Trial Outcomes & Findings for Effect of Ketoconazole on Breathlessness (NCT NCT01378520)

NCT ID: NCT01378520

Last Updated: 2018-06-01

Results Overview

The average of all ratings for the unpleasantness of breathlessness at equivalent times for each subject during Resistive Load Breathing (RLB). For example, if 1 subject provided 6 ratings during 6 minutes of RLB with Ketoconazole and 10 ratings during 10 minutes of RLB with inert powder, then ratings for unpleasantness through 6 minutes were used for analysis for that patient. This approach was used for all subjects to yield a total of 252 ratings for Ketoconazole and for inert powder. Subject rating of intensity of unpleasantness was obtained during RLB on a 100 mm Visual Analog Scale anchored at the bottom by "No Unpleasantness" and at the top by "Greatest Unpleasantness".

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

20 participants

Primary outcome timeframe

At 1 minute intervals during Resistive Load Breathing at Period 1 (Day 3 or 4) and Period 2 (Day 5, 6 or 7)

Results posted on

2018-06-01

Participant Flow

June 2011 - January 2012; medical center

23 subjects recruited; 1 excluded (did not meet inclusion/exclusion criteria); 2 withdrawn prior to randomization (1 could not tolerate breathing through the initial inspiratory resistance (15 cm H 2 O/L/s); 1 gave ratings of breathlessness of \< 50 mm on the VAS for the highest resistance (50 cm H2O/L/s))

Participant milestones

Participant milestones
Measure
First Ketoconazole, Then Inert Powder
Ketoconzaole (600 mg taken orally) in first intervention period and inert powder (in capsule taken orally) in second intervention period.
First Inert Powder, Then Ketoconazole
Inert powder (in capsule taken orally) in first intervention period and Ketoconzaole (600 mg taken orally) in second intervention period.
First Intervention (Day 2-3)
STARTED
10
10
First Intervention (Day 2-3)
COMPLETED
10
10
First Intervention (Day 2-3)
NOT COMPLETED
0
0
Second Intervention (Day 4-6)
STARTED
10
10
Second Intervention (Day 4-6)
COMPLETED
10
10
Second Intervention (Day 4-6)
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Effect of Ketoconazole on Breathlessness

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Entire Study Population
n=20 Participants
Includes groups randomized to receive Ketoconazole first and inert powder first.
Age, Continuous
69.6 years
STANDARD_DEVIATION 6.9 • n=99 Participants
Sex: Female, Male
Female
10 Participants
n=99 Participants
Sex: Female, Male
Male
10 Participants
n=99 Participants
Region of Enrollment
United States
20 participants
n=99 Participants

PRIMARY outcome

Timeframe: At 1 minute intervals during Resistive Load Breathing at Period 1 (Day 3 or 4) and Period 2 (Day 5, 6 or 7)

The average of all ratings for the unpleasantness of breathlessness at equivalent times for each subject during Resistive Load Breathing (RLB). For example, if 1 subject provided 6 ratings during 6 minutes of RLB with Ketoconazole and 10 ratings during 10 minutes of RLB with inert powder, then ratings for unpleasantness through 6 minutes were used for analysis for that patient. This approach was used for all subjects to yield a total of 252 ratings for Ketoconazole and for inert powder. Subject rating of intensity of unpleasantness was obtained during RLB on a 100 mm Visual Analog Scale anchored at the bottom by "No Unpleasantness" and at the top by "Greatest Unpleasantness".

Outcome measures

Outcome measures
Measure
Ketoconazole
n=20 Participants
Ketoconazole (600 mg given orally)
Inert Powder
n=20 Participants
Inert powder (in capsule taken orally)
Unpleasantness of Breathlessness
72.5 units on a scale
Standard Deviation 23.8
72.6 units on a scale
Standard Deviation 23.5

PRIMARY outcome

Timeframe: At 1 minute intervals during Resistive Load Breathing at Period 1 (Day 3 or 4) and Period 2 (Day 5, 6 or 7)

The average of all ratings for the intensity of breathlessness at equivalent times for each subject during Resistive Load Breathing (RLB). For example, if 1 subject provided 6 ratings during 6 minutes of RLB with Ketoconazole and 10 ratings during 10 minutes of RLB with inert powder, then ratings for intensity through 6 minutes were used for analysis for that patient. This approach was used for all subjects to yield a total of 252 ratings for Ketoconazole and for inert powder. Subject rating of intensity of breathlessness was obtained at 1 minute intervals during RLB on a 100 mm Visual Analog Scale anchored at the bottom by "No Intensity" and at the top by "Greatest Intensity".

Outcome measures

Outcome measures
Measure
Ketoconazole
n=20 Participants
Ketoconazole (600 mg given orally)
Inert Powder
n=20 Participants
Inert powder (in capsule taken orally)
Intensity of Breathlessness
77.6 units on a scale
Standard Deviation 22.3
78.2 units on a scale
Standard Deviation 21.4

SECONDARY outcome

Timeframe: At the end of resistance load breathing (4.5 hours after receiving the test article)

Change between pre-treatment and post treatment serum levels of beta-endorphin immunoreactivity measured in pmol/L

Outcome measures

Outcome measures
Measure
Ketoconazole
n=20 Participants
Ketoconazole (600 mg given orally)
Inert Powder
n=20 Participants
Inert powder (in capsule taken orally)
Change in Level of B-endorphin Immunoreactivity
153.9 pmol/L
Standard Deviation 18.0
93.9 pmol/L
Standard Deviation 7.9

Adverse Events

Ketoconazole

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Inert Powder

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Donald A. Mahler, M.D.

Dartmouth-Hitchcock

Phone: 603 650-5533

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place