Home Therapy With VPRIV in Gaucher's Disease
NCT01356537 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 34
Last updated 2021-03-17
Summary
The purpose of this study is to proof increasing patient satisfaction and preservation of quality of life in patients with Gaucher's Disease receiving their enzyme replacement therapy with VPRIV (Velaglucerase alfa)at their home setting compared to receiving the infusions at the clinic or at doctor's practice.
Conditions
- Gaucher Disease
Sponsors & Collaborators
-
Shire
lead INDUSTRY
Principal Investigators
-
Study Director · Takeda
Eligibility
- Min Age
- 2 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2011-05-20
- Primary Completion
- 2017-09-30
- Completion
- 2017-09-30
Countries
- Austria
- Germany
Study Locations
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