Natural History Study of Patients With Leber Congenital Amaurosis Associated With Mutations in RPE65
NCT02714816 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 37
Last updated 2023-08-14
Summary
MGT005 is a natural history study to collect longitudinal prospective data from patients with Leber Congenital Amaurosis associated with defects in RPE65.
Conditions
- Leber Congenital Amaurosis
Sponsors & Collaborators
-
MeiraGTx UK II Ltd
lead INDUSTRY
Principal Investigators
-
Michel Michealides, Prof · UCL/Moorfileds
Eligibility
- Min Age
- 3 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2016-04-30
- Primary Completion
- 2023-07-22
- Completion
- 2023-07-22
Countries
- United States
- United Kingdom
Study Locations
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