Trial Outcomes & Findings for Phase 2 Study of MGL-3196 in Patients With Non-Alcoholic Steatohepatitis (NASH) (NCT NCT02912260)

NCT ID: NCT02912260

Last Updated: 2025-12-23

Results Overview

The primary endpoint was relative change in MRI-PDFF assessed hepatic fat fraction compared with placebo at Week 12 in participants who had both a baseline and Week 12 MRI-PDFF. Least squares (LS) mean was provided for the statistical comparison of MGL-3196 versus placebo.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

125 participants

Primary outcome timeframe

Week 12

Results posted on

2025-12-23

Participant Flow

Participants underwent screening procedures within 42 days of randomization. To participate in the study, participants were required to have had a qualifying liver biopsy within 180 days of randomization.

Participant milestones

Participant milestones
Measure
MGL-3196
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Main Study
STARTED
84
41
Main Study
Received at Least 1 Dose of Study Drug
84
41
Main Study
COMPLETED
74
34
Main Study
NOT COMPLETED
10
7
Extension Study
STARTED
17
14
Extension Study
COMPLETED
16
13
Extension Study
NOT COMPLETED
1
1

Reasons for withdrawal

Reasons for withdrawal
Measure
MGL-3196
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Main Study
Lost to Follow-up
5
4
Main Study
Withdrawal by Subject
2
2
Main Study
Adverse Event
3
0
Main Study
Physician Decision
0
1
Extension Study
Withdrawal by Subject
1
1

Baseline Characteristics

Phase 2 Study of MGL-3196 in Patients With Non-Alcoholic Steatohepatitis (NASH)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
MGL-3196
n=84 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=41 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Total
n=125 Participants
Total of all reporting groups
Age, Continuous
51.8 years
STANDARD_DEVIATION 10.35 • n=9 Participants
47.3 years
STANDARD_DEVIATION 11.71 • n=6 Participants
50.3 years
STANDARD_DEVIATION 10.97 • n=9 Participants
Sex: Female, Male
Female
46 Participants
n=9 Participants
17 Participants
n=6 Participants
63 Participants
n=9 Participants
Sex: Female, Male
Male
38 Participants
n=9 Participants
24 Participants
n=6 Participants
62 Participants
n=9 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
37 Participants
n=9 Participants
22 Participants
n=6 Participants
59 Participants
n=9 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
47 Participants
n=9 Participants
19 Participants
n=6 Participants
66 Participants
n=9 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=9 Participants
0 Participants
n=6 Participants
0 Participants
n=9 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=9 Participants
0 Participants
n=6 Participants
0 Participants
n=9 Participants
Race (NIH/OMB)
Asian
2 Participants
n=9 Participants
3 Participants
n=6 Participants
5 Participants
n=9 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=9 Participants
0 Participants
n=6 Participants
0 Participants
n=9 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=9 Participants
1 Participants
n=6 Participants
2 Participants
n=9 Participants
Race (NIH/OMB)
White
80 Participants
n=9 Participants
37 Participants
n=6 Participants
117 Participants
n=9 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=9 Participants
0 Participants
n=6 Participants
0 Participants
n=9 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=9 Participants
0 Participants
n=6 Participants
1 Participants
n=9 Participants
Hepatic Fat Fraction by MRI-PDFF at Screening
20.25 percentage
STANDARD_DEVIATION 6.843 • n=9 Participants
19.63 percentage
STANDARD_DEVIATION 8.159 • n=6 Participants
20.05 percentage
STANDARD_DEVIATION 7.274 • n=9 Participants

PRIMARY outcome

Timeframe: Week 12

Population: MRI-PDFF evaluable population: all participants who were randomized in the study, received study drug, and finished Week 12 visit, with valid MRI-PDFF measurements at both baseline and Week 12 Visit.

The primary endpoint was relative change in MRI-PDFF assessed hepatic fat fraction compared with placebo at Week 12 in participants who had both a baseline and Week 12 MRI-PDFF. Least squares (LS) mean was provided for the statistical comparison of MGL-3196 versus placebo.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percent Change From Baseline To Week 12 In Hepatic Fat Fraction Assessed By Magnetic Resonance Imaging Proton Density Fat Fraction (MRI-PDFF)
-32.9 percent change
Standard Error 3.0
-10.4 percent change
Standard Error 4.3

SECONDARY outcome

Timeframe: Week 12 and Week 36

Population: Safety population: all randomized participants who received at least 1 dose of study drug.

