Trial Outcomes & Findings for Pilot Study of the Effect of Duavee® on Benign Breast Tissue Proliferation (NCT NCT02729701)

NCT ID: NCT02729701

Last Updated: 2022-03-09

Results Overview

Outcome will be based on three separate factors used collectively to determine feasibility of the study and consideration of a subsequent larger trial. These are accrual rate (ability to accrue target number of subjects in a timely manner), dropout rate (frequency of subjects who are compliant and complete the intervention) and change in Ki-67 (increase vs decrease in percent of cells stained positive in the majority of subjects). Should accrual be inadequate or too slow; or if retention is too low; then a decision would be made not to proceed to a larger trial. Also, if there is evidence of an increase in proliferation (Ki-67) then no further studies would be planned.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

28 participants

Primary outcome timeframe

6 Months

Results posted on

2022-03-09

Participant Flow

Women were recruited from the Breast Cancer Prevention Center. Accrual May 2016 - August 2018. 42 women were considered medically eligible and were screened by Random Periareolar Fine Needle Aspiration (RPFNA). 14 did not enter the trial for a variety of reasons.

Participant milestones

Participant milestones
Measure
Duavee
Participants asked to take Duavee for 6 months while on the study. Duavee: Once daily tablet of Duavee (Bazedoxifene (20 mg) plus conjugated estrogen (0.45 mg))
Overall Study
STARTED
28
Overall Study
COMPLETED
28
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Pilot Study of the Effect of Duavee® on Benign Breast Tissue Proliferation

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Duavee
n=28 Participants
Participants will be asked to take Duavee for 6 months while on the study. Duavee: Once daily tablet of Duavee (Bazedoxifene (20 mg) plus conjugated estrogen (0.45 mg))
Age, Continuous
53 years
n=99 Participants
Sex: Female, Male
Female
28 Participants
n=99 Participants
Sex: Female, Male
Male
0 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
27 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
1 Participants
n=99 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
Race (NIH/OMB)
Asian
0 Participants
n=99 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=99 Participants
Race (NIH/OMB)
White
27 Participants
n=99 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
Region of Enrollment
United States
28 participants
n=99 Participants
Proliferation Index (percent of breast epithelial cells that are Ki-67 immunocytochemistry positive)
1 percent
n=99 Participants
Fibroglandular Volume (FGV)
133 cm-squared
n=99 Participants

PRIMARY outcome

Timeframe: 6 Months

Population: potential subjects screened for eligibility.

Outcome will be based on three separate factors used collectively to determine feasibility of the study and consideration of a subsequent larger trial. These are accrual rate (ability to accrue target number of subjects in a timely manner), dropout rate (frequency of subjects who are compliant and complete the intervention) and change in Ki-67 (increase vs decrease in percent of cells stained positive in the majority of subjects). Should accrual be inadequate or too slow; or if retention is too low; then a decision would be made not to proceed to a larger trial. Also, if there is evidence of an increase in proliferation (Ki-67) then no further studies would be planned.

Outcome measures

Outcome measures
Measure
Duavee
n=42 Participants
Participants asked to take Duavee for 6 months while on the study. Duavee: Once daily tablet of Duavee (Bazedoxifene (20 mg) plus conjugated estrogen (0.45 mg))
Feasibility for a Larger Trial
Screened
42 Participants
Feasibility for a Larger Trial
Eligible
28 Participants
Feasibility for a Larger Trial
Complete
28 Participants

SECONDARY outcome

Timeframe: Change from Baseline to Month 6

Population: All subjects with baseline Ki-67 \>1%

Assessment by immunocytochemistry of the percent of breast epithelial cells staining positive. Per protocol, restricted to those subjects with baseline Ki-67 positivity \>1.0% but \< 4%

Outcome measures

Outcome measures
Measure
Duavee
n=15 Participants
Participants asked to take Duavee for 6 months while on the study. Duavee: Once daily tablet of Duavee (Bazedoxifene (20 mg) plus conjugated estrogen (0.45 mg))
Change in Ki-67
-1.2 change in percent positivity
Interval -3.2 to 3.2

SECONDARY outcome

Timeframe: Change from Baseline to Month 6

Population: Subjects with baseline and post-intervention mammograms assessed by Volpara

Assessment of mammograms for percent of breast defined as FGV by Volpara automated assessment.

Outcome measures

Outcome measures
Measure
Duavee
n=26 Participants
Participants asked to take Duavee for 6 months while on the study. Duavee: Once daily tablet of Duavee (Bazedoxifene (20 mg) plus conjugated estrogen (0.45 mg))
Change in Fibroglandular Volume (FGV)
-12 cm-squared
Interval -204.0 to 62.0

SECONDARY outcome

Timeframe: Change from Baseline to Month 6

Population: All subjects enrolled and completed

Assessment by Dual Energy X-ray Absorptivity (DEXA)

Outcome measures

Outcome measures
Measure
Duavee
n=28 Participants
Participants asked to take Duavee for 6 months while on the study. Duavee: Once daily tablet of Duavee (Bazedoxifene (20 mg) plus conjugated estrogen (0.45 mg))
Change in Body Composition (Total Mass)
0.9 kg
Interval -11.8 to 10.4

SECONDARY outcome

Timeframe: Month 6

Population: With residual plasma available for analysis

Assessment of concentration of bazedoxifene in plasma by High-performance liquid chromatography (HPLC)

Outcome measures

Outcome measures
Measure
Duavee
n=25 Participants
Participants asked to take Duavee for 6 months while on the study. Duavee: Once daily tablet of Duavee (Bazedoxifene (20 mg) plus conjugated estrogen (0.45 mg))
Levels of Bazedoxifene in the Blood
1.83 ng/ml
Interval 0.004 to 7.86

Adverse Events

Duavee

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Bruce F. Kimler, Ph.D.

University of Kansas Medical Center

Phone: 913-205-6382

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place