Emergency Administration of EPI-743 to a Single Patient With Leber's Hereditary Optic Neuropathy [LHON]
NCT02300753 · Status: NO_LONGER_AVAILABLE · Type: EXPANDED_ACCESS
Last updated 2014-11-25
Summary
Expanded access Protocol to treat LHON subjects with EPI743
Conditions
- Leber's Hereditary Optic Neuropathy
Interventions
- DRUG
-
EPI-743
EPI-743 is a quinone oxidation product of alpha-tocotrienol
Sponsors & Collaborators
-
Edison Pharmaceuticals Inc
lead INDUSTRY
Eligibility
- Min Age
- 8 Years
- Max Age
- 65 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
Countries
- United States
Study Locations
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