An AE was defined as any untoward medical occurrence in a clinical investigation participant administered a pharmaceutical product, which does not necessarily have a causal relationship with the treatment. A summary of serious and all other non-serious AEs, regardless of causality, is located in the Reported Adverse Events module.

Outcome measures

Outcome measures
Measure
MGL-3196
n=84 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=41 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants With Adverse Events (AEs)
Week 12
71.4 percentage of participants
46.3 percentage of participants
Percentage Of Participants With Adverse Events (AEs)
Week 36
86.9 percentage of participants
68.3 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: Modified Intent-to-Treat (mITT) population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The endpoint was relative change assessed hepatic fat fraction compared with placebo at Week 36. LS mean was provided for the statistical comparison of MGL-3196 versus placebo.

Outcome measures

Outcome measures
Measure
MGL-3196
n=74 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percent Change From Baseline To Week 36 In Hepatic Fat Fraction Assessed By MRI-PDFF
-37.3 percent change
Standard Error 3.7
-8.9 percent change
Standard Error 5.4

SECONDARY outcome

Timeframe: Week 12

Population: MRI-PDFF evaluable population: all participants who were randomized in the study, received study drug, and finished Week 12 visit, with valid MRI-PDFF measurements at both baseline and Week 12 Visit.

The endpoint was change in MRI-PDFF assessed absolute hepatic fat fraction compared with placebo at Week 12. LS mean was provided for the comparison of MGL-3196 versus placebo.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline To Week 12 In Absolute Hepatic Fat Fraction Assessed By MRI-PDFF
-7.0 percentage
Standard Error 0.6
-2.7 percentage
Standard Error 0.8

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The endpoint was change in assessed absolute hepatic fat fraction compared with placebo at Week 36. LS mean was provided for the comparison of MGL-3196 versus placebo.

Outcome measures

Outcome measures
Measure
MGL-3196
n=74 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline To Week 36 In Absolute Hepatic Fat Fraction Assessed By MRI-PDFF
-8.2 percentage
Standard Error 0.7
-2.9 percentage
Standard Error 1.0

SECONDARY outcome

Timeframe: Week 12

Population: MRI-PDFF evaluable population: all participants who were randomized in the study, received study drug, and finished Week 12 visit, with valid MRI-PDFF measurements at both baseline and Week 12 Visit.

The endpoint presented the percentage of participants achieving a relative fat reduction of ≥30% at Week 12.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants With At Least 30% Relative Fat Reduction at Week 12
60.3 percentage of participants
18.4 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The endpoint presented the percentage of participants achieving a relative fat reduction of ≥30% at Week 36.

Outcome measures

Outcome measures
Measure
MGL-3196
n=74 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants With At Least 30% Relative Fat Reduction At Week 36
67.6 percentage of participants
29.4 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The NAS is a histologic scale for non-alcoholic steatohepatitis (NASH) activity, which combines into a single score steatosis (Grade 0 to 3), ballooning (Grade 0 to 2), and lobular inflammation (Grade 0 to 3). The endpoint presented the percentage of participants with a 1-point or greater reduction in NAS.

Outcome measures

Outcome measures
Measure
MGL-3196
n=73 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants Achieving A 1-Point Reduction In Non-alcoholic Fatty Liver Disease Activity Score (NAS) At Week 36
76.7 percentage of participants
64.7 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The NAS is a histologic scale for NASH activity, which combines into a single score steatosis (Grade 0 to 3), ballooning (Grade 0 to 2), and lobular inflammation (Grade 0 to 3). The endpoint presented the percentage of participants with a 2-point or greater reduction in NAS.

Outcome measures

Outcome measures
Measure
MGL-3196
n=73 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants Achieving A 2-Point Reduction In NAS At Week 36
56.2 percentage of participants
32.4 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The NAS is a histologic scale for NASH activity, which combines into a single score steatosis (Grade 0 to 3), ballooning (Grade 0 to 2), and lobular inflammation (Grade 0 to 3). The endpoint presented the percentage of participants with a 2-point or greater reduction in NAS and a 1-point or greater reduction in lobular inflammation or hepatocellular ballooning.

