Trial Outcomes & Findings for Survey of Osteoarthritis Real World Therapies (MK-0663-140) (NCT NCT01294696)

NCT ID: NCT01294696

Last Updated: 2024-08-29

Results Overview

Participant pain at baseline was recorded using the Brief Pain Inventory (BPI). The BPI is an inventory of subject-reported questions, where for each pain severity item the response scale is 0 = No Pain and 10 = Worst Pain You Can Imagine. The questions refer to pain due to osteoarthritis in the affected knee in the last week: at its worst, at its least, on the average, and right now. Adequate pain control was defined as a score of \<=4 on question 5 of the BPI. Inadequate pain control was defined as a score \>4 on question 5 of the BPI. Question 5 of the BPI asked participants to rate their pain by circling the number that best describes their pain on the average scale from 0 to 10 (with 0=no pain and 10=worst pain imaginable).

Recruitment status

COMPLETED

Target enrollment

1261 participants

Primary outcome timeframe

Baseline (Day 1)

Results posted on

2024-08-29

Participant Flow

The study was conducted in 54 trial centers: 18 in France; 4 in Italy; 5 in The Netherlands; 5 in Portugal; and 9 in the United Kingdom.

Participant milestones

Participant milestones
Measure
All Enrolled Participants
The population consisted of all enrolled participants with adequate and inadequate pain relief.
Overall Study
STARTED
1261
Overall Study
COMPLETED
1187
Overall Study
NOT COMPLETED
74

Reasons for withdrawal

Reasons for withdrawal
Measure
All Enrolled Participants
The population consisted of all enrolled participants with adequate and inadequate pain relief.
Overall Study
Screening failures
7
Overall Study
Protocol Violation
8
Overall Study
Missing BPI Response
7
Overall Study
Site closure
52

Baseline Characteristics

Survey of Osteoarthritis Real World Therapies (MK-0663-140)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Participants With Adequate Pain Relief
n=548 Participants
Adequate pain relief was defined as an average pain score of \<=4 on the Brief Pain Inventory (BPI). Baseline characteristics are only reported for participants with data available at baseline.
Participants With Inadequate Pain Relief
n=639 Participants
Inadequate pain relief was defined as an average pain score of \>4 on the BPI. Baseline characteristics are only reported for participants with data available at baseline.
Total
n=1187 Participants
Total of all reporting groups
Age, Continuous
67.6 Years
STANDARD_DEVIATION 9.03 • n=99 Participants
68.0 Years
STANDARD_DEVIATION 9.76 • n=107 Participants
67.8 Years
STANDARD_DEVIATION 9.43 • n=206 Participants
Sex: Female, Male
Female
329 Participants
n=99 Participants
479 Participants
n=107 Participants
808 Participants
n=206 Participants
Sex: Female, Male
Male
219 Participants
n=99 Participants
160 Participants
n=107 Participants
379 Participants
n=206 Participants

PRIMARY outcome

Timeframe: Baseline (Day 1)

Population: The population consisted of all participants for which a BPI value was available at baseline.

Participant pain at baseline was recorded using the Brief Pain Inventory (BPI). The BPI is an inventory of subject-reported questions, where for each pain severity item the response scale is 0 = No Pain and 10 = Worst Pain You Can Imagine. The questions refer to pain due to osteoarthritis in the affected knee in the last week: at its worst, at its least, on the average, and right now. Adequate pain control was defined as a score of \<=4 on question 5 of the BPI. Inadequate pain control was defined as a score \>4 on question 5 of the BPI. Question 5 of the BPI asked participants to rate their pain by circling the number that best describes their pain on the average scale from 0 to 10 (with 0=no pain and 10=worst pain imaginable).

Outcome measures

Outcome measures
Measure
All Enrolled Participants
n=1187 Participants
All enrolled participants that were treated with the local standard of care for osteoarthritis of the knee.
Percentage of Participants Who Reported Adequate vs. Inadequate Pain Relief at Baseline
Adequate Pain Relief
46.2 Percentage of Participants
Percentage of Participants Who Reported Adequate vs. Inadequate Pain Relief at Baseline
Inadequate Pain Relief
53.8 Percentage of Participants

PRIMARY outcome

Timeframe: Month 12

Population: The population consisted of all participants for which a BPI value was avaialble at Month 12.

