Treatment of TNNT1-Myopathy With L-Tyrosine.
NCT02035501 · Status: UNKNOWN · Phase: PHASE2 · Type: INTERVENTIONAL · Enrollment: 10
Last updated 2014-01-14
Summary
The purpose of the study is to investigate if treatment with L-Tyrosine improves selected outcome measures of TNNT1 myopathy.
Conditions
- Nemaline Myopathy
Interventions
- DRUG
-
L-Tyrosine
- DRUG
Sponsors & Collaborators
-
Hadassah Medical Organization
lead OTHER
Study Design
- Allocation
- RANDOMIZED
- Purpose
- TREATMENT
- Masking
- QUADRUPLE
- Model
- CROSSOVER
Eligibility
- Max Age
- 20 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2014-01-31
- Primary Completion
- 2015-01-31
Countries
- Israel
Study Locations
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