Trial Outcomes & Findings for A Proof-of-Concept Study of AC-201 to Prevent Gout Flares (NCT NCT01712204)

NCT ID: NCT01712204

Last Updated: 2018-05-22

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

82 participants

Primary outcome timeframe

16 weeks

Results posted on

2018-05-22

Participant Flow

Overall, 82 patients from 8 clinical centers participated in the study between 28 January 2013 to 04 September 2013.

Participants were assessed at an initial screening visit within 2 weeks before the baseline visit.

Participant milestones

Participant milestones
Measure
Placebo
Placebo Capsule BID for 16 Weeks
AC-201
AC-201 50mg Capsule BID for 16 Weeks
Overall Study
STARTED
41
41
Overall Study
COMPLETED
33
36
Overall Study
NOT COMPLETED
8
5

Reasons for withdrawal

Reasons for withdrawal
Measure
Placebo
Placebo Capsule BID for 16 Weeks
AC-201
AC-201 50mg Capsule BID for 16 Weeks
Overall Study
Adverse Event
3
1
Overall Study
Withdrawal by Subject
3
3
Overall Study
Lost to Follow-up
1
0
Overall Study
Protocol Violation
1
1

Baseline Characteristics

A Proof-of-Concept Study of AC-201 to Prevent Gout Flares

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo Capsule BID
n=41 Participants
Placebo Capsule BID for 16 Weeks
AC-201 50mg Capsule BID
n=41 Participants
AC-201 50mg Capsule BID for 16 Weeks
Total
n=82 Participants
Total of all reporting groups
Age, Continuous
43.6 years
STANDARD_DEVIATION 11.8 • n=99 Participants
43.7 years
STANDARD_DEVIATION 12.6 • n=107 Participants
43.6 years
STANDARD_DEVIATION 12.1 • n=206 Participants
Sex: Female, Male
Female
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Sex: Female, Male
Male
41 Participants
n=99 Participants
41 Participants
n=107 Participants
82 Participants
n=206 Participants

PRIMARY outcome

Timeframe: 16 weeks

Outcome measures

Outcome measures
Measure
Placebo
n=41 Participants
Placebo Capsule BID for 16 Weeks Background therapy: Urate-Lowering Therapy (Febuxostat 80 mg QD)
AC-201
n=41 Participants
AC-201 50mg Capsule BID for 16 Weeks Background therapy: Urate-Lowering Therapy (Febuxostat 80 mg QD)
Number of Gout Flares Per Subject
3.02 flares
Interval 2.51 to 3.64
2.45 flares
Interval 2.01 to 3.0

Adverse Events

Placebo

Serious events: 1 serious events
Other events: 11 other events
Deaths: 0 deaths

AC-201

Serious events: 0 serious events
Other events: 10 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Placebo
n=41 participants at risk
Placebo Capsule BID for 16 Weeks Background therapy: Urate-Lowering Therapy (Febuxostat 80 mg QD)
AC-201
n=41 participants at risk
AC-201 50mg Capsule BID for 16 Weeks Background therapy: Urate-Lowering Therapy (Febuxostat 80 mg QD)
Metabolism and nutrition disorders
Frequent Gout Attack
2.4%
1/41 • Number of events 1 • 16 weeks
0.00%
0/41 • 16 weeks

Other adverse events

Other adverse events
Measure
Placebo
n=41 participants at risk
Placebo Capsule BID for 16 Weeks Background therapy: Urate-Lowering Therapy (Febuxostat 80 mg QD)
AC-201
n=41 participants at risk
AC-201 50mg Capsule BID for 16 Weeks Background therapy: Urate-Lowering Therapy (Febuxostat 80 mg QD)
Investigations
Blood CPK increased
9.8%
4/41 • Number of events 4 • 16 weeks
2.4%
1/41 • Number of events 1 • 16 weeks
Hepatobiliary disorders
Hepatic function abnormal
7.3%
3/41 • Number of events 3 • 16 weeks
4.9%
2/41 • Number of events 2 • 16 weeks
Investigations
ALT increased
7.3%
3/41 • Number of events 3 • 16 weeks
0.00%
0/41 • 16 weeks
Musculoskeletal and connective tissue disorders
Tendonitis
2.4%
1/41 • Number of events 1 • 16 weeks
4.9%
2/41 • Number of events 2 • 16 weeks
Renal and urinary disorders
Renal Impairment
2.4%
1/41 • Number of events 1 • 16 weeks
4.9%
2/41 • Number of events 2 • 16 weeks
Blood and lymphatic system disorders
Anemia
0.00%
0/41 • 16 weeks
4.9%
2/41 • Number of events 2 • 16 weeks
Infections and infestations
Nasopharyngitis
0.00%
0/41 • 16 weeks
4.9%
2/41 • Number of events 2 • 16 weeks
Investigations
Creatinine renal clearance decreased
0.00%
0/41 • 16 weeks
4.9%
2/41 • Number of events 2 • 16 weeks

Additional Information

Medical Director

TWi Biotechnology, Inc.

Phone: +886-2-26573350

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60