Participant pain at baseline was recorded using the Brief Pain Inventory (BPI). The BPI is an inventory of subject-reported questions, where for each pain severity item the response scale is 0 = No Pain and 10 = Worst Pain You Can Imagine. The questions refer to pain in the last week: at its worst, at its least, on the average, and right now. Adequate pain control was defined as a score of \<=4 on question 5 of the BPI. Inadequate pain control was defined as a score \>4 on question 5 of the BPI. Question 5 of the BPI asked participants to rate their pain by circling the number that best describes their pain on the average scale from 0 to 10 (with 0=no pain and 10=worst pain imaginable).

Outcome measures

Outcome measures
Measure
All Enrolled Participants
n=1074 Participants
All enrolled participants that were treated with the local standard of care for osteoarthritis of the knee.
Percentage of Participants Who Reported Adequate vs. Inadequate Pain Relief at Month 12
Adequate Pain Relief
47.3 Percentage of Participants
Percentage of Participants Who Reported Adequate vs. Inadequate Pain Relief at Month 12
Inadequate Pain Relief
52.7 Percentage of Participants

SECONDARY outcome

Timeframe: Baseline (Day 1)

Population: The population consisted of all participants for which WOMAC VA 3.0 data for joint stiffness and limiation in physical function were available at Baseline.

Joint stiffness or limitation in physical function was evaluated using the Western Ontario and McMasters Universities (WOMAC) visual analog (VA)3.0 Index. The WOMAC VA 3.0 is a self-administered, tri-dimensional, disease-specific health status measure. It probes clinically important, subject-relevant symptoms in the areas of pain, joint stiffness and physical function in subjects with osteoarthritis of the knee. The index consists of 24 questions (5 pain, 2 stiffness and 17 physical function) and uses a VA scale of 0-500 mm for pain, 0-200 mm for stiffness, and 0-1700 for physical limitation with higher scores indicating poorer outcomes. Adequate pain was defined as participants reporting less than 4 on the BPI average pain scale.

Outcome measures

Outcome measures
Measure
All Enrolled Participants
n=1097 Participants
All enrolled participants that were treated with the local standard of care for osteoarthritis of the knee.
Percentage of Participants Who Reported Adequate Relief From Joint Stiffness or Limitation in Physical Function at Baseline (Day 1)
43.4 Percentage of Participants

SECONDARY outcome

Timeframe: Month 1

Population: The population consisted of all participants for which a WOMAC VA 3.0 measurement was available at Month 1.

Joint stiffness or limitation in physical function was evaluated using the Western Ontario McMaster Osteoarthritis (WOMAC) visual analog (VA)3.0 Index. The WOMAC VA 3.0 is a self-administered, tri-dimensional, disease-specific health status measure. It probes clinically important, subject-relevant symptoms in the areas of pain, joint stiffness and physical function in subjects with osteoarthritis of the knee. The index consists of 24 questions (5 pain, 2 stiffness and 17 physical function) and uses a VA scale of 0-500 mm for pain, 0-200 mm for stiffness, and 0-1700 for physical limitation with higher scores indicating poorer outcomes. Adequate pain was defined as participants reporting less than 4 on the BPI average pain scale.

Outcome measures

Outcome measures
Measure
All Enrolled Participants
n=1026 Participants
All enrolled participants that were treated with the local standard of care for osteoarthritis of the knee.
Percentage of Participants Who Reported Adequate Relief From Joint Stiffness or Limitation in Physical Function at Month 1
44.8 Percentage of Participants

SECONDARY outcome

Timeframe: Month 3

Population: The population consisted of all participants for which WOMAC VA 3.0 data were available at Month 3.

