Phase 2 Study of EPI-743 in Children With Pearson Syndrome
NCT02104336 · Status: TERMINATED · Phase: PHASE2 · Type: INTERVENTIONAL · Enrollment: 2
Last updated 2020-11-18
Summary
Treatment of Pediatric Subjects with Pearson syndrome
Conditions
- Pearson Syndrome
Interventions
- DRUG
-
EPI-743
EPI-743 is the quinone oxidation product of alpha-tocotrienol
Sponsors & Collaborators
-
Edison Pharmaceuticals Inc
lead INDUSTRY
Principal Investigators
-
Matthew Klein, MD, FACS · Edison Pharmaceuticals
Study Design
- Allocation
- NA
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Max Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2014-08-31
- Primary Completion
- 2015-11-30
- Completion
- 2016-02-29
Countries
- United States
Study Locations
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