Trial Outcomes & Findings for Obstructive Sleep Apnea in World Trade Center Responders (NCT NCT01753999)

NCT ID: NCT01753999

Last Updated: 2025-04-30

Results Overview

The use (number of hours per night) will be compared between standard CPAP and CPAP flex. Results are based on the first treatment period only (pre-crossover).

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

317 participants

Primary outcome timeframe

5 weeks after initiation of treatment

Results posted on

2025-04-30

Participant Flow

Subjects were recruited between January 2013 and December 2016 at three World Trade Center Health Program Clinical Centers of Excellence (Rutgers University, Icahn School of Medicine at Mount Sinai, and New York University School of Medicine).

Subjects without OSA were excluded from the trial.

Participant milestones

Participant milestones
Measure
Standard CPAP Followed by CPAP-Flex
Participants were first treated with standard CPAP (continuous positive airway pressure with constant pressure) using a REMstar Auto A-flex in standard CPAP therapy mode for 4 weeks. The therapy mode was then switched to CPAP-Flex for 4 weeks. CPAP-Flex provides a decrease in pressure during expiration.
CPAP-Flex Followed by Standard CPAP
Participants were treated with CPAP-Flex (continuous positive airway pressure with a decrease in pressure during expiration) using a REMstar Auto A-flex in C-Flex mode for 4 weeks. The therapy mode was then switched to standard CPAP for 4 weeks. Standard CPAP provides a constant pressure (no decrease after expiration).
Period 1 - Initial Assignment
STARTED
155
162
Period 1 - Initial Assignment
Received Intervention
144
146
Period 1 - Initial Assignment
COMPLETED
116
112
Period 1 - Initial Assignment
NOT COMPLETED
39
50
Period 2 -Cross to Alternate Arm
STARTED
116
112
Period 2 -Cross to Alternate Arm
Received Intervention
103
95
Period 2 -Cross to Alternate Arm
COMPLETED
99
89
Period 2 -Cross to Alternate Arm
NOT COMPLETED
17
23

Reasons for withdrawal

Reasons for withdrawal
Measure
Standard CPAP Followed by CPAP-Flex
Participants were first treated with standard CPAP (continuous positive airway pressure with constant pressure) using a REMstar Auto A-flex in standard CPAP therapy mode for 4 weeks. The therapy mode was then switched to CPAP-Flex for 4 weeks. CPAP-Flex provides a decrease in pressure during expiration.
CPAP-Flex Followed by Standard CPAP
Participants were treated with CPAP-Flex (continuous positive airway pressure with a decrease in pressure during expiration) using a REMstar Auto A-flex in C-Flex mode for 4 weeks. The therapy mode was then switched to standard CPAP for 4 weeks. Standard CPAP provides a constant pressure (no decrease after expiration).
Period 1 - Initial Assignment
Physician Decision
2
3
Period 1 - Initial Assignment
Withdrawal by Subject
19
20
Period 1 - Initial Assignment
Lost to Follow-up
18
27
Period 2 -Cross to Alternate Arm
Lost to Follow-up
13
17
Period 2 -Cross to Alternate Arm
Withdrawal by Subject
3
5
Period 2 -Cross to Alternate Arm
Physician Decision
1
1

Baseline Characteristics

TNR measurement was missing for 16 subjects at baseline.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
All Study Participants
n=317 Participants
Participants who were randomized to receive either standard CPAP or CPAP-Flex.
Age, Categorical
<=18 years
0 Participants
n=317 Participants
Age, Categorical
Between 18 and 65 years
288 Participants
n=317 Participants
Age, Categorical
>=65 years
29 Participants
n=317 Participants
Age, Continuous
53.29 years
STANDARD_DEVIATION 8.23 • n=317 Participants
Sex: Female, Male
Female
35 Participants
n=317 Participants
Sex: Female, Male
Male
282 Participants
n=317 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
45 Participants
n=317 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
264 Participants
n=317 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
8 Participants
n=317 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=317 Participants
Race (NIH/OMB)
Asian
12 Participants
n=317 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=317 Participants
Race (NIH/OMB)
Black or African American
32 Participants
n=317 Participants
Race (NIH/OMB)
White
227 Participants
n=317 Participants
Race (NIH/OMB)
More than one race
33 Participants
n=317 Participants
Race (NIH/OMB)
Unknown or Not Reported
13 Participants
n=317 Participants
Apnea and Hypopnea Index (AHI4%)
17.01 Events/hour
STANDARD_DEVIATION 14.42 • n=317 Participants
Total Nasal Resistance
High Nasal Resistance (LogTNR>0.8)
132 Participants
n=301 Participants • TNR measurement was missing for 16 subjects at baseline.
Total Nasal Resistance
Low Nasal Resistance (LogTNR<=0.8)
169 Participants
n=301 Participants • TNR measurement was missing for 16 subjects at baseline.