Outcome measures

Outcome measures
Measure
MGL-3196
n=73 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants Achieving A 2-Point Reduction In NAS And Either A ≥1-Point Reduction In Lobular Inflammation Or Hepatocellular Ballooning At Week 36
50.7 percentage of participants
32.4 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The NAS is a histologic scale for NASH activity, which combines into a single score steatosis (Grade 0 to 3), ballooning (Grade 0 to 2), and lobular inflammation (Grade 0 to 3). Fibrosis stage (0 to 3) was also included in the assessment. The endpoint presented the percentage of participants with a 2-point or greater reduction in NAS without worsening fibrosis.

Outcome measures

Outcome measures
Measure
MGL-3196
n=73 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants Achieving A 2-Point Reduction In NAS Without Fibrosis Worsening At Week 36
45.2 percentage of participants
32.4 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The NAS is a histologic scale for NASH activity, which combines into a single score steatosis (Grade 0 to 3), ballooning (Grade 0 to 2), and lobular inflammation (Grade 0 to 3). The endpoint presented the percentage of participants with a reduction in hepatocellular steatosis.

Outcome measures

Outcome measures
Measure
MGL-3196
n=73 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants With A Reduction In Hepatocellular Steatosis At Week 36
61.6 percentage of participants
44.1 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The NAS is a histologic scale for NASH activity, which combines into a single score steatosis (Grade 0 to 3), ballooning (Grade 0 to 2), and lobular inflammation (Grade 0 to 3). The endpoint presented the percentage of participants with a reduction in lobular inflammation.

Outcome measures

Outcome measures
Measure
MGL-3196
n=73 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants With A Reduction In Lobular Inflammation At Week 36
21.9 percentage of participants
17.6 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The NAS is a histologic scale for NASH activity, which combines into a single score steatosis (Grade 0 to 3), ballooning (Grade 0 to 2), and lobular inflammation (Grade 0 to 3). The endpoint presented the percentage of participants with a reduction in hepatocellular ballooning.

Outcome measures

Outcome measures
Measure
MGL-3196
n=73 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants With A Reduction In Hepatocellular Ballooning At Week 36
58.9 percentage of participants
58.8 percentage of participants

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The endpoint presented the percentage of participants achieving NASH resolution with a 2-point reduction at Week 36.

Outcome measures

Outcome measures
Measure
MGL-3196
n=73 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percentage Of Participants Achieving NASH Resolution With At Least 2-Point Reduction In NAS At Week 36
27.4 percentage of participants
14.7 percentage of participants

SECONDARY outcome

Timeframe: Week 12

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

hsCRP was used as a non-invasive inflammation marker for this study. Blood samples were collected to determine the effect of MGL-3196 on hsCRP.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percent Change From Baseline To Week 12 In High-sensitivity C-reactive Protein (hsCRP)
29.3 percent change
Standard Error 18.36
13.2 percent change
Standard Error 25.97

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

hsCRP was used as a non-invasive inflammation marker for this study. Blood samples were collected to determine the effect of MGL-3196 on hsCRP.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percent Change From Baseline To Week 36 In hsCRP
90.9 percent change
Standard Error 67.52
34.0 percent change
Standard Error 96.88

SECONDARY outcome

Timeframe: Week 12

Population: MRI-PDFF evaluable population: all participants who were randomized in the study, received study drug, and finished Week 12 visit, with valid MRI-PDFF measurements at both baseline and Week 12 Visit.

Blood samples were collected to determine the effect of MGL-3196 on serum ALT.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline To Week 12 In Serum Alanine Aminotransferase (ALT)
-8.2 IU/L
Standard Error 2.7
-5.2 IU/L
Standard Error 3.9

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits

Blood samples were collected to determine the effect of MGL-3196 on serum ALT.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=37 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline To Week 36 In ALT
-15.4 IU/L
Standard Error 4.7
11.0 IU/L
Standard Error 6.8

SECONDARY outcome

Timeframe: Week 12

Population: MRI-PDFF evaluable population: all participants who were randomized in the study, received study drug, and finished Week 12 visit, with valid MRI-PDFF measurements at both baseline and Week 12 Visit.

