Long-Term Safety, Tolerability, and Efficacy of DTX101 (AAVrh10FIX) in Adults With Moderate/Severe to Severe Hemophilia B
NCT02971969 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 6
Last updated 2022-01-06
Summary
A long-term follow-up study to evaluate the safety, tolerability, and efficacy of DTX101 in adult males with moderate/severe to severe hemophilia B.
Conditions
- Hemophilia B
Sponsors & Collaborators
- lead INDUSTRY
Principal Investigators
-
Medical Director · Ultragenyx Pharmaceutical Inc
Eligibility
- Min Age
- 18 Years
- Sex
- MALE
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2017-01-31
- Primary Completion
- 2021-11-06
- Completion
- 2021-11-06
Countries
- United States
- United Kingdom
Study Locations
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