Trial Outcomes & Findings for Regorafenib Second Line Treatment of Metastatic or Advanced Upper GI Cancers (NCT NCT02241720)

NCT ID: NCT02241720

Last Updated: 2018-01-11

Results Overview

Patients had disease assessed by CT scans. Stable Disease is defined by any response better than Progression as defined by RECIST 1.1. Progression is defined as a 20% increase in the sum of the longest diameter of target lesions, or a measurable increase in a non-target lesion, or the appearance of new lesions.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

5 participants

Primary outcome timeframe

5 months - 3 months treatment and 8 weeks post end of treatment visit

Results posted on

2018-01-11

Participant Flow

Participant milestones

Participant milestones
Measure
Regorafenib Treatment
160 mg regorafenib by mouth once daily for 3 weeks of every 4 week cycle
Overall Study
STARTED
5
Overall Study
COMPLETED
1
Overall Study
NOT COMPLETED
4

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Regorafenib Second Line Treatment of Metastatic or Advanced Upper GI Cancers

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Regorafenib Treatment
n=5 Participants
regorafenib
Age, Categorical
<=18 years
0 Participants
n=99 Participants
Age, Categorical
Between 18 and 65 years
2 Participants
n=99 Participants
Age, Categorical
>=65 years
3 Participants
n=99 Participants
Sex: Female, Male
Female
0 Participants
n=99 Participants
Sex: Female, Male
Male
5 Participants
n=99 Participants
Region of Enrollment
United States
5 Participants
n=99 Participants

PRIMARY outcome

Timeframe: 5 months - 3 months treatment and 8 weeks post end of treatment visit

Population: 3 subjects did not complete an 8 week EOT visit for: Death, Patient W/D, AE.

Patients had disease assessed by CT scans. Stable Disease is defined by any response better than Progression as defined by RECIST 1.1. Progression is defined as a 20% increase in the sum of the longest diameter of target lesions, or a measurable increase in a non-target lesion, or the appearance of new lesions.

Outcome measures

Outcome measures
Measure
Regorafenib Treatment
n=2 Participants
regorafenib
Number of Participants With Stable Disease at Eight Weeks Post-Treatment
2 Participants

Adverse Events

Regorafenib Treatment

Serious events: 3 serious events
Other events: 5 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Regorafenib Treatment
n=5 participants at risk
regorafenib
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Disease Progression
20.0%
1/5 • Number of events 1
Infections and infestations
Lung infection
20.0%
1/5 • Number of events 1
Cardiac disorders
heart failure
20.0%
1/5 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Tracheoesophageal fistula
20.0%
1/5 • Number of events 1

Other adverse events

Other adverse events
Measure
Regorafenib Treatment
n=5 participants at risk
regorafenib
General disorders
Fatigue
60.0%
3/5 • Number of events 3
Vascular disorders
Hypertension
80.0%
4/5 • Number of events 4
Metabolism and nutrition disorders
deydration
40.0%
2/5 • Number of events 2
Gastrointestinal disorders
Abdominal pain
20.0%
1/5 • Number of events 2
Investigations
hyperbilirubinemia
20.0%
1/5 • Number of events 1
Skin and subcutaneous tissue disorders
maculopapular rash
20.0%
1/5 • Number of events 2
Blood and lymphatic system disorders
anemia
20.0%
1/5 • Number of events 1
Endocrine disorders
hypothyroidism
20.0%
1/5 • Number of events 1
Gastrointestinal disorders
dysphagia
40.0%
2/5 • Number of events 2
Nervous system disorders
headache
20.0%
1/5 • Number of events 1
Gastrointestinal disorders
oral pain
20.0%
1/5 • Number of events 1
Gastrointestinal disorders
mucositis oral
40.0%
2/5 • Number of events 2
Nervous system disorders
syncope
20.0%
1/5 • Number of events 1
Vascular disorders
hypotension
20.0%
1/5 • Number of events 1
Respiratory, thoracic and mediastinal disorders
voice alteration
20.0%
1/5 • Number of events 1
Respiratory, thoracic and mediastinal disorders
aspiration
20.0%
1/5 • Number of events 1
Skin and subcutaneous tissue disorders
Palmar-plantar erythrodysesthesia syndrome
20.0%
1/5 • Number of events 1

Additional Information

Kimberlee Taylor

Huntsman Cancer Institute

Phone: 801-213-5673

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place