Blood samples were collected to determine the effect of MGL-3196 on serum AST.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline To Week 12 In Serum Aspartate Aminotransferase (AST)
-5.8 IU/L
Standard Error 1.8
-1.1 IU/L
Standard Error 2.5

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

Blood samples were collected to determine the effect of MGL-3196 on serum AST.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=37 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline To Week 36 In AST
-7.4 IU/L
Standard Error 1.9
3.6 IU/L
Standard Error 2.8

SECONDARY outcome

Timeframe: Week 12

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

Blood samples were collected to determine the effect of MGL-3196 on lipid parameters including low-density lipoprotein cholesterol (LDL-C), high-density lipoprotein cholesterol (HDL-C), non-HDL-C, total cholesterol (TC), triglycerides (TG), apolipoprotein B (ApoB), and Apolipoprotein CIII (ApoCIII).

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percent Change From Baseline To Week 12 In Lipid Parameters
LDL-C
-10.6 percent change
Standard Error 1.96
2.2 percent change
Standard Error 2.79
Percent Change From Baseline To Week 12 In Lipid Parameters
HDL-C
5.0 percent change
Standard Error 1.91
1.8 percent change
Standard Error 2.72
Percent Change From Baseline To Week 12 In Lipid Parameters
non-HDL-C
-12.1 percent change
Standard Error 1.74
1.2 percent change
Standard Error 2.47
Percent Change From Baseline To Week 12 In Lipid Parameters
TC
-8.7 percent change
Standard Error 1.37
0.9 percent change
Standard Error 1.95
Percent Change From Baseline To Week 12 In Lipid Parameters
TG
-6.8 percent change
Standard Error 4.23
9.8 percent change
Standard Error 6.01
Percent Change From Baseline To Week 12 In Lipid Parameters
ApoB
-14.5 percent change
Standard Error 1.59
0.8 percent change
Standard Error 2.25
Percent Change From Baseline To Week 12 In Lipid Parameters
ApoCIII
-9.1 percent change
Standard Error 3.23
8.7 percent change
Standard Error 4.62
Percent Change From Baseline To Week 12 In Lipid Parameters
Lp(a)
-8.6 percent change
Standard Error 7.54
12.3 percent change
Standard Error 10.67

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits

Blood samples were collected to determine the effect of MGL-3196 on lipid parameters including LDL-C, HDL-C, non-HDL-C, TC, TG, ApoB, and ApoCIII.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percent Change From Baseline To Week 36 In Lipid Parameters
LDL-C
-11.0 percent change
Standard Error 2.14
1.5 percent change
Standard Error 3.11
Percent Change From Baseline To Week 36 In Lipid Parameters
HDL-C
10.5 percent change
Standard Error 3.72
12.0 percent change
Standard Error 5.41
Percent Change From Baseline To Week 36 In Lipid Parameters
non-HDL-C
-14.0 percent change
Standard Error 1.90
2.1 percent change
Standard Error 2.76
Percent Change From Baseline To Week 36 In Lipid Parameters
TC
-8.9 percent change
Standard Error 1.61
3.6 percent change
Standard Error 2.34
Percent Change From Baseline To Week 36 In Lipid Parameters
TG
-19.8 percent change
Standard Error 4.29
17.5 percent change
Standard Error 6.24
Percent Change From Baseline To Week 36 In Lipid Parameters
ApoB
-16.5 percent change
Standard Error 1.79
0.9 percent change
Standard Error 2.58
Percent Change From Baseline To Week 36 In Lipid Parameters
ApoCIII
-12.0 percent change
Standard Error 3.72
24.5 percent change
Standard Error 5.42
Percent Change From Baseline To Week 36 In Lipid Parameters
Lp(a)
19.0 percent change
Standard Error 10.95
39.0 percent change
Standard Error 15.82

SECONDARY outcome

Timeframe: Week 12

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

Blood samples were collected to determine the effect of MGL-3196 on lipid parameter Lp(a).