Joint stiffness or limitation in physical function was evaluated using the Western Ontario and McMasters Universities (WOMAC) visual analog (VA)3.0 Index. The WOMAC VA 3.0 is a self-administered, tri-dimensional, disease-specific health status measure. It probes clinically important, subject-relevant symptoms in the areas of pain, joint stiffness and physical function in subjects with osteoarthritis of the knee. The index consists of 24 questions (5 pain, 2 stiffness and 17 physical function) and uses a VA scale of 0-500 mm for pain, 0-200 mm for stiffness, and 0-1700 for physical limitation with higher scores indicating poorer outcomes. Adequate pain was defined as participants reporting less than 4 on the BPI average pain scale.

Outcome measures

Outcome measures
Measure
All Enrolled Participants
n=1013 Participants
All enrolled participants that were treated with the local standard of care for osteoarthritis of the knee.
Percentage of Participants Who Reported Adequate Relief From Joint Stiffness or Limitation in Physical Function at Month 3
44.7 Percentage of Participants

SECONDARY outcome

Timeframe: Month 6

Population: The population consisted of all participants for which WOMAC VA 3.0 data were available at Month 6.

Joint stiffness or limitation in physical function was evaluated using the Western Ontario and McMasters Universities (WOMAC) visual analog (VA)3.0 Index. The WOMAC VA 3.0 is a self-administered, tri-dimensional, disease-specific health status measure. It probes clinically important, subject-relevant symptoms in the areas of pain, joint stiffness and physical function in subjects with osteoarthritis of the knee. The index consists of 24 questions (5 pain, 2 stiffness and 17 physical function) and uses a VA scale of 0-500 mm for pain, 0-200 mm for stiffness, and 0-1700 for physical limitation with higher scores indicating poorer outcomes. Adequate pain was defined as participants reporting less than 4 on the BPI average pain scale.

Outcome measures

Outcome measures
Measure
All Enrolled Participants
n=1070 Participants
All enrolled participants that were treated with the local standard of care for osteoarthritis of the knee.
Percentage of Participants Who Reported Adequate Relief From Joint Stiffness or Limitation in Physical Function at Month 6
45.3 Percentage of Participants

SECONDARY outcome

Timeframe: Month 9

Population: The population consistated of all participants for which WOMAC VA 3.0 data were available at Month 9.

Joint stiffness or limitation in physical function was evaluated using the Western Ontario and McMasters Universities (WOMAC) visual analog (VA)3.0 Index. The WOMAC VA 3.0 is a self-administered, tri-dimensional, disease-specific health status measure. It probes clinically important, subject-relevant symptoms in the areas of pain, joint stiffness and physical function in subjects with osteoarthritis of the knee. The index consists of 24 questions (5 pain, 2 stiffness and 17 physical function) and uses a VA scale of 0-500 mm for pain, 0-200 mm for stiffness, and 0-1700 for physical limitation with higher scores indicating poorer outcomes. Adequate pain was defined as participants reporting less than 4 on the BPI average pain scale.

Outcome measures

Outcome measures
Measure
All Enrolled Participants
n=1039 Participants
All enrolled participants that were treated with the local standard of care for osteoarthritis of the knee.
Percentage of Participants Who Reported Adequate Relief From Joint Stiffness or Limitation in Physical Function at Month 9
48.6 Percentage of Participants

SECONDARY outcome

Timeframe: Month 12

Population: The population consisted of all participants for which WOMAC VA 3.0 data was available at Month 12.

Joint stiffness or limitation in physical function was evaluated using the Western Ontario and McMasters Universities (WOMAC) visual analog (VA)3.0 Index. The WOMAC VA 3.0 is a self-administered, tri-dimensional, disease-specific health status measure. It probes clinically important, subject-relevant symptoms in the areas of pain, joint stiffness and physical function in subjects with osteoarthritis of the knee. The index consists of 24 questions (5 pain, 2 stiffness and 17 physical function) and uses a VA scale of 0-500 mm for pain, 0-200 mm for stiffness, and 0-1700 for physical limitation with higher scores indicating poorer outcomes. Adequate pain was defined as participants reporting less than 4 on the BPI average pain scale.

