Observational Study of Outcomes in Cystic Fibrosis Patients With Selected Gating Mutations on a CFTR Allele (The VOCAL Study)
NCT02445053 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 75
Last updated 2020-11-13
Summary
To describe the effectiveness of Kalydeco® treatment in patients with cystic fibrosis (CF) who have 1 of 8 non G551D gating CFTR mutations (G178R, S549N, S549R, G551S, G1244E, S1251N, S1255P, or G1349D).
Conditions
Interventions
- DRUG
-
ivacaftor
Sponsors & Collaborators
-
Vertex Pharmaceuticals Incorporated
lead INDUSTRY
Eligibility
- Min Age
- 6 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2015-04-30
- Primary Completion
- 2020-10-31
- Completion
- 2020-10-31
Countries
- Italy
- Netherlands
- United Kingdom
Study Locations
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