Trial Outcomes & Findings for Thrombolysis in Pediatric Stroke (TIPS) (NCT NCT01591096)

NCT ID: NCT01591096

Last Updated: 2018-05-25

Results Overview

Any PH 2 OR, Any intracranial hemorrhage which is judged to be the most important cause of neurological deterioration (a minimum of change of 2 or more points on the PedNIHSS from the lowest PedNIHSS). At the time of each PedNIHSS assessment, the site PI or co-PI will review the patient's course with the care team to ensure that all changes in neurologic status, including improvements since the last assessment by the study team, are captured, OR, Any hemorrhage that results in the need for transfusion, need to discontinue study drug, surgical evacuation of hemorrhage, or death.

Recruitment status

TERMINATED

Study phase

PHASE1

Target enrollment

1 participants

Primary outcome timeframe

36 hours

Results posted on

2018-05-25

Participant Flow

1 patient was recruited for the study, however, they did not receive the intervention due to an AE

Participant milestones

Participant milestones
Measure
Tissue Plasminogen Activator
All patients will receive study drug. Tissue plasminogen activator (Activase®): Investigation labeled tPA will be obtained for all sites by the Core Pharmacy as commercially available recombinant tPA (Genentech as Activase®) for IV administration. The Bayesian method of toxicity probability intervals will be used to select one of the following three dose tiers (0.75, 0.9, 1.0 mg/kg) of IV tPA. The dose escalation for the two age groups (2-10, 11-17 years) will be performed independently. The maximum dose for each tier will be reached at a weight of 90 kg.
Overall Study
STARTED
1
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Tissue Plasminogen Activator
All patients will receive study drug. Tissue plasminogen activator (Activase®): Investigation labeled tPA will be obtained for all sites by the Core Pharmacy as commercially available recombinant tPA (Genentech as Activase®) for IV administration. The Bayesian method of toxicity probability intervals will be used to select one of the following three dose tiers (0.75, 0.9, 1.0 mg/kg) of IV tPA. The dose escalation for the two age groups (2-10, 11-17 years) will be performed independently. The maximum dose for each tier will be reached at a weight of 90 kg.
Overall Study
Adverse Event
1

Baseline Characteristics

Thrombolysis in Pediatric Stroke (TIPS)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Tissue Plasminogen Activator
n=1 Participants
All patients will receive study drug. Tissue plasminogen activator (Activase®): Investigation labeled tPA will be obtained for all sites by the Core Pharmacy as commercially available recombinant tPA (Genentech as Activase®) for IV administration. The Bayesian method of toxicity probability intervals will be used to select one of the following three dose tiers (0.75, 0.9, 1.0 mg/kg) of IV tPA. The dose escalation for the two age groups (2-10, 11-17 years) will be performed independently. The maximum dose for each tier will be reached at a weight of 90 kg.
Age, Categorical
<=18 years
1 Participants
n=99 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=99 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
Sex: Female, Male
Female
1 Participants
n=99 Participants
Sex: Female, Male
Male
0 Participants
n=99 Participants
Region of Enrollment
United States
1 Participants
n=99 Participants

PRIMARY outcome

Timeframe: 36 hours

Population: Data cannot be reported in the data table as no data was collected

Any PH 2 OR, Any intracranial hemorrhage which is judged to be the most important cause of neurological deterioration (a minimum of change of 2 or more points on the PedNIHSS from the lowest PedNIHSS). At the time of each PedNIHSS assessment, the site PI or co-PI will review the patient's course with the care team to ensure that all changes in neurologic status, including improvements since the last assessment by the study team, are captured, OR, Any hemorrhage that results in the need for transfusion, need to discontinue study drug, surgical evacuation of hemorrhage, or death.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 24 hours

Population: Data cannot be reported in the data table as no data was collected

TIPS will determine the pharmacokinetics of tPA and its inhibitor, plasminogen activator inhibitor, including free tPA, PAI-1, and tPA antigen in children receiving IV tPA for acute AIS. In addition, TIPS will measure the 3-month neurological outcome in children treated with IV tPA.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 24 hours

Population: Data cannot be reported in the data table as no data was collected

TIPS will determine the pharmacokinetics of tPA and its inhibitor, plasminogen activator inhibitor, including free tPA, PAI-1, and tPA antigen in children receiving IV tPA for acute AIS. In addition, TIPS will measure the 3-month neurological outcome in children treated with IV tPA.

Outcome measures

Outcome data not reported

Adverse Events

Tissue Plasminogen Activator

Serious events: 1 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Tissue Plasminogen Activator
n=1 participants at risk
All patients will receive study drug. Tissue plasminogen activator (Activase®): Investigation labeled tPA will be obtained for all sites by the Core Pharmacy as commercially available recombinant tPA (Genentech as Activase®) for IV administration. The Bayesian method of toxicity probability intervals will be used to select one of the following three dose tiers (0.75, 0.9, 1.0 mg/kg) of IV tPA. The dose escalation for the two age groups (2-10, 11-17 years) will be performed independently. The maximum dose for each tier will be reached at a weight of 90 kg.
Cardiac disorders
Hypoventilation, bradycardia
100.0%
1/1 • Number of events 1

Other adverse events

Adverse event data not reported

Additional Information

Catherine Amlie-Lefond MD

SeattleChildrens

Phone: 206-987-2078

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place