Trial Outcomes & Findings for Special Investigation (All Case Survey) in Patients With Juvenile Idiopathic Arthritis (NCT NCT01412021)

NCT ID: NCT01412021

Last Updated: 2019-08-08

Results Overview

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, ESR, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Recruitment status

COMPLETED

Target enrollment

375 participants

Primary outcome timeframe

Baseline, Week 4

Results posted on

2019-08-08

Participant Flow

Participant milestones

Participant milestones
Measure
Humira
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Overall Study
STARTED
375
Overall Study
Case Report Forms Locked
368
Overall Study
COMPLETED
356
Overall Study
NOT COMPLETED
19

Reasons for withdrawal

Reasons for withdrawal
Measure
Humira
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Overall Study
Case Report Forms Not Retrieved
7
Overall Study
Treatment Prior to Approval
3
Overall Study
Transferred to Other Hospital
9

Baseline Characteristics

participants in the efficacy analysis set with an assessment

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Humira
n=356 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Age, Continuous
12.8 years
STANDARD_DEVIATION 4.8 • n=356 Participants
Sex: Female, Male
Female
241 Participants
n=356 Participants
Sex: Female, Male
Male
115 Participants
n=356 Participants
Race/Ethnicity, Customized
Japanese
352 Participants
n=356 Participants
Race/Ethnicity, Customized
Other, Not Specified
4 Participants
n=356 Participants
Disease Activity Scale 28 (DAS28)-4/Erythrocyte Sedimentation Rate (ESR)
3.70 units on a scale
STANDARD_DEVIATION 1.48 • n=170 Participants • participants in the efficacy analysis set with an assessment
DAS28-4/C-Reactive Protein (CRP)
3.42 units on a scale
STANDARD_DEVIATION 1.32 • n=175 Participants • participants in the efficacy analysis set with an assessment
Serum Matrix Metalloprotease-3 (MMP3) Level
162.68 ng/mL
STANDARD_DEVIATION 191.30 • n=180 Participants • participants in the efficacy analysis set with an assessment
Physician Global Assessment Visual Analog Scale (VAS)
40.6 mm
STANDARD_DEVIATION 25.1 • n=169 Participants • participants in the efficacy analysis set with an assessment
Anti-Cyclic Citullinated Peptide Antibody
89.41 U/mL
STANDARD_DEVIATION 158.34 • n=115 Participants • participants in the efficacy analysis set with an assessment
Height
143.86 cm
STANDARD_DEVIATION 19.24 • n=291 Participants • participants in the safety analysis set with an assessment
Weight
40.54 kg
STANDARD_DEVIATION 14.51 • n=299 Participants • participants in the safety analysis set with an assessment

PRIMARY outcome

Timeframe: Baseline, Week 4

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, ESR, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=145 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/ESR at Week 4
-1.01 units on a scale
Standard Deviation 1.08

PRIMARY outcome

Timeframe: Baseline, Week 8

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, ESR, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=123 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/ESR at Week 8
-1.39 units on a scale
Standard Deviation 1.26

PRIMARY outcome

Timeframe: Baseline, Week 12

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, ESR, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=127 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/ESR at Week 12
-1.39 units on a scale
Standard Deviation 1.28

PRIMARY outcome

Timeframe: Baseline, Week 16

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, ESR, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=134 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/ESR at Week 16
-1.46 units on a scale
Standard Deviation 1.40

PRIMARY outcome

Timeframe: Baseline, Week 24

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, ESR, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=128 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/ESR at Week 24
-1.64 units on a scale
Standard Deviation 1.52

PRIMARY outcome

Timeframe: Baseline, Week 4

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, CRP, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=155 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/CRP at Week 4
-0.94 units on a scale
Standard Deviation 1.01

PRIMARY outcome

Timeframe: Baseline, Week 8

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, CRP, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=130 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/CRP at Week 8
-1.24 units on a scale
Standard Deviation 1.14

PRIMARY outcome

Timeframe: Baseline, Week 12

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, CRP, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=135 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/CRP at Week 12
-1.29 units on a scale
Standard Deviation 1.12

PRIMARY outcome

Timeframe: Baseline, Week 16

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, CRP, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=140 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/CRP at Week 16
-1.35 units on a scale
Standard Deviation 1.23

PRIMARY outcome

Timeframe: Baseline, Week 24

Population: participants in the efficacy analysis set with an assessment

The DAS28 is a validated index of arthritis disease activity. Twenty-eight tender joint counts, 28 swollen joint counts, CRP, and the Subject's Global Assessment of Disease Activity (subject rates disease activity using a Likert scale from 0 \[low activity\] to 10 \[high activity\]) are included in the DAS28 score. Scores on the DAS28 range from 0 to 10. A DAS28 score \>5.1 indicates high disease activity, a DAS28 score \<3.2 indicates low disease activity, and a DAS28 score \<2.6 indicates clinical remission.

