
Hyperthyroidism
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
General disorders
Fever
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Investigations
Alkaline Phosphatase Increased
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
28.6%
2/7 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Investigations
Aspartate aminotransferase increased
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
28.6%
2/7 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).

Other adverse events

Other adverse events
Measure
Arm A: 1st Dose of Pembrolizumab After HIFU
n=6 participants at risk
Pembrolizumab (200 mg) administered intravenously, days 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Arm B: 1st Dose of Pembrolizumab Before HIFU
n=7 participants at risk
Pembrolizumab (200 mg) intravenously, days 1, 22, 43, 64, followed by day 1 of each ensuing 3 -week cycle. Focused ultrasound tumor ablation day 15. High-intensity focused ultrasound ablation will target 50% of the tumor, up to 3 cubic centimeters. Pembrolizumab: Pembrolizumab (200 mg) High-intensity focused ultrasound (HIFU): Ablation will target 50% of the tumor, up to 3 cubic centimeters
Ear and labyrinth disorders
Tinnitus
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Endocrine disorders
Hypothyroidism
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Gastrointestinal disorders
Abdominal Pain
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Gastrointestinal disorders
Diarrhea
33.3%
2/6 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
42.9%
3/7 • Number of events 3 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Gastrointestinal disorders
Nausea
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Gastrointestinal disorders
Vomiting
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
General disorders
Fatigue
33.3%
2/6 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
42.9%
3/7 • Number of events 3 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
General disorders
Pain
33.3%
2/6 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
General disorders
Bruising
33.3%
2/6 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Investigations
Alanine aminotransferase increased
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Investigations
Lymphocyte count decreased
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Investigations
Weight Loss
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Investigations
White blood cell decreased
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Metabolism and nutrition disorders
Anorexia
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Metabolism and nutrition disorders
Hypercalcemia
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Metabolism and nutrition disorders
Hyperglycemia
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
28.6%
2/7 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Metabolism and nutrition disorders
Hyperuricemia
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Metabolism and nutrition disorders
Hypoalbuminemia
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Metabolism and nutrition disorders
Hypoglycemia
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Metabolism and nutrition disorders
Hypokalemia
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Metabolism and nutrition disorders
Hypomagnesemia
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
28.6%
2/7 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Metabolism and nutrition disorders
Hyponatremia
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Respiratory, thoracic and mediastinal disorders
Dyspnea
33.3%
2/6 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Skin and subcutaneous tissue disorders
Pruritus
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
28.6%
2/7 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Skin and subcutaneous tissue disorders
Rash maculo-papular
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
0.00%
0/7 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Skin and subcutaneous tissue disorders
Skin and subcutaneous tissue disorders - Other, specify
0.00%
0/6 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
14.3%
1/7 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
Skin and subcutaneous tissue disorders
Skin induration
16.7%
1/6 • Number of events 1 • AEs were collected from the time treatment begins until end of treatment (about 1 year).
28.6%
2/7 • Number of events 2 • AEs were collected from the time treatment begins until end of treatment (about 1 year).

Additional Information

Patrick Dillon MD

University of Virginia

Phone: 434-924-8073

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place