Trial Outcomes & Findings for Biomarkers in First Episode Schizophrenia (NCT NCT02033382)

NCT ID: NCT02033382

Last Updated: 2021-01-14

Results Overview

Compare biomarkers for inflammation, BDNF, oxidative stress, glucocorticoids and folate/methylation status in medication-naïve schizophrenia/schizophreniform subjects and matched healthy controls to identify illness-related factors.

Recruitment status

COMPLETED

Target enrollment

165 participants

Primary outcome timeframe

Baseline

Results posted on

2021-01-14

Participant Flow

Participant milestones

Participant milestones
Measure
Healthy Controls
Age and gender matched healthy controls
Patients
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Overall Study
STARTED
83
82
Overall Study
COMPLETED
32
36
Overall Study
NOT COMPLETED
51
46

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Biomarkers in First Episode Schizophrenia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Healthy Controls
n=73 Participants
Age and gender matched healthy controls
Patients
n=79 Participants
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Total
n=152 Participants
Total of all reporting groups
Age, Continuous
23.86 years
STANDARD_DEVIATION 6.40 • n=39 Participants
25.19 years
STANDARD_DEVIATION 7.39 • n=41 Participants
24.56 years
STANDARD_DEVIATION 6.95 • n=35 Participants
Sex: Female, Male
Female
40 Participants
n=39 Participants
40 Participants
n=41 Participants
80 Participants
n=35 Participants
Sex: Female, Male
Male
33 Participants
n=39 Participants
39 Participants
n=41 Participants
72 Participants
n=35 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=39 Participants
0 Participants
n=41 Participants
0 Participants
n=35 Participants
Race (NIH/OMB)
Asian
73 Participants
n=39 Participants
74 Participants
n=41 Participants
147 Participants
n=35 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=39 Participants
0 Participants
n=41 Participants
0 Participants
n=35 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=39 Participants
3 Participants
n=41 Participants
3 Participants
n=35 Participants
Race (NIH/OMB)
White
0 Participants
n=39 Participants
2 Participants
n=41 Participants
2 Participants
n=35 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=39 Participants
0 Participants
n=41 Participants
0 Participants
n=35 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=39 Participants
0 Participants
n=41 Participants
0 Participants
n=35 Participants
Region of Enrollment
China
73 participants
n=39 Participants
79 participants
n=41 Participants
152 participants
n=35 Participants

PRIMARY outcome

Timeframe: Baseline

Population: Not all biomarkers were available for analysis for all subjects.

Compare biomarkers for inflammation, BDNF, oxidative stress, glucocorticoids and folate/methylation status in medication-naïve schizophrenia/schizophreniform subjects and matched healthy controls to identify illness-related factors.

Outcome measures

Outcome measures
Measure
Healthy Controls
n=62 Participants
Age and gender matched healthy controls
Patients
n=69 Participants
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Biomarkers
Interleukin 1B
76.77 pg/mL
Interval 44.41 to 225.11
68.82 pg/mL
Interval 35.35 to 166.58
Biomarkers
Interleukin 8
63.41 pg/mL
Interval 50.77 to 82.46
71.30 pg/mL
Interval 49.79 to 83.26
Biomarkers
Tumor Necrosis Factor
92.03 pg/mL
Interval 74.28 to 103.94
93.60 pg/mL
Interval 76.02 to 105.44
Biomarkers
Interferon gamma
88.96 pg/mL
Interval 64.69 to 131.47
89.42 pg/mL
Interval 70.87 to 113.86
Biomarkers
Aspartate
102.32 pg/mL
Interval 79.33 to 141.65
134.32 pg/mL
Interval 86.67 to 198.31
Biomarkers
Lactate
13.28 pg/mL
Interval 9.83 to 17.75
15.08 pg/mL
Interval 11.27 to 20.34
Biomarkers
BDNF
287.37 pg/mL
Interval 145.99 to 722.44
340.83 pg/mL
Interval 142.52 to 340.83
Biomarkers
Thioredoxin
492.33 pg/mL
Interval 324.17 to 637.67
420.17 pg/mL
Interval 323.58 to 609.5
Biomarkers
S100B
130.44 pg/mL
Interval 61.14 to 265.52
125.13 pg/mL
Interval 69.76 to 211.93
Biomarkers
C-Reactive Protein
7610.07 pg/mL
Interval 6937.9 to 9025.92
7631.41 pg/mL
Interval 6778.62 to 9456.46
Biomarkers
Glutamate
105.00 pg/mL
Interval 92.0 to 121.6
111.00 pg/mL
Interval 98.2 to 128.0
Biomarkers
Homocysteine
4.79 pg/mL
Interval 4.44 to 5.38
4.83 pg/mL
Interval 4.53 to 5.26