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percent Change From Baseline To Week 12 In Lipid Parameter Lipoprotein(a) (Lp[a])
-8.6 percent change
Standard Error 7.54
12.3 percent change
Standard Error 10.67

SECONDARY outcome

Timeframe: Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

Blood samples were collected to determine the effect of MGL-3196 on lipid parameter Lp(a).

Outcome measures

Outcome measures
Measure
MGL-3196
n=71 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=34 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Percent Change From Baseline To Week 36 In Lipid Parameter Lp[a]
19.0 percent change
Standard Error 10.95
39.0 percent change
Standard Error 15.82

SECONDARY outcome

Timeframe: Week 12 and Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

Serum CK-18 fragments, detected using the M30 antibody, is a non-invasive biomarker for NASH that may reflect hepatocyte apoptosis.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=37 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline To Week 12 And Week 36 In Cytokeratin-18 (CK-18)
Week 12
-146.2 U/L
Standard Error 35
-87.5 U/L
Standard Error 51
Change From Baseline To Week 12 And Week 36 In Cytokeratin-18 (CK-18)
Week 36
-272.0 U/L
Standard Error 33
-101.0 U/L
Standard Error 47

SECONDARY outcome

Timeframe: Week 12 and Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The ELF Test is a non-invasive blood test that provides a simple, unitless numeric score that is used as a marker of collagen formation and fibrogenic activity and can be used to assess the risk of progression to cirrhosis. Scores below 9.8 indicate low risk of disease progression, and scores above 11.29 indicate high risk. The ELF score is derived from values of three serum biomarkers: hyaluronic acid (HA), procollagen III N-terminal peptide (PIIINP), and tissue inhibitor of metalloproteinase-1 (TIMP-1). The formula is 2.278 + 0.851 × ln(HA) + 0.751 × ln(PIIINP) + 0.394 × ln(TIMP-1); there are no minimum or maximum values.

Outcome measures

Outcome measures
Measure
MGL-3196
n=40 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=21 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline To Week 12 And Week 36 In Enhanced Liver Fibrosis (ELF) Test
Week 12
-0.38 score on a scale
Standard Error 0.09
-0.02 score on a scale
Standard Error 0.12
Change From Baseline To Week 12 And Week 36 In Enhanced Liver Fibrosis (ELF) Test
Week 36
-0.66 score on a scale
Standard Error 0.12
-0.18 score on a scale
Standard Error 0.16

SECONDARY outcome

Timeframe: Week 12 and Week 36

Population: mITT population: all participants who were randomized in the study, received at least 1 dose of study drug, and had lipid and other efficacy measurements at Week 4 or later visits.

The Fib-4 score is a scoring system used to estimate the amount of scarring in the liver. It is based on common clinical parameters (age, AST, ALT, and platelets) and has been shown to have the best diagnostic accuracy for advanced fibrosis when compared with other noninvasive clinical scores. Scores are categorized into low (\<1.30), indeterminate (1.30-2.67), or high (\>2.67) risk of fibrosis. The formula for Fib-4 is: (Age \[yr\] x AST \[U/L\]) / ((PLT \[109/L\]) x (ALT \[U/L\])½); there are no minimum or maximum values

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline To Week 12 And Week 36 In Fibrosis-4 (Fib-4) Score
Week 12
-0.03 score on a scale
Standard Deviation 0.386
0.05 score on a scale
Standard Deviation 0.374
Change From Baseline To Week 12 And Week 36 In Fibrosis-4 (Fib-4) Score
Week 36
0.02 score on a scale
Standard Deviation 0.356
0.07 score on a scale
Standard Deviation 0.436

SECONDARY outcome

Timeframe: Baseline up to Week 12

Thyrotropin (TSH) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Thyrotropin at Week 12
0.096 mIU/L
Standard Deviation 0.9136
-0.101 mIU/L
Standard Deviation 0.9742

SECONDARY outcome

Timeframe: Baseline up to Week 12

Total thyroxine (FT4) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Total Thyroxine at Week 12
-1.18 μg/dL
Standard Deviation 0.958
-0.07 μg/dL
Standard Deviation 0.726

SECONDARY outcome

Timeframe: Baseline up to Week 12

Free thyroxine (FT4) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Free Thyroxine at Week 12
-0.147 ng/dL
Standard Deviation 0.1154
0.001 ng/dL
Standard Deviation 0.0930

