Trial Outcomes & Findings for Tilt-Table Study of the Clinical Efficacy of Midodrine in Symptomatic Orthostatic Hypotension (NCT NCT01518946)

NCT ID: NCT01518946

Last Updated: 2021-06-08

Results Overview

After a 30-minute supine period, the table was tilted from 0-90º within 30 seconds and maintained in that position for 45 minutes or until endpoint. Subjects were monitored for near-syncopal symptoms (subject felt sufficiently dizzy, lightheaded, faint, or felt like they were about to black out and requested the table to be returned to horizontal). Such a report ended the test. Alternatively, if the investigator observed that the subject was about to lose consciousness, that also constituted an endpoint.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

24 participants

Primary outcome timeframe

1 hour post-dose

Results posted on

2021-06-08

Participant Flow

Participant milestones

Participant milestones
Measure
Midodrine HCl (Open-label Phase)
On the morning of Day -1, subjects took their usual morning dose of midodrine HCl, using their own midodrine HCl supplies at approximately the same time before rising that they would normally take their morning dose. On the morning of Day 1, subjects had their usual morning dose of midodrine HCl withheld.
Placebo First, Then Midodrine HCl (Randomized Phase)
Placebo for first intervention on Day 2, then Midodrine hydrochloride dose at the subject's current dose level for the second intervention on Day 3.
Midodrine HCl First, Then Placebo (Randomized Phase)
Midodrine hydrochloride dose at the subject's current dose level for the first intervention Day 2, then placebo for second intervention on Day 3.
Open-label Phase
STARTED
24
0
0
Open-label Phase
COMPLETED
20
0
0
Open-label Phase
NOT COMPLETED
4
0
0
Randomized Phase (First Intervention)
STARTED
0
10
10
Randomized Phase (First Intervention)
COMPLETED
0
9
10
Randomized Phase (First Intervention)
NOT COMPLETED
0
1
0
Randomized Phase (Second Intervention)
STARTED
0
9
10
Randomized Phase (Second Intervention)
COMPLETED
0
9
10
Randomized Phase (Second Intervention)
NOT COMPLETED
0
0
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Midodrine HCl (Open-label Phase)
On the morning of Day -1, subjects took their usual morning dose of midodrine HCl, using their own midodrine HCl supplies at approximately the same time before rising that they would normally take their morning dose. On the morning of Day 1, subjects had their usual morning dose of midodrine HCl withheld.
Placebo First, Then Midodrine HCl (Randomized Phase)
Placebo for first intervention on Day 2, then Midodrine hydrochloride dose at the subject's current dose level for the second intervention on Day 3.
Midodrine HCl First, Then Placebo (Randomized Phase)
Midodrine hydrochloride dose at the subject's current dose level for the first intervention Day 2, then placebo for second intervention on Day 3.
Open-label Phase
Other
4
0
0
Randomized Phase (First Intervention)
Other
0
1
0

Baseline Characteristics

Tilt-Table Study of the Clinical Efficacy of Midodrine in Symptomatic Orthostatic Hypotension

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo First, Then Midodrine HCl (Randomized Phase)
n=10 Participants
Placebo for first intervention on Day 2, then Midodrine hydrochloride dose at the subject's current dose level for the second intervention on Day 3.
Midodrine HCl First, Then Placebo (Randomized Phase)
n=10 Participants
Midodrine hydrochloride dose at the subject's current dose level for the first intervention Day 2, then placebo for second intervention on Day 3.
Total
n=20 Participants
Total of all reporting groups
Age, Continuous
48.0 years
STANDARD_DEVIATION 19.52 • n=99 Participants
42.1 years
STANDARD_DEVIATION 18.64 • n=107 Participants
45.1 years
STANDARD_DEVIATION 18.82 • n=206 Participants
Age, Customized
18 to 65 years, inclusive
8 Participants
n=99 Participants
8 Participants
n=107 Participants
16 Participants
n=206 Participants
Age, Customized
>= 66 years
2 Participants
n=99 Participants
2 Participants
n=107 Participants
4 Participants
n=206 Participants
Sex: Female, Male
Female
8 Participants
n=99 Participants
10 Participants
n=107 Participants
18 Participants
n=206 Participants
Sex: Female, Male
Male
2 Participants
n=99 Participants
0 Participants
n=107 Participants
2 Participants
n=206 Participants
Region of Enrollment
United States
10 Participants
n=99 Participants
10 Participants
n=107 Participants
20 Participants
n=206 Participants

PRIMARY outcome

Timeframe: 1 hour post-dose

Population: The Full Analysis Set was defined as all randomized subjects who received at least 1 dose of randomized investigational product and who had at least 1 measurement of the time to onset of syncopal symptoms/near syncope during tilt-table testing.

After a 30-minute supine period, the table was tilted from 0-90º within 30 seconds and maintained in that position for 45 minutes or until endpoint. Subjects were monitored for near-syncopal symptoms (subject felt sufficiently dizzy, lightheaded, faint, or felt like they were about to black out and requested the table to be returned to horizontal). Such a report ended the test. Alternatively, if the investigator observed that the subject was about to lose consciousness, that also constituted an endpoint.

Outcome measures

Outcome measures
Measure
Placebo
n=19 Participants
single dose of matching placebo
Midodrine HCl
n=19 Participants
dose at the subject's current dose level
Time to Onset of Syncope/Near Syncope While on Tilt Table
1105.6 seconds
Standard Error 186.82
1626.6 seconds
Standard Error 186.82

Adverse Events

Midodrine HCl (Open-label Phase)

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

Placebo (Randomized Phase)

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Midodrine HCl (Randomized Phase)

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Midodrine HCl (Open-label Phase)
n=24 participants at risk
dose at the subject's current dose level
Placebo (Randomized Phase)
n=20 participants at risk
single dose of matching placebo
Midodrine HCl (Randomized Phase)
n=20 participants at risk
dose at the subject's current dose level
Gastrointestinal disorders
Nausea
8.3%
2/24 • Number of events 2
0.00%
0/20
0.00%
0/20
General disorders
Fatigue
0.00%
0/24
0.00%
0/20
5.0%
1/20 • Number of events 1
Musculoskeletal and connective tissue disorders
Back Pain
0.00%
0/24
5.0%
1/20 • Number of events 1
0.00%
0/20
Nervous system disorders
Headache
8.3%
2/24 • Number of events 2
0.00%
0/20
0.00%
0/20
Vascular disorders
Flushing
0.00%
0/24
0.00%
0/20
5.0%
1/20 • Number of events 1
Vascular disorders
Hot Flush
0.00%
0/24
0.00%
0/20
5.0%
1/20 • Number of events 1

Additional Information

Study Director

Shire

Phone: +1 866-842-5335

Results disclosure agreements

  • Principal investigator is a sponsor employee If a multicenter publication is not submitted within twelve (12) months after conclusion, abandonment or termination of the Study at all sites, or after Sponsor confirms there shall be no multicenter Study publication, the Institution and/or such Principal Investigator may publish the results from the Institution site individually.
  • Publication restrictions are in place

Restriction type: OTHER