PRIMARY outcome

Timeframe: Baseline and week 8

Population: Analysis was done for first episode participants who completed both Baseline and Week 8 only.

Compare biomarkers at baseline and after 8 weeks of risperidone treatment in medication-naïve schizophrenia/schizophreniform subjects to identify treatment-related factors. Since Blood and Saliva was only collected from First Episode participants (FEP) at week 8 (not from healthy controls) these results only report the baseline and week 8 biomarker levels for FEP participants who completed week 8.

Outcome measures

Outcome measures
Measure
Healthy Controls
n=29 Participants
Age and gender matched healthy controls
Patients
n=29 Participants
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Salivary Cortisol Levels
C-reactive protein
7541.41 pg/mL
Interval 6647.32 to 9445.12
7627.60 pg/mL
Interval 6708.99 to 9474.72
Salivary Cortisol Levels
Interleukin 1B
68.81 pg/mL
Interval 34.82 to 153.33
57.01 pg/mL
Interval 28.18 to 168.11
Salivary Cortisol Levels
Interleukin 8
74.34 pg/mL
Interval 50.02 to 93.98
65.79 pg/mL
Interval 51.16 to 82.38
Salivary Cortisol Levels
Interferon gamma
95.26 pg/mL
Interval 73.44 to 117.9
98.14 pg/mL
Interval 61.71 to 124.71
Salivary Cortisol Levels
Tumor necrosis factor
93.60 pg/mL
Interval 75.75 to 107.69
89.45 pg/mL
Interval 71.25 to 109.15
Salivary Cortisol Levels
Aspartate
3.71 pg/mL
Interval 2.6 to 4.55
4.75 pg/mL
Interval 3.76 to 6.37
Salivary Cortisol Levels
Glutamate
5.21 pg/mL
Interval 4.54 to 6.2
5.29 pg/mL
Interval 4.77 to 6.33
Salivary Cortisol Levels
Lactate
4.49 pg/mL
Interval 3.11 to 5.21
3.95 pg/mL
Interval 2.75 to 6.11
Salivary Cortisol Levels
Homocysteine
4.78 pg/mL
Interval 4.51 to 5.11
5.02 pg/mL
Interval 4.75 to 5.31
Salivary Cortisol Levels
BDNF
465.98 pg/mL
Interval 145.23 to 1965.72
356.20 pg/mL
Interval 218.79 to 1040.88
Salivary Cortisol Levels
Thioredoxin
417.50 pg/mL
Interval 291.67 to 547.75
405.33 pg/mL
Interval 326.92 to 519.25
Salivary Cortisol Levels
S100B
154.63 pg/mL
Interval 91.25 to 299.88
111.39 pg/mL
Interval 49.78 to 278.73

PRIMARY outcome

Timeframe: Baseline

Compare biomarkers for stress (salivary cortisol) in medication-naïve schizophrenia/schizophreniform subjects and matched healthy controls to identify illness-related factors.

Outcome measures

Outcome measures
Measure
Healthy Controls
n=54 Participants
Age and gender matched healthy controls
Patients
n=46 Participants
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Salivary Cortisol Levels
4.88 µg/dL
Interval 3.19 to 7.51
6.56 µg/dL
Interval 4.18 to 8.98

PRIMARY outcome

Timeframe: Baseline and week 8

Population: Analysis was done for first episode subjects who completed both Baseline and Week 8 only.