PRIMARY outcome

Timeframe: 5 weeks after initiation of treatment

Population: Subjects who received the allocated treatment (i.e., turned on the PAP device). The difference between the number allocated and the number of analyzed is the result of some subjects (n=11 in CPAP and n=16 in C-Flex) who did not turn on the device despite taking it home. These were assumed to have NOT received the allocated treatment.

The use (number of hours per night) will be compared between standard CPAP and CPAP flex. Results are based on the first treatment period only (pre-crossover).

Outcome measures

Outcome measures
Measure
Standard CPAP
n=144 Participants
Use of a standard CPAP (continuous positive airway pressure) device with constant pressure for 4 weeks to improve breathing during sleep Standard CPAP: Use of the REMstar Auto A-Flex in standard CPAP therapy mode
CPAP-Flex
n=146 Participants
Use of CPAP-Flex (continuous positive airway pressure) device with decreased pressure during expiration for 4 weeks to improve breathing during sleep CPAP - Flex: Use of Philips Respironics REMstar Auto A-Flex in C-Flex mode
Adherence to CPAP Pre-crossover
1 Hours/night
Interval 0.0 to 3.32
0.89 Hours/night
Interval 0.0 to 3.17

PRIMARY outcome

Timeframe: 9 weeks after initiation of treatment

Population: Subjects who received the allocated treatment (i.e., turned on the PAP device) in either the first treatment period or the second treatment period.

The use (number of hours per night) will be compared between standard CPAP and CPAP flex. Results are based on both periods.

Outcome measures

Outcome measures
Measure
Standard CPAP
n=239 Participants
Use of a standard CPAP (continuous positive airway pressure) device with constant pressure for 4 weeks to improve breathing during sleep Standard CPAP: Use of the REMstar Auto A-Flex in standard CPAP therapy mode
CPAP-Flex
n=249 Participants
Use of CPAP-Flex (continuous positive airway pressure) device with decreased pressure during expiration for 4 weeks to improve breathing during sleep CPAP - Flex: Use of Philips Respironics REMstar Auto A-Flex in C-Flex mode
Adherence to CPAP Overall Study
1.03 Hours/night
Interval 0.0 to 3.33
0.8 Hours/night
Interval 0.0 to 2.86

SECONDARY outcome

Timeframe: 5 weeks after initiation of treatment

Population: Subjects who received treatment (turned on the PAP device). An additional 48 subjects on CPAP and 53 on CPAP-FLex were not analyzed as an AHI could not be generated during the analysis period due to insufficient use.

Efficacy will be evaluated by measuring the residual apnea and hypopnea index (AHI) while on treatment. The efficacy of standard CPAP and CPAP-flex will be compared. Results are based on the first treatment period only (pre-crossover).

Outcome measures

Outcome measures
Measure
Standard CPAP
n=96 Participants
Use of a standard CPAP (continuous positive airway pressure) device with constant pressure for 4 weeks to improve breathing during sleep Standard CPAP: Use of the REMstar Auto A-Flex in standard CPAP therapy mode
CPAP-Flex
n=93 Participants
Use of CPAP-Flex (continuous positive airway pressure) device with decreased pressure during expiration for 4 weeks to improve breathing during sleep CPAP - Flex: Use of Philips Respironics REMstar Auto A-Flex in C-Flex mode
CPAP Efficacy
2.89 Events/hour
Standard Deviation 3.06
3.12 Events/hour
Standard Deviation 2.95

SECONDARY outcome

Timeframe: 9 weeks after initiation of treatment

Population: Subjects who received the allocated treatment (i.e., turned on the PAP device; N=239 for CPAP and N=249 for CPAP Flex). An additional 82 subjects on CPAP and 102 subjects on CPAP-Flex were not analyzed as an AHI could not be generated during the analysis period due to insufficient use.