Outcome measures

Outcome measures
Measure
All Enrolled Participants
n=1058 Participants
All enrolled participants that were treated with the local standard of care for osteoarthritis of the knee.
Percentage of Participants Who Reported Adequate Relief From Joint Stiffness or Limitation in Physical Function at Month 12
49.6 Percentage of Participants

Adverse Events

Participants With Adequate Pain Relief

Serious events: 11 serious events
Other events: 0 other events
Deaths: 0 deaths

Participants With Inadequate Pain Relief

Serious events: 25 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Participants With Adequate Pain Relief
n=548 participants at risk
Adequate pain relief was fedined as an average pain score of \<=4 on the Brief Pain Inventory (BPI).
Participants With Inadequate Pain Relief
n=639 participants at risk
Inadequate pain relief was defined as an average pain score of \>4 on the BPI. Baseline characteristics are only reported for participants with data available at baseline.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Lung Neoplasm Malignant
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Malignant Melanoma
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Chronic Lymphocytic Leukaemia
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Blood and lymphatic system disorders
Anaemia
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Cardiac disorders
Angina Unstable
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Cardiac disorders
Palpitations
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Eye disorders
Cataract
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 2 • Up to Month 12
Gastrointestinal disorders
Abdominal Distention
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Gastrointestinal disorders
Diarrhoea
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Gastrointestinal disorders
Nausea
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
General disorders
Death
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
General disorders
Oedema Peripheral
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Hepatobiliary disorders
Cholecystitis
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Infections and infestations
Abscess
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Infections and infestations
Cellulitis
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Infections and infestations
Influenza
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Infections and infestations
Localized Infection
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Infections and infestations
Neutropenic Sepsis
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Infections and infestations
Periumbilical Abscess
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Infections and infestations
Pneumonia
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Infections and infestations
Sepsis
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Injury, poisoning and procedural complications
Burns Third Degree
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Injury, poisoning and procedural complications
Fall
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Injury, poisoning and procedural complications
Femoral Neck Fracture
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Injury, poisoning and procedural complications
Fracture
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Injury, poisoning and procedural complications
Radius Fracture
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Injury, poisoning and procedural complications
Wrist Fracture
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Musculoskeletal and connective tissue disorders
Arthralgia
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Musculoskeletal and connective tissue disorders
Arthritis
0.18%
1/548 • Number of events 1 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Musculoskeletal and connective tissue disorders
Bone Pain
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Musculoskeletal and connective tissue disorders
Foot Deformity
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Musculoskeletal and connective tissue disorders
Osteoarthritis
0.00%
0/548 • Up to Month 12
0.63%
4/639 • Number of events 4 • Up to Month 12
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Bladder Neoplasm
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Bladder Transitional Cell Carcinoma
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Neoplasm
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Nervous system disorders
Cerebrovascular Accident
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Nervous system disorders
Haemorrhagic Stroke
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Nervous system disorders
Parkinson's Disease
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Nervous system disorders
Transient Ischaemic Attack
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Renal and urinary disorders
Calculus Bladder
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Renal and urinary disorders
Renal Colic
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Renal and urinary disorders
Urethral Sclerosis
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Respiratory, thoracic and mediastinal disorders
Chronic Respiratory Failure
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Respiratory, thoracic and mediastinal disorders
Pneumonia Aspiration
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12
Respiratory, thoracic and mediastinal disorders
Respiratory Failure
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Skin and subcutaneous tissue disorders
Skin Ulcer
0.00%
0/548 • Up to Month 12
0.16%
1/639 • Number of events 1 • Up to Month 12
Vascular disorders
Hypotension
0.18%
1/548 • Number of events 1 • Up to Month 12
0.00%
0/639 • Up to Month 12

Other adverse events

Adverse event data not reported

Additional Information

Vice President, Late Stage Group Development Leader

Merck Sharp & Dohme Corp

Phone: 1-800-672-6372

Results disclosure agreements

  • Principal investigator is a sponsor employee The Sponsor must have the opportunity to review all proposed abstracts, manuscripts, or presentations regarding this study 60 days prior to submission for publication/presentation.
  • Publication restrictions are in place

Restriction type: OTHER