Compare salivary cortisol at baseline and after 8 weeks of risperidone treatment in medication-naïve schizophrenia/schizophreniform subjects to identify treatment-related factors. Since Blood and Saliva was only collected from First Episode participants (FEP) at week 8 (not from healthy controls) these results only report the baseline and week 8 biomarker levels for FEP participants who completed week 8.

Outcome measures

Outcome measures
Measure
Healthy Controls
n=19 Participants
Age and gender matched healthy controls
Patients
n=19 Participants
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Change in Salivary Cortisol Levels
7.41 µg/dL
Interval 1.89 to 9.17
4.36 µg/dL
Interval 2.37 to 8.2

SECONDARY outcome

Timeframe: Baseline

Compare hippocampal volume in medication-naïve schizophrenia/schizophreniform subjects and healthy controls and examine whether biomarkers predict differences between groups in baseline hippocampal volume.

Outcome measures

Outcome measures
Measure
Healthy Controls
n=54 Participants
Age and gender matched healthy controls
Patients
n=57 Participants
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Left Hippocampal Volumetric Integrity (HVI)
.9512 % of hippocampal volumetric integrity
Interval 0.8501 to 0.9825
.9275 % of hippocampal volumetric integrity
Interval 0.8256 to 0.9689

SECONDARY outcome

Timeframe: Baseline, week 8

Population: Data provided only for subjects who completed assessments at both time points.

Compare cognitive performance on the Measurement and Treatment Research to Improve Cognition in Schizophrenia (MATRICS) Consensus Cognitive Battery (MCCB) in medication- naïve schizophrenia/schizophreniform subjects and healthy controls and examine whether biomarkers predict differences between groups in baseline cognitive performance. The composite score on the MCCB is calculated by the software using all tests administered. The composite score is a t-score assuming the mean score (50%) is the normative performance of the general population. The composite score ranges from 0-100 with a standard deviation of 10. A score greater than 50 implies a score better than the average population norm and a score less than 50 indicates performance worse than the general population norm. For schizophrenia subjects who complete 8 weeks of antipsychotic treatment, week 8 MATRICS testing results will be used to minimize the effect of psychosis on cognitive performance.

Outcome measures

Outcome measures
Measure
Healthy Controls
n=36 Participants
Age and gender matched healthy controls
Patients
n=30 Participants
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Cognitive Performance
Baseline MCCB Composite Score
47.50 units on a scale
Interval 41.0 to 53.0
34 units on a scale
Interval 24.5 to 45.25
Cognitive Performance
Week 8 MCCB Composite Score
49.50 units on a scale
Interval 44.25 to 54.0
42.50 units on a scale
Interval 32.25 to 49.0

SECONDARY outcome

Timeframe: Baseline, week 8

Population: This analysis includes participants that completed both baseline and week 8 visits.

Compare hippocampal volume in medication-naïve schizophrenia/schizophreniform subjects before and after 8 weeks treatment with antipsychotic to assess evidence for early neurotoxicity. This outcome measure reports annualized rate of change in Left Hippocampal Volume Integrity (LHVI) because a few participants had a delay in their week 8 visit.

Outcome measures

Outcome measures
Measure
Healthy Controls
n=31 Participants
Age and gender matched healthy controls
Patients
n=24 Participants
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Annualized Change in Left Hippocampal Volume Integrity
0.004535 Percentage of standard hippocampal vol.
Interval -0.0151 to 0.035
-0.03027 Percentage of standard hippocampal vol.
Interval -0.0817 to 0.00004

Adverse Events

Healthy Controls

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Patients

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Healthy Controls
n=73 participants at risk
Age and gender matched healthy controls
Patients
n=79 participants at risk
Participants diagnosed with Schizophrenia, schizophreniform disorder, or schizoaffective disorder, depressed type that are naive to anti-psychotic treatment.
Eye disorders
Blurred Vision
0.00%
0/73
1.3%
1/79 • Number of events 1
Cardiac disorders
Hypertension
0.00%
0/73
1.3%
1/79 • Number of events 1

Additional Information

Principal Investigator

NYU Langone Health

Phone: 646-754-4843

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place