SECONDARY outcome

Timeframe: Baseline up to Week 12

Total Triiodothyronine (T3) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Total Triiodothyronine at Week 12
0.03 μg/L
Standard Deviation 0.189
0.02 μg/L
Standard Deviation 0.236

SECONDARY outcome

Timeframe: Baseline up to Week 12

Free triiodothyronine (T3) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Free Triiodothyronine at Week 12
0.05 ng/L
Standard Deviation 0.363
-0.02 ng/L
Standard Deviation 0.513

SECONDARY outcome

Timeframe: Baseline up to Week 12

Thyroxine Binding Globulin was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Thyroxine Binding Globulin at Week 12
-1.42 mg/L
Standard Deviation 3.859
0.39 mg/L
Standard Deviation 3.522

SECONDARY outcome

Timeframe: Baseline up to Week 12

Reverse Triiodothyronine (T3) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=78 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=38 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Reverse Triiodothyronine Globulin at Week 12
-5.22 ng/dL
Standard Deviation 5.255
-0.96 ng/dL
Standard Deviation 5.757

SECONDARY outcome

Timeframe: Baseline up to Week 36

Tyrotropin (TSH) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Thyrotropin at Week 36
0.034 mIU/L
Standard Deviation 0.9705
0.043 mIU/L
Standard Deviation 0.9481

SECONDARY outcome

Timeframe: Baseline up to Week 36

Total thyroxine (FT4), thyrotropin (TSH) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Total Thyroxine at Week 36
-1.10 μg/dL
Standard Deviation 1.013
-0.17 μg/dL
Standard Deviation 0.846

SECONDARY outcome

Timeframe: Baseline up to Week 36

Total free thyroxine (FT4) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Free Thyroxine Week 36
-0.138 ng/dL
Standard Deviation 0.1280
-0.007 ng/dL
Standard Deviation 0.1162

SECONDARY outcome

Timeframe: Baseline up to Week 36

Total triiodothyronine (T3) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Total Triiodothyronine at Week 36
0.02 μg/L
Standard Deviation 0.212
-0.2 μg/L
Standard Deviation 0.190

SECONDARY outcome

Timeframe: Baseline up to Week 36

Free triiodothyronine (T3) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Free Triiodothyronine at Week 36
0.02 ng/L
Standard Deviation 0.404
-0.02 ng/L
Standard Deviation 0.475

SECONDARY outcome

Timeframe: Baseline up to Week 36

Thyroxine-binding globulin (TBG) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Thyroxine-Binding Globulin at Week 36
-0.38 mg/L
Standard Deviation 4.411
1.35 mg/L
Standard Deviation 5.639

SECONDARY outcome

Timeframe: Baseline up to Week 36

Reverse triiodothyronine (T3) was assessed at each study visit.

Outcome measures

Outcome measures
Measure
MGL-3196
n=79 Participants
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo
n=39 Participants
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Change From Baseline of Reverse Triiodothyronine at Week 36
-4.41 ng/dL
Standard Deviation 5.582
-1.04 ng/dL
Standard Deviation 5.493

Adverse Events

MGL-3196 Main Study

Serious events: 5 serious events
Other events: 73 other events
Deaths: 0 deaths

Placebo Main Study

Serious events: 2 serious events
Other events: 28 other events
Deaths: 0 deaths

Extension Study

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
MGL-3196 Main Study
n=84 participants at risk
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo Main Study
n=41 participants at risk
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Extension Study
n=31 participants at risk
Patients randomized to MGL-3196 during the Main Study remained on the same dose of MGL-3196 or had a prespecified increase in dose upon entering the Extension Study. Former placebo patients were treated with 80 mg MGL-3196 initially, then up-titrated to 100 mg, remained on 80 mg, or had their dose reduced to 60 mg at Week 4 based on a PK sample obtained during Week 2.
Gastrointestinal disorders
Umbilical hernia
0.00%
0/84 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
2.4%
1/41 • Number of events 1 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Hepatobiliary disorders
Bile duct stones
0.00%
0/84 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
2.4%
1/41 • Number of events 1 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Infections and infestations
Clostridium difficile colitis
1.2%
1/84 • Number of events 1 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/41 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Injury, poisoning and procedural complications
Post procedural haemorrhage
1.2%
1/84 • Number of events 1 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/41 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Musculoskeletal and connective tissue disorders
Spinal column stenosis
1.2%
1/84 • Number of events 1 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/41 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Nervous system disorders
Cerebrovascular accident
1.2%
1/84 • Number of events 1 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/41 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Renal and urinary disorders
Ureterolithiasis
1.2%
1/84 • Number of events 1 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/41 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.

