Trial Outcomes & Findings for A Pilot Study of Dociparstat Sodium (ODSH) in Acute Myeloid Leukemia (NCT NCT02056782)

NCT ID: NCT02056782

Last Updated: 2023-02-21

Results Overview

A primary endpoint of this study was evidence of an effect of dociparstat on transfusion independent platelet recovery time. The time (days) to transfusion-independent platelet recovery will be defined as the number of days from the first day of chemotherapy until the first of 5 consecutive days with platelet counts values ≥ 20,000/μL and ≥ 50,000/μL without a platelet transfusion.

Recruitment status

COMPLETED

Study phase

PHASE1

Target enrollment

12 participants

Primary outcome timeframe

Day 1 to Day 35 (35 days)

Results posted on

2023-02-21

Participant Flow

Participant milestones

Participant milestones
Measure
Dociparstat
Subjects received the following dosing regimen: * Cytarabine (100 mg/m2/day) via continuous intravenous (IV) infusion 24 hours daily for 7 days. * Idarubicin (12 mg/m2/day) IV on Days 1, 2, and 3. * Dociparstat (4 mg/kg) given over 5 minutes IV, immediately after the idarubicin dose on Day 1, followed by a continuous IV infusion (0.25 mg/kg/hr for 24 hours daily) for a total of 7 days.
Overall Study
STARTED
12
Overall Study
COMPLETED
10
Overall Study
NOT COMPLETED
2

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

A Pilot Study of Dociparstat Sodium (ODSH) in Acute Myeloid Leukemia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Dociparstat
n=12 Participants
Subjects received the following dosing regimen: * Cytarabine (100 mg/m2/day) via continuous intravenous (IV) infusion 24 hours daily for 7 days. * Idarubicin (12 mg/m2/day) IV on Days 1, 2, and 3. * Dociparstat (4 mg/kg) given over 5 minutes IV, immediately after the idarubicin dose on Day 1, followed by a continuous IV infusion (0.25 mg/kg/hr for 24 hours daily) for a total of 7 days.
Age, Continuous
54 years
n=99 Participants
Sex: Female, Male
Female
3 Participants
n=99 Participants
Sex: Female, Male
Male
9 Participants
n=99 Participants
Region of Enrollment
United States
12 participants
n=99 Participants

PRIMARY outcome

Timeframe: Day 1 to Day 35 (35 days)

Population: Count recovery was analyzed after induction on the 10 subjects who received a full induction cycle.

A primary endpoint of this study was evidence of an effect of dociparstat on transfusion independent platelet recovery time. The time (days) to transfusion-independent platelet recovery will be defined as the number of days from the first day of chemotherapy until the first of 5 consecutive days with platelet counts values ≥ 20,000/μL and ≥ 50,000/μL without a platelet transfusion.

Outcome measures

Outcome measures
Measure
Dociparstat
n=10 Participants
Subjects received the following dosing regimen: * Cytarabine (100 mg/m2/day) via continuous intravenous (IV) infusion 24 hours daily for 7 days. * Idarubicin (12 mg/m2/day) IV on Days 1, 2, and 3. * Dociparstat (4 mg/kg) given over 5 minutes IV, immediately after the idarubicin dose on Day 1, followed by a continuous IV infusion (0.25 mg/kg/hr for 24 hours daily) for a total of 7 days.
Time (Days) to Transfusion-independent Platelet Recovery (Platelet Counts Values ≥ 20,000/μL and ≥ 50,000/μL Without a Platelet Transfusion)
Platelet count of ≥20,000/µL
21.3 days
Interval 18.0 to 22.0
Time (Days) to Transfusion-independent Platelet Recovery (Platelet Counts Values ≥ 20,000/μL and ≥ 50,000/μL Without a Platelet Transfusion)
Platelet count of ≥50,000/µL
23.1 days
Interval 19.0 to 25.0

SECONDARY outcome

Timeframe: Day 1 to Day 35 (35 days)

Population: All randomized subjects were included in this analysis, including the 2 subjects who did not complete induction.

A secondary endpoint of this study was to determine whether there was preliminary evidence of an effect of dociparstat on remission rate following cytarabine and idarubicin induction in acute myeloid leukemia (AML) patients, which included complete remission (CR) rate (with neutrophil and platelet count recovery) after the first induction cycle. Morphologic CR was defined as absolute neutrophil count (ANC) \>1000/μL, platelet count \>100,000/μL, \<5% bone marrow blasts, no Auer rods, and no evidence of extramedullary disease.

Outcome measures

Outcome measures
Measure
Dociparstat
n=12 Participants
Subjects received the following dosing regimen: * Cytarabine (100 mg/m2/day) via continuous intravenous (IV) infusion 24 hours daily for 7 days. * Idarubicin (12 mg/m2/day) IV on Days 1, 2, and 3. * Dociparstat (4 mg/kg) given over 5 minutes IV, immediately after the idarubicin dose on Day 1, followed by a continuous IV infusion (0.25 mg/kg/hr for 24 hours daily) for a total of 7 days.
Number of Subjects Who Achieved a Morphologic Complete Remission
11 Participants

Adverse Events

Dociparstat

Serious events: 5 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Dociparstat
n=12 participants at risk
Subjects received the following dosing regimen: * Cytarabine (100 mg/m2/day) via continuous intravenous (IV) infusion 24 hours daily for 7 days. * Idarubicin (12 mg/m2/day) IV on Days 1, 2, and 3. * Dociparstat (4 mg/kg) given over 5 minutes IV, immediately after the idarubicin dose on Day 1, followed by a continuous IV infusion (0.25 mg/kg/hr for 24 hours daily) for a total of 7 days.
Infections and infestations
Sepsis
16.7%
2/12 • Number of events 2
Blood and lymphatic system disorders
Febrile neutropenia
8.3%
1/12 • Number of events 1
Infections and infestations
Perirectal abscess
8.3%
1/12 • Number of events 1
Renal and urinary disorders
Acute tubular necrosis
8.3%
1/12 • Number of events 1
Immune system disorders
angioedema
8.3%
1/12 • Number of events 1

Other adverse events

Adverse event data not reported

Additional Information

CBertrand

Cantex

Phone: 954-315-3660

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place