Trial Outcomes & Findings for DOTAREM Pharmacokinetics and Safety Study in Pediatric Subjects Aged < 2 Years (NCT NCT02411201)

NCT ID: NCT02411201

Last Updated: 2017-03-09

Results Overview

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Area under the curve was determined from typical and individual DOTAREM concentration-time profiles.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

51 participants

Primary outcome timeframe

Blood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Results posted on

2017-03-09

Participant Flow

A total of 51 children aged less than 2 years were recruited in 4 countries: Austria, France, Hungary and Poland.

Participant milestones

Participant milestones
Measure
DOTAREM
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Overall Study
STARTED
51
Overall Study
COMPLETED
45
Overall Study
NOT COMPLETED
6

Reasons for withdrawal

Reasons for withdrawal
Measure
DOTAREM
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Overall Study
Adverse Event
2
Overall Study
Withdrawal by Subject
2
Overall Study
Age group completed
2

Baseline Characteristics

DOTAREM Pharmacokinetics and Safety Study in Pediatric Subjects Aged < 2 Years

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
DOTAREM
n=45 Participants
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Age, Continuous
9.9 months
STANDARD_DEVIATION 7.4 • n=39 Participants
Age, Customized
<1 month
5 Participants
n=39 Participants
Age, Customized
1 to 3 months
9 Participants
n=39 Participants
Age, Customized
>3 months to <24 months
31 Participants
n=39 Participants
Sex: Female, Male
Female
23 Participants
n=39 Participants
Sex: Female, Male
Male
22 Participants
n=39 Participants
Region of Enrollment
Austria
3 participants
n=39 Participants
Region of Enrollment
Hungary
9 participants
n=39 Participants
Region of Enrollment
Poland
29 participants
n=39 Participants
Region of Enrollment
France
4 participants
n=39 Participants

PRIMARY outcome

Timeframe: Blood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Population: Among the 45 subjects who received one injection of DOTAREM, all had at least one blood sample available for pharmacokinetics.

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Area under the curve was determined from typical and individual DOTAREM concentration-time profiles.

Outcome measures

Outcome measures
Measure
DOTAREM
n=45 Participants
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Pre- + Post-contrast
Lesion visualization was assessed after DOTAREM injection
Area Under the Curve of DOTAREM in Plasma
1591.1 hour.µmol/L
Interval 981.43 to 2841.0

PRIMARY outcome

Timeframe: Blood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Population: Among the 45 subjects who received one injection of DOTAREM, all had at least one blood sample available for pharmacokinetics.

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Rate constant of the terminal phase was determined from typical and individual DOTAREM concentration-time profiles.

Outcome measures

Outcome measures
Measure
DOTAREM
n=45 Participants
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Pre- + Post-contrast
Lesion visualization was assessed after DOTAREM injection
Rate Constant of the Terminal Phase of DOTAREM
0.5117 hour-1
Interval 0.2288 to 0.7824

PRIMARY outcome

Timeframe: Blood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Population: Among the 45 subjects who received one injection of DOTAREM, all had at least one blood sample available for pharmacokinetics.

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Terminal elimination half-life was determined from typical and individual DOTAREM concentration-time profiles.

Outcome measures

Outcome measures
Measure
DOTAREM
n=45 Participants
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Pre- + Post-contrast
Lesion visualization was assessed after DOTAREM injection
Terminal Elimination Half-life of DOTAREM From Plasma
1.3545 hour
Interval 0.8859 to 3.0291

PRIMARY outcome

Timeframe: Blood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Population: Among the 45 subjects who received one injection of DOTAREM, all had at least one blood sample available for pharmacokinetics.

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Total clearance was determined from typical and individual DOTAREM concentration-time profiles.

Outcome measures

Outcome measures
Measure
DOTAREM
n=45 Participants
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Pre- + Post-contrast
Lesion visualization was assessed after DOTAREM injection
Total Clearance of DOTAREM From Plasma
0.0602 L/hour per kg
Interval 0.0352 to 0.1019

PRIMARY outcome

Timeframe: Blood samples were collected during 3 time windows: 15 min to 60 min, 2 hours to 4 hours and 6 hours to 8 hours post-injection

Population: Among the 45 subjects who received one injection of DOTAREM, all had at least one blood sample available for pharmacokinetics.

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method. Volume of distribution at steady state was determined from typical and individual DOTAREM concentration-time profiles.

Outcome measures

Outcome measures
Measure
DOTAREM
n=45 Participants
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Pre- + Post-contrast
Lesion visualization was assessed after DOTAREM injection
Volume of Distribution of DOTAREM at Steady State
0.0473 L/kg
Interval 0.0273 to 0.1597

SECONDARY outcome

Timeframe: at 10 and 20 min post-injection

Population: Among the 45 subjects who received one injection of DOTAREM, all had at least one blood sample available for pharmacokinetics.