Outcome measures

Outcome measures
Measure
Humira
n=135 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in DAS28-4/CRP at Week 24
-1.57 units on a scale
Standard Deviation 1.36

PRIMARY outcome

Timeframe: Baseline, Week 4

Population: participants in the efficacy analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=158 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Serum MMP3 Level at Week 4
-72.18 ng/mL
Standard Deviation 138.24

PRIMARY outcome

Timeframe: Baseline, Week 8

Population: participants in the efficacy analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=131 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Serum MMP3 Level at Week 8
-83.36 ng/mL
Standard Deviation 159.27

PRIMARY outcome

Timeframe: Baseline, Week 12

Population: participants in the efficacy analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=140 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Serum MMP3 Level at Week 12
-78.05 ng/mL
Standard Deviation 144.73

PRIMARY outcome

Timeframe: Baseline, Week 16

Population: participants in the efficacy analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=148 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Serum MMP3 Level at Week 16
-86.28 ng/mL
Standard Deviation 178.51

PRIMARY outcome

Timeframe: Baseline, Week 24

Population: participants in the efficacy analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=146 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Serum MMP3 Level at Week 24
-98.67 ng/mL
Standard Deviation 185.07

PRIMARY outcome

Timeframe: Baseline, Week 4

Population: participants in the efficacy analysis set with an assessment

A VAS was used for the Physician Global Assessment of disease activity (current status). The left end of the VAS scale (0 mm) signifies the absence of symptoms and the right end (100 mm) signifies maximum disease activity. A negative change from baseline indicates improvement.

Outcome measures

Outcome measures
Measure
Humira
n=152 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Physician Global Assessment (VAS) at Week 4
-15.5 mm
Standard Deviation 20.8

PRIMARY outcome

Timeframe: Baseline, Week 8

Population: participants in the efficacy analysis set with an assessment

A VAS was used for the Physician Global Assessment of disease activity (current status). The left end of the VAS scale (0 mm) signifies the absence of symptoms and the right end (100 mm) signifies maximum disease activity. A negative change from baseline indicates improvement.

Outcome measures

Outcome measures
Measure
Humira
n=132 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Physician Global Assessment (VAS) at Week 8
-21.5 mm
Standard Deviation 23.7

PRIMARY outcome

Timeframe: Baseline, Week 12

Population: participants in the efficacy analysis set with an assessment

A VAS was used for the Physician Global Assessment of disease activity (current status). The left end of the VAS scale (0 mm) signifies the absence of symptoms and the right end (100 mm) signifies maximum disease activity. A negative change from baseline indicates improvement.

Outcome measures

Outcome measures
Measure
Humira
n=132 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Physician Global Assessment (VAS) at Week 12
-21.8 mm
Standard Deviation 25.8

PRIMARY outcome

Timeframe: Baseline, Week 16

Population: participants in the efficacy analysis set with an assessment

A VAS was used for the Physician Global Assessment of disease activity (current status). The left end of the VAS scale (0 mm) signifies the absence of symptoms and the right end (100 mm) signifies maximum disease activity. A negative change from baseline indicates improvement.

Outcome measures

Outcome measures
Measure
Humira
n=136 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Physician Global Assessment (VAS) at Week 16
-25.3 mm
Standard Deviation 24.9

PRIMARY outcome

Timeframe: Baseline, Week 24

Population: participants in the efficacy analysis set with an assessment

A VAS was used for the Physician Global Assessment of disease activity (current status). The left end of the VAS scale (0 mm) signifies the absence of symptoms and the right end (100 mm) signifies maximum disease activity. A negative change from baseline indicates improvement.

Outcome measures

Outcome measures
Measure
Humira
n=136 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Physician Global Assessment (VAS) at Week 24
-27.0 mm
Standard Deviation 27.9

PRIMARY outcome

Timeframe: Baseline, Week 24

Population: participants in the efficacy analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=33 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Anti-Cyclic Citrullinated Peptide Antibodies at Week 24
-45.03 U/mL
Standard Deviation 98.58

PRIMARY outcome

Timeframe: Baseline, Week 4

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=152 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Height at Week 4
0.24 cm
Standard Deviation 0.65

PRIMARY outcome

Timeframe: Baseline, Week 8

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=130 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Height at Week 8
0.59 cm
Standard Deviation 0.92

PRIMARY outcome

Timeframe: Baseline, Week 12

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=146 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Height at Week 12
0.88 cm
Standard Deviation 0.96

PRIMARY outcome

Timeframe: Baseline, Week 16

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=154 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Height at Week 16
1.25 cm
Standard Deviation 1.40

PRIMARY outcome

Timeframe: Baseline, Week 24

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=164 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Height at Week 24
1.60 cm
Standard Deviation 1.63

