Trial Outcomes & Findings for Treatment of Sickle Cell Patients Hospitalized in Pain Crisis With Prophylactic Dose Low-molecular-weight Heparin (LMWH) Versus Placebo (NCT NCT01419977)

NCT ID: NCT01419977

Last Updated: 2015-02-16

Results Overview

Patients will have D-dimer,for samples drawn on Day 1 and Day 3

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

34 participants

Primary outcome timeframe

Day 1 and Day 3

Results posted on

2015-02-16

Participant Flow

Of the 34 subjects were consented, 29 are received drug and had the day 1 blood draw. 2 subjects withdrew prior to receiving study drug. In addition, 2 subjects were discharged and 1 subject received a transfusion prior to the blood draw on day 1.

Participant milestones

Participant milestones
Measure
Placebo
Placebo: Normal saline solution, administered by nursing staff once daily
Dalteparin
Dalteparin: Low molecular weight heparin (LMWH), 5000 units subcutaneously, administered by nursing staff once daily, Other Name: Fragmin
Overall Study
STARTED
16
13
Overall Study
COMPLETED
16
13
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Treatment of Sickle Cell Patients Hospitalized in Pain Crisis With Prophylactic Dose Low-molecular-weight Heparin (LMWH) Versus Placebo

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo
n=16 Participants
Placebo: Normal saline solution, administered by nursing staff once daily
Dalteparin
n=13 Participants
Dalteparin: Low molecular weight heparin (LMWH), 5000 units subcutaneously, administered by nursing staff once daily, Other Name: Fragmin
Total
n=29 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Categorical
Between 18 and 65 years
16 Participants
n=99 Participants
13 Participants
n=107 Participants
29 Participants
n=206 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Sex: Female, Male
Female
4 Participants
n=99 Participants
7 Participants
n=107 Participants
11 Participants
n=206 Participants
Sex: Female, Male
Male
12 Participants
n=99 Participants
6 Participants
n=107 Participants
18 Participants
n=206 Participants
Region of Enrollment
United States
16 participants
n=99 Participants
13 participants
n=107 Participants
29 participants
n=206 Participants

PRIMARY outcome

Timeframe: Day 1 and Day 3

Population: 9 subjects were discharged prior to day 3 so the day 3 blood sample was not obtained.

Patients will have D-dimer,for samples drawn on Day 1 and Day 3

Outcome measures

Outcome measures
Measure
Placebo
n=11 Participants
Placebo: Normal saline solution, administered by nursing staff once daily
Dalteparin
n=9 Participants
Dalteparin: Low molecular weight heparin (LMWH), 5000 units subcutaneously, administered by nursing staff once daily, Other Name: Fragmin
Change in D-dimer
478.8 ng/mL
Standard Deviation 312.4
260.1 ng/mL
Standard Deviation 200.3

PRIMARY outcome

Timeframe: Baseline to day 1

The primary pain assessment tool will be a 10-cm horizontal visual analog scale (VAS), with "0" corresponding to no pain at one end and "10" indicating the worst pain at the other.

Outcome measures

Outcome measures
Measure
Placebo
n=16 Participants
Placebo: Normal saline solution, administered by nursing staff once daily
Dalteparin
n=13 Participants
Dalteparin: Low molecular weight heparin (LMWH), 5000 units subcutaneously, administered by nursing staff once daily, Other Name: Fragmin
Change in Clinical Pain Scores
-0.3 units on a scale
Standard Deviation 0.5
-1.6 units on a scale
Standard Deviation 0.4

PRIMARY outcome

Timeframe: Day 1 and Day 3

Population: 9 subjects were discharged prior to day 3 so the day 3 blood sample was not obtained.

Patients will have thrombin generation assay samples drawn on Day 1 and 3

Outcome measures

Outcome measures
Measure
Placebo
n=11 Participants
Placebo: Normal saline solution, administered by nursing staff once daily
Dalteparin
n=9 Participants
Dalteparin: Low molecular weight heparin (LMWH), 5000 units subcutaneously, administered by nursing staff once daily, Other Name: Fragmin
Change in Thrombin Generation Assay - Endogenous Thrombin Potential
13.4 nM
Standard Deviation 34.5
-45.98 nM
Standard Deviation 47.31

PRIMARY outcome

Timeframe: Baseline to day 3

Population: 9 subjects were discharged prior to obtaining day 3 VAS score.

The primary pain assessment tool will be a 10-cm horizontal visual analog scale (VAS), with "0" corresponding to no pain at one end and "10" indicating the worst pain at the other.

Outcome measures

Outcome measures
Measure
Placebo
n=11 Participants
Placebo: Normal saline solution, administered by nursing staff once daily
Dalteparin
n=9 Participants
Dalteparin: Low molecular weight heparin (LMWH), 5000 units subcutaneously, administered by nursing staff once daily, Other Name: Fragmin
Change in Clinical Pain Scores
-0.9 units on a scale
Standard Deviation 0.2
-2.4 units on a scale
Standard Deviation 0.9

Adverse Events

Placebo

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Dalteparin

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Nirmish Shah, MD

Duke University Medical Center

Phone: 919-684-5350

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place