Efficacy will be evaluated by measuring the residual apnea and hypopnea index (AHI) while on treatment. The efficacy of standard CPAP and CPAP-flex will be compared. Results are based on both treatment periods.

Outcome measures

Outcome measures
Measure
Standard CPAP
n=157 Participants
Use of a standard CPAP (continuous positive airway pressure) device with constant pressure for 4 weeks to improve breathing during sleep Standard CPAP: Use of the REMstar Auto A-Flex in standard CPAP therapy mode
CPAP-Flex
n=147 Participants
Use of CPAP-Flex (continuous positive airway pressure) device with decreased pressure during expiration for 4 weeks to improve breathing during sleep CPAP - Flex: Use of Philips Respironics REMstar Auto A-Flex in C-Flex mode
CPAP Efficacy
2.71 events/hour
Standard Deviation 2.76
2.94 events/hour
Standard Deviation 2.65

OTHER_PRE_SPECIFIED outcome

Timeframe: 9 weeks after initiation of treatment

Population: Subjects with high total nasal resistance who received the allocated treatment (i.e., turned on the PAP device) in either the first treatment period or in the second treatment period.Total nasal resistance data are missing for 8 subjects.

The use (number of hours per night) will be compared between standard CPAP and CPAP flex for subjects with high total nasal resistance (logTNR\>0.8). The analysis is based on both periods.

Outcome measures

Outcome measures
Measure
Standard CPAP
n=105 Participants
Use of a standard CPAP (continuous positive airway pressure) device with constant pressure for 4 weeks to improve breathing during sleep Standard CPAP: Use of the REMstar Auto A-Flex in standard CPAP therapy mode
CPAP-Flex
n=110 Participants
Use of CPAP-Flex (continuous positive airway pressure) device with decreased pressure during expiration for 4 weeks to improve breathing during sleep CPAP - Flex: Use of Philips Respironics REMstar Auto A-Flex in C-Flex mode
Adherence to CPAP Overall Study, Subjects With High Nasal Resistance
2.08 Hours/night
Interval 1.6 to 2.55
1.75 Hours/night
Interval 1.31 to 2.2

OTHER_PRE_SPECIFIED outcome

Timeframe: 9 weeks after initiation of treatment

Population: Subjects with low total nasal resistance who received the allocated treatment (i.e., turned on the PAP device) in either the first treatment period or in the second treatment period. Total nasal resistance data are missing for 8 subjects.

The use (number of hours per night) will be compared between standard CPAP and CPAP flex for subjects with low total nasal resistance (logTNR\<=0.8). The analysis is based on both periods.

Outcome measures

Outcome measures
Measure
Standard CPAP
n=126 Participants
Use of a standard CPAP (continuous positive airway pressure) device with constant pressure for 4 weeks to improve breathing during sleep Standard CPAP: Use of the REMstar Auto A-Flex in standard CPAP therapy mode
CPAP-Flex
n=131 Participants
Use of CPAP-Flex (continuous positive airway pressure) device with decreased pressure during expiration for 4 weeks to improve breathing during sleep CPAP - Flex: Use of Philips Respironics REMstar Auto A-Flex in C-Flex mode
Adherence to CPAP Overall Study, Subjects With Low Nasal Resistance
1.81 Hours/night
Interval 1.44 to 2.18
1.55 Hours/night
Interval 1.22 to 1.88

Adverse Events

Standard CPAP

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

CPAP - Flex

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Dr. Jag Sunderram

Rutgers Robert Wood Johnson Medical School

Phone: 732-235-7038

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place