PRIMARY outcome

Timeframe: Baseline, Week 4

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=164 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Weight at Week 4
0.47 kg
Standard Deviation 1.22

PRIMARY outcome

Timeframe: Baseline, Week 8

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=139 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Weight at Week 8
0.82 kg
Standard Deviation 1.56

PRIMARY outcome

Timeframe: Baseline, Week 12

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=158 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Weight at Week 12
1.10 kg
Standard Deviation 1.90

PRIMARY outcome

Timeframe: Baseline, Week 16

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=166 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Weight at Week 16
1.37 kg
Standard Deviation 2.14

PRIMARY outcome

Timeframe: Baseline, Week 24

Population: participants in the safety analysis set with an assessment

Outcome measures

Outcome measures
Measure
Humira
n=174 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Change From Baseline in Weight at Week 24
1.76 kg
Standard Deviation 2.34

OTHER_PRE_SPECIFIED outcome

Timeframe: up to Week 24

Population: participants in the safety analysis set with an assessment

Adverse drug reactions are defined and totaled as collected adverse events whose causal relation with adalimumab cannot be ruled out. An adverse event refers to any unfavorable and unintended sign (including an abnormal laboratory finding), symptom or disease associated with the use of a drug, whether or not considered related to the drug.

Outcome measures

Outcome measures
Measure
Humira
n=356 Participants
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Number of Participants With Adverse Drug Reactions (ADRs)
ADRs
106 Participants
Number of Participants With Adverse Drug Reactions (ADRs)
Serious ADRs
12 Participants

Adverse Events

Humira

Serious events: 17 serious events
Other events: 20 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Humira
n=356 participants at risk
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Infections and infestations
Appendicitis
0.28%
1/356 • up to Week 24
Infections and infestations
Bronchitis
0.28%
1/356 • up to Week 24
Infections and infestations
Disseminated tuberculosis
0.28%
1/356 • up to Week 24
Infections and infestations
Pharyngitis
0.56%
2/356 • up to Week 24
Infections and infestations
Pulmonary tuberculosis
0.28%
1/356 • up to Week 24
Infections and infestations
Salpingitis
0.28%
1/356 • up to Week 24
Infections and infestations
Tonsillitis
0.56%
2/356 • up to Week 24
Infections and infestations
Upper respiratory tract infection
0.28%
1/356 • up to Week 24
Blood and lymphatic system disorders
Lymphadenitis
0.28%
1/356 • up to Week 24
Metabolism and nutrition disorders
Hyponatraemia
0.28%
1/356 • up to Week 24
Metabolism and nutrition disorders
Water intoxication
0.28%
1/356 • up to Week 24
Nervous system disorders
Epilepsy
0.28%
1/356 • up to Week 24
Nervous system disorders
Febrile convulsion
0.28%
1/356 • up to Week 24
Eye disorders
Papillophlebitis
0.28%
1/356 • up to Week 24
Respiratory, thoracic and mediastinal disorders
Adenoidal hypertrophy
0.28%
1/356 • up to Week 24
Respiratory, thoracic and mediastinal disorders
Tonsillar hypertrophy
0.28%
1/356 • up to Week 24
Gastrointestinal disorders
Stomatitis
0.28%
1/356 • up to Week 24
Gastrointestinal disorders
Gastric mucosal lesion
0.28%
1/356 • up to Week 24
Musculoskeletal and connective tissue disorders
Arthralgia
0.28%
1/356 • up to Week 24
Musculoskeletal and connective tissue disorders
Arthritis
0.56%
2/356 • up to Week 24
Musculoskeletal and connective tissue disorders
Mixed connective tissue disease
0.28%
1/356 • up to Week 24
Musculoskeletal and connective tissue disorders
Osteonecrosis
0.28%
1/356 • up to Week 24
Musculoskeletal and connective tissue disorders
Temporomandibular joint syndrome
0.28%
1/356 • up to Week 24
Musculoskeletal and connective tissue disorders
Juvenile idiopathic arthritis
0.28%
1/356 • up to Week 24

Other adverse events

Other adverse events
Measure
Humira
n=356 participants at risk
Participants with juvenile idiopathic arthritis who received Humira (adalimumab).
Respiratory, thoracic and mediastinal disorders
Upper respiratory tract inflammation
5.6%
20/356 • up to Week 24

Additional Information

Global Medical Services

AbbVie

Phone: 800-633-9110

Results disclosure agreements

  • Principal investigator is a sponsor employee AbbVie requests that any investigator or institution that plans on presenting/publishing results disclosure, provide written notification of their request 60 days prior to their presentation/publication. AbbVie requests that no presentation/publication will be instituted until 12 months after a study is completed, or after the first presentation/publication whichever occurs first. A delay may be proposed of a presentation/publication if AbbVie needs to secure patent or proprietary protection.
  • Publication restrictions are in place

Restriction type: OTHER