Trial Outcomes & Findings for A Biomarker Study in Patients Getting Regorafenib for Metastatic Colorectal Cancer (NCT NCT02402036)

NCT ID: NCT02402036

Last Updated: 2019-01-29

Results Overview

Serum microRNAs will be quantified using miScript MiRNA PCR arrays

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

10 participants

Primary outcome timeframe

2 years

Results posted on

2019-01-29

Participant Flow

Participant milestones

Participant milestones
Measure
Regorafenib
Regorafenib 120 mg orally daily for 21 days out of a 28 day cycle Regorafenib: Regorafenib orally for 21 days every 28 day cycle
Overall Study
STARTED
10
Overall Study
COMPLETED
10
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

A Biomarker Study in Patients Getting Regorafenib for Metastatic Colorectal Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Regorafenib
n=10 Participants
Regorafenib 120 mg orally daily for 21 days out of a 28 day cycle Regorafenib: Regorafenib orally for 21 days every 28 day cycle
Age, Categorical
<=18 years
0 Participants
n=99 Participants
Age, Categorical
Between 18 and 65 years
8 Participants
n=99 Participants
Age, Categorical
>=65 years
2 Participants
n=99 Participants
Sex: Female, Male
Female
3 Participants
n=99 Participants
Sex: Female, Male
Male
7 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
7 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
3 Participants
n=99 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
Race (NIH/OMB)
Asian
0 Participants
n=99 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
Race (NIH/OMB)
Black or African American
5 Participants
n=99 Participants
Race (NIH/OMB)
White
2 Participants
n=99 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
Race (NIH/OMB)
Unknown or Not Reported
3 Participants
n=99 Participants
Region of Enrollment
United States
10 participants
n=99 Participants

PRIMARY outcome

Timeframe: 2 years

Population: Due to issues with recruitment and the principal investigator leaving the institution, no analysis of the collected samples was performed.

Serum microRNAs will be quantified using miScript MiRNA PCR arrays

Outcome measures

Outcome data not reported

Adverse Events

Regorafenib

Serious events: 5 serious events
Other events: 10 other events
Deaths: 1 deaths

Serious adverse events

Serious adverse events
Measure
Regorafenib
n=10 participants at risk
Regorafenib 120 mg orally daily for 21 days out of a 28 day cycle Regorafenib: Regorafenib orally for 21 days every 28 day cycle
General disorders
Abdominal Pain
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Blood and lymphatic system disorders
Anemia
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Gastrointestinal disorders
Colonic Obstruction
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Respiratory, thoracic and mediastinal disorders
Dyspnea
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Skin and subcutaneous tissue disorders
Erythema multiforme
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Hyponatremia
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Gastrointestinal disorders
Mucositis oral
20.0%
2/10 • Number of events 2 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Pain
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.

Other adverse events

Other adverse events
Measure
Regorafenib
n=10 participants at risk
Regorafenib 120 mg orally daily for 21 days out of a 28 day cycle Regorafenib: Regorafenib orally for 21 days every 28 day cycle
General disorders
Abdominal Pain
50.0%
5/10 • Number of events 7 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Alkaline phosphatase increased
30.0%
3/10 • Number of events 3 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Blood and lymphatic system disorders
Anemia
20.0%
2/10 • Number of events 3 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Hepatobiliary disorders
Aspartate aminotransferase increased
30.0%
3/10 • Number of events 5 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Gastrointestinal disorders
Colonic obstruction
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Renal and urinary disorders
Creatinine increased
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Hepatobiliary disorders
Elevated total bilirrubin
20.0%
2/10 • Number of events 3 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Immune system disorders
High Neutrophils
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Hepatobiliary disorders
Hypoalbuminemia
40.0%
4/10 • Number of events 7 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Hyponatremia
20.0%
2/10 • Number of events 3 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Blood and lymphatic system disorders
PT increased
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Immune system disorders
WBC increased
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Hepatobiliary disorders
Alanine aminotransferase increased
20.0%
2/10 • Number of events 3 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Fatigue
60.0%
6/10 • Number of events 7 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Skin and subcutaneous tissue disorders
Hand and foot syndrome
50.0%
5/10 • Number of events 8 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Metabolism and nutrition disorders
Weight loss
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Chills
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Dehydration
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Gastrointestinal disorders
Diarrhea
30.0%
3/10 • Number of events 3 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Gastrointestinal disorders
Constipation
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Skin and subcutaneous tissue disorders
Erythema multiforme
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Fever
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Gastrointestinal disorders
Gastrointestinal disorders - Other, specify
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Nervous system disorders
Headache
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Hoarseness
20.0%
2/10 • Number of events 2 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Cardiac disorders
Hypertension
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Immune system disorders
Lymphocyte count decreased
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Blood and lymphatic system disorders
Nasal bleed
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Nausea
20.0%
2/10 • Number of events 2 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Pain
30.0%
3/10 • Number of events 6 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Respiratory, thoracic and mediastinal disorders
Sinusitis
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Musculoskeletal and connective tissue disorders
Back pain
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Nasal congestion
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Respiratory, thoracic and mediastinal disorders
Cough
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
General disorders
Hot flashes
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Skin and subcutaneous tissue disorders
Pruritus
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Musculoskeletal and connective tissue disorders
Tooth development disorder
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Gastrointestinal disorders
Abdominal distension
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Musculoskeletal and connective tissue disorders
Arthralgia
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.
Respiratory, thoracic and mediastinal disorders
Pleural effusion
10.0%
1/10 • Number of events 1 • Adverse events were collected for each subject from the time they signed the informed consent until study completion up to 1 year of treatment and safety follow-up. The period of collection depended on the length of the treatment period.

Additional Information

Mohamed Salem, MD

Levine Cancer Institute-Concord

Phone: 704-403-1370

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place