Pharmacokinetics interpretation was performed using a pharmacokinetic population modelling approach. DOTAREM concentrations in plasma were analyzed using a validated LC-MS/MS method.

Outcome measures

Outcome measures
Measure
DOTAREM
n=45 Participants
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Pre- + Post-contrast
Lesion visualization was assessed after DOTAREM injection
Simulated Plasma Concentration of DOTAREM
Simulated concentration at 10 min
320.92 µmol/L
Interval 45.223 to 2857.0
Simulated Plasma Concentration of DOTAREM
Simulated concentration at 20 min
275.67 µmol/L
Interval 47.048 to 1565.1

SECONDARY outcome

Timeframe: Pre-injection and post-injection (estimated between 5 and 20 minutes after injection)

Population: Lesion visualization was evaluated in 28 subjects who underwent contrast-enhanced MRI for central nervous system indication.

Lesion visualization was assessed on up to five most representative lesions per subject based on scoring of 3 co-endpoints: * border delineation (based on a 3-point scale where 1=none; 2=moderate and 3=clear and complete) * internal morphology (based on a 3-point scale where 1=poorly visible; 2=moderately visible and 3=sufficiently visible) * contrast enhancement (based on a 3-point scale where 1=none; 2=weak and 3=clear and bright) For each co-endpoint, a sum of scores was calculated at subject level as follows: sum of scores = score of the lesion 1 (+ score of the lesion 2 + score of the lesion 3 + score of the lesion 4 + score of the lesion 5, when applicable)

Outcome measures

Outcome measures
Measure
DOTAREM
n=28 Participants
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Pre- + Post-contrast
n=28 Participants
Lesion visualization was assessed after DOTAREM injection
MRI Lesion Visualization at Subject Level
Sum of scores of lesion border delineation
4.3 units on a scale
Standard Deviation 3.7
5.1 units on a scale
Standard Deviation 4.0
MRI Lesion Visualization at Subject Level
Sum of scores of internal morphology
4.3 units on a scale
Standard Deviation 3.9
5.2 units on a scale
Standard Deviation 4.3
MRI Lesion Visualization at Subject Level
Sum of scores of contrast enhancement
1.9 units on a scale
Standard Deviation 1.5
5.0 units on a scale
Standard Deviation 4.5

Adverse Events

DOTAREM

Serious events: 1 serious events
Other events: 12 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
DOTAREM
n=45 participants at risk
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
Blood and lymphatic system disorders
Anaemia
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
General disorders
Pyrexia
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Infections and infestations
Upper respiratory tract infection
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)

Other adverse events

Other adverse events
Measure
DOTAREM
n=45 participants at risk
Subjects receiving a single intravenous injection of 0.1 mmol/kg body weight of DOTAREM
General disorders
Pyrexia
11.1%
5/45 • Number of events 5 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
General disorders
Device difficult to use
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
General disorders
Fatigue
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Infections and infestations
Bronchitis
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Infections and infestations
Infection
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Infections and infestations
Nasopharyngitis
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Infections and infestations
Rhinitis
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Infections and infestations
Tonsillitis
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Infections and infestations
Urinary tract infection
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Gastrointestinal disorders
Abdominal pain
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Gastrointestinal disorders
Diarrhoea
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Gastrointestinal disorders
Vomiting
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Blood and lymphatic system disorders
Leukopenia
4.4%
2/45 • Number of events 2 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Blood and lymphatic system disorders
Thrombocytopenia
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Nervous system disorders
Tremor
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Respiratory, thoracic and mediastinal disorders
Cough
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Skin and subcutaneous tissue disorders
Rash
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)
Gastrointestinal disorders
Nausea
2.2%
1/45 • Number of events 1 • Adverse Events were collected from informed consent signature to the end of the study (7+/-1 day after DOTAREM administration)

Additional Information

Corinne Dubourdieu, PharmD, Head of Clinical Projects and Medical Writing

Guerbet

Phone: +33 (0) 1 45 91 50 00

Results disclosure agreements

  • Principal investigator is a sponsor employee All written or oral papers and publications must have the joint agreement of the investigator and Guerbet. The Investigator shall not use the sponsor's name in any publication without the prior permission of Guerbet. Each investigator agrees not to publish/present the evaluation of the main criterion involving only the patients he/she has included. Any abstract project will be first submitted to Guerbet at least 10 working days before submission to the congress scientific committee.
  • Publication restrictions are in place

Restriction type: OTHER