Trial Outcomes & Findings for Genetics, Brain Structure and Thinking Skills in Autism (NCT NCT01451983)

NCT ID: NCT01451983

Last Updated: 2015-01-14

Results Overview

Recruitment status

COMPLETED

Target enrollment

138 participants

Primary outcome timeframe

Baseline

Results posted on

2015-01-14

Participant Flow

Participant milestones

Participant milestones
Measure
ASD With PTEN
Individuals with autism spectrum disorder who are also found to have a PTEN mutation.
ASD no PTEN Macrocephaly
Individuals with autism spectrum disorder who do not have a PTEN mutation with a large head circumference.
ASD no PTEN no Macrocephaly
Individuals with autism spectrum disorder who do not have a PTEN mutation without a large head circumference.
Siblings
Siblings of individuals with autism spectrum disorders.
Overall Study
STARTED
26
27
61
24
Overall Study
COMPLETED
26
27
61
24
Overall Study
NOT COMPLETED
0
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Genetics, Brain Structure and Thinking Skills in Autism

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
ASD With PTEN
n=26 Participants
Individuals with autism spectrum disorder who are also found to have a PTEN mutation.
ASD no PTEN Macrocephaly
n=27 Participants
Individuals with autism spectrum disorder who do not have a PTEN mutation with a large head circumference.
ASD no PTEN no Macrocephaly
n=61 Participants
Individuals with autism spectrum disorder who do not have a PTEN mutation without a large head circumference.
Siblings
n=24 Participants
Siblings of individuals with autism spectrum disorders.
Total
n=138 Participants
Total of all reporting groups
Age, Continuous
11.9 years
n=39 Participants
13.3 years
n=41 Participants
9.0 years
n=35 Participants
11.7 years
n=31 Participants
11.4 years
n=146 Participants
Sex: Female, Male
Female
8 Participants
n=39 Participants
4 Participants
n=41 Participants
8 Participants
n=35 Participants
10 Participants
n=31 Participants
30 Participants
n=146 Participants
Sex: Female, Male
Male
18 Participants
n=39 Participants
23 Participants
n=41 Participants
53 Participants
n=35 Participants
14 Participants
n=31 Participants
108 Participants
n=146 Participants

PRIMARY outcome

Timeframe: Baseline

Population: MRI acquisition was performed using Siemens Q4 TIM Trio 3 tesla scanner with standard 12-channel receive-only head coil. An 8-minute whole-brain T1-weighted inversion recovery turboflash (MPRAGE) was acquired. Volumetric measurements were obtained using the software suite Freesurfer. Not all participants received imaging due to age and impairment.

Outcome measures

Outcome measures
Measure
ASD With PTEN
n=17 Participants
Individuals with autism spectrum disorder who are also found to have a PTEN mutation.
ASD no PTEN Macrocephaly
n=16 Participants
Individuals with autism spectrum disorder who do not have a PTEN mutation with a large head circumference.
ASD no PTEN no Macrocephaly
n=38 Participants
Individuals with autism spectrum disorder who do not have a PTEN mutation without a large head circumference.
Siblings
n=14 Participants
Siblings of individuals with autism spectrum disorders.
Total Brain Volume
1634.1 cubic centimeters
Standard Deviation 272.6
1409.8 cubic centimeters
Standard Deviation 158.6
1236.7 cubic centimeters
Standard Deviation 121.3
1401.9 cubic centimeters
Standard Deviation 199.2

Adverse Events

ASD With PTEN

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

ASD no PTEN Macrocephaly

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

ASD no PTEN no Macrocephaly

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Siblings

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Thomas W. Frazier, PhD

Cleveland Clinic Center for Autism

Phone: 216-448-6440

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place