Trial Outcomes & Findings for Phase II FANG™ in Advanced Melanoma (NCT NCT01453361)

NCT ID: NCT01453361

Last Updated: 2018-05-24

Results Overview

To determine if subjects will have a positive (defined as \>10 ELISPOTS from baseline) immune response to Vigil. Blood was collected to compare ELISPOT results from baseline until EOT (30 days after last dose).

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

18 participants

Primary outcome timeframe

Baseline, End of Treatment (30 days after last dose) up to 12 months

Results posted on

2018-05-24

Participant Flow

This study recruited patients with Stages IIIc and IV melanoma.

18 were enrolled but 10 screen-failed so only 8 proceeded with the single group assignment (Vigil treatment).

Participant milestones

Participant milestones
Measure
Vigil™ Vaccine
Autologous Vigil™ vaccine will be supplied by Gradalis, Inc. Patients will receive 1 x 10e7 cells via intradermal injection one day each month for a minimum maximum of 12 doses as long as subject is clinically stable. Vigil™ Vaccine
Overall Study
STARTED
18
Overall Study
COMPLETED
2
Overall Study
NOT COMPLETED
16

Reasons for withdrawal

Reasons for withdrawal
Measure
Vigil™ Vaccine
Autologous Vigil™ vaccine will be supplied by Gradalis, Inc. Patients will receive 1 x 10e7 cells via intradermal injection one day each month for a minimum maximum of 12 doses as long as subject is clinically stable. Vigil™ Vaccine
Overall Study
Disease Progression
6
Overall Study
Screen-Failures
10

Baseline Characteristics

Phase II FANG™ in Advanced Melanoma

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Vigil™ Vaccine
n=18 Participants
Autologous Vigil™ vaccine will be supplied by Gradalis, Inc. Patients will receive 1 x 10e7 cells via intradermal injection one day each month for a minimum maximum of 12 doses as long as subject is clinically stable. Vigil™ Vaccine
Age, Customized
Age · 0-15 Years
0 Participants
n=99 Participants
Age, Customized
Age · 16-64 Years
9 Participants
n=99 Participants
Age, Customized
Age · 65 and Older Years
9 Participants
n=99 Participants
Sex: Female, Male
Female
6 Participants
n=99 Participants
Sex: Female, Male
Male
12 Participants
n=99 Participants
Race/Ethnicity, Customized
White/Caucasian
18 Participants
n=99 Participants
Race/Ethnicity, Customized
Black/African American
0 Participants
n=99 Participants
Race/Ethnicity, Customized
Asian
0 Participants
n=99 Participants
Race/Ethnicity, Customized
Hispanic
0 Participants
n=99 Participants
Race/Ethnicity, Customized
Other
0 Participants
n=99 Participants

PRIMARY outcome

Timeframe: Baseline, End of Treatment (30 days after last dose) up to 12 months

Population: 18 subjects were consented but only 8 subjects were administered Vigil treatment (10 screen-failed). 7 completed treatment (ELISPOT done) while 1 subject died soon after baseline (ELISPOT not done). After 12 months, 7 subjects had positive ELISPOT response. Statistical analysis was not done. This study was terminated.

To determine if subjects will have a positive (defined as \>10 ELISPOTS from baseline) immune response to Vigil. Blood was collected to compare ELISPOT results from baseline until EOT (30 days after last dose).

Outcome measures

Outcome measures
Measure
Vigil™ Vaccine
n=18 Participants
Autologous Vigil™ vaccine will be supplied by Gradalis, Inc. Patients will receive 1 x 10e7 cells via intradermal injection one day each month for a minimum maximum of 12 doses as long as subject is clinically stable. Vigil™ Vaccine
Enzyme-Linked ImmunoSorbent Spot (ELISPOT)
Not Done/Died immediately after Baseline
1 Participants
Enzyme-Linked ImmunoSorbent Spot (ELISPOT)
Not Done/Screen-Failed
10 Participants
Enzyme-Linked ImmunoSorbent Spot (ELISPOT)
ELISPOT Positive After 12 months
7 Participants
Enzyme-Linked ImmunoSorbent Spot (ELISPOT)
ELISPOT Negative After 12 months
0 Participants

SECONDARY outcome

Timeframe: 3 years

Population: 18 subjects were consented but only 8 were administered Vigil treatment (10 screen-failed). These 8 subjects were followed for survival up to 3 years after Vigil treatment.

The survival status in patients with stages IIIc and IV melanoma treated with Vigil™ vaccine was determined by following these patients up to 3 years.

Outcome measures

Outcome measures
Measure
Vigil™ Vaccine
n=18 Participants
Autologous Vigil™ vaccine will be supplied by Gradalis, Inc. Patients will receive 1 x 10e7 cells via intradermal injection one day each month for a minimum maximum of 12 doses as long as subject is clinically stable. Vigil™ Vaccine
Number of Alive Subjects
Alive Subjects After 3 years
1 Participants
Number of Alive Subjects
Dead Subjects After 3 years
7 Participants
Number of Alive Subjects
Screen-Failed
10 Participants

Adverse Events

Vigil™ Vaccine

Serious events: 3 serious events
Other events: 3 other events
Deaths: 15 deaths

Serious adverse events

Serious adverse events
Measure
Vigil™ Vaccine
n=18 participants at risk
Autologous Vigil™ vaccine will be supplied by Gradalis, Inc. Patients will receive 1 x 10e7 cells via intradermal injection one day each month for a minimum maximum of 12 doses as long as subject is clinically stable. Vigil™ Vaccine
Infections and infestations
Soft Tissue Infection
5.6%
1/18 • Number of events 1
Skin and subcutaneous tissue disorders
Skin Ulceration
5.6%
1/18 • Number of events 1
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Tumor Pain
5.6%
1/18 • Number of events 1
Gastrointestinal disorders
Abdominal Hernia
5.6%
1/18 • Number of events 1

Other adverse events

Other adverse events
Measure
Vigil™ Vaccine
n=18 participants at risk
Autologous Vigil™ vaccine will be supplied by Gradalis, Inc. Patients will receive 1 x 10e7 cells via intradermal injection one day each month for a minimum maximum of 12 doses as long as subject is clinically stable. Vigil™ Vaccine
General disorders
Injection Site Reaction
16.7%
3/18 • Number of events 9

Additional Information

Director of Clinical Trials

Gradalis, Inc.

Phone: 2144428124

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place