Other adverse events

Other adverse events
Measure
MGL-3196 Main Study
n=84 participants at risk
Randomized participants received MGL-3196 80 mg orally once daily in the morning for 36 weeks.
Placebo Main Study
n=41 participants at risk
Randomized participants received matching placebo orally once daily in the morning for 36 weeks.
Extension Study
n=31 participants at risk
Patients randomized to MGL-3196 during the Main Study remained on the same dose of MGL-3196 or had a prespecified increase in dose upon entering the Extension Study. Former placebo patients were treated with 80 mg MGL-3196 initially, then up-titrated to 100 mg, remained on 80 mg, or had their dose reduced to 60 mg at Week 4 based on a PK sample obtained during Week 2.
Gastrointestinal disorders
Diarrhoea
36.9%
31/84 • Number of events 49 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
9.8%
4/41 • Number of events 4 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
6.5%
2/31 • Number of events 6 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Gastrointestinal disorders
Nausea
20.2%
17/84 • Number of events 17 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
4.9%
2/41 • Number of events 2 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Gastrointestinal disorders
Abdominal Pain
7.1%
6/84 • Number of events 8 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
7.3%
3/41 • Number of events 3 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Gastrointestinal disorders
Abdominal Pain Upper
8.3%
7/84 • Number of events 9 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
2.4%
1/41 • Number of events 2 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Infections and infestations
Urinary tract infection
10.7%
9/84 • Number of events 10 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
9.8%
4/41 • Number of events 6 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Infections and infestations
Nasopharyngitis
6.0%
5/84 • Number of events 5 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
4.9%
2/41 • Number of events 3 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
9.7%
3/31 • Number of events 3 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Infections and infestations
Influenza
7.1%
6/84 • Number of events 6 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/41 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Musculoskeletal and connective tissue disorders
Arthralgia
6.0%
5/84 • Number of events 5 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
4.9%
2/41 • Number of events 3 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Musculoskeletal and connective tissue disorders
Back pain
7.1%
6/84 • Number of events 6 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
2.4%
1/41 • Number of events 1 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Nervous system disorders
Headache
13.1%
11/84 • Number of events 14 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
14.6%
6/41 • Number of events 7 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Nervous system disorders
Dizziness
7.1%
6/84 • Number of events 7 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
9.8%
4/41 • Number of events 4 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
General disorders
Fatigue
4.8%
4/84 • Number of events 5 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
9.8%
4/41 • Number of events 4 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Injury, poisoning and procedural complications
Accidental overdose
2.4%
2/84 • Number of events 2 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
7.3%
3/41 • Number of events 3 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Psychiatric disorders
Insomnia
6.0%
5/84 • Number of events 6 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
2.4%
1/41 • Number of events 1 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/31 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Gastrointestinal disorders
Abdominal Discomfort
0.00%
0/84 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/41 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
6.5%
2/31 • Number of events 2 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
Gastrointestinal disorders
Constipation
0.00%
0/84 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
0.00%
0/41 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.
6.5%
2/31 • Number of events 2 • Screening up to Week 36
Safety population: all randomized participants who received at least 1 dose of study drug. No summaries of AEs by dose level were planned or performed.

Additional Information

Thomas Hare

Madrigal Pharmaceuticals, Inc.

Phone: 267-268-7800

Results disclosure agreements

  • Principal investigator is a sponsor employee The only disclosure restriction on the PI is that the sponsor can review results communications prior to public release up to 45 days prior to submission and can embargo communications regarding study results for a period that is more than 90 days from the date that the communication is submitted to the sponsor for review. The sponsor cannot require changes to the communication and cannot unilaterally extend the embargo.
  • Publication restrictions are in place

Restriction type: OTHER