Trial Outcomes & Findings for Beta Blockers and Angiotensin Receptor Blockers in Bicuspid Aortic Valve Disease Aortopathy (BAV Study) (NCT NCT01202721)

NCT ID: NCT01202721

Last Updated: 2019-09-18

Results Overview

The primary analyses include the evaluation of the effects of monotherapy (atenolol vs. placebo, telmisartan vs. placebo) on the change in aortic root size measured at 3 years. Change is measured in centimeters squared (final measurement - baseline measurement). Original outcome measure time frame was scheduled for 5 years, however due to poor study participant and site recruitment study was closed early and final outcome measures taken at approximately 3 years.

Recruitment status

TERMINATED

Study phase

PHASE3

Target enrollment

85 participants

Primary outcome timeframe

The difference between baseline measures (2012-2013) and Year 3 measure (2015-2016)

Results posted on

2019-09-18

Participant Flow

Participant milestones

Participant milestones
Measure
Atenolol
Atenolol 25 mg up-titrated to 100 mg.
Telmisartan
Telmisartan 40 mg up-titrated to 80mg
Atenolol Placebo
Participants in Atenolol group, randomized to receive matching placebo
Telmisartan Placebo
Participants in Telmisartan group, randomized to receive matching placebo
Overall Study
STARTED
18
26
14
27
Overall Study
COMPLETED
18
26
14
27
Overall Study
NOT COMPLETED
0
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Beta Blockers and Angiotensin Receptor Blockers in Bicuspid Aortic Valve Disease Aortopathy (BAV Study)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Atenolol
n=18 Participants
Atenolol 25 mg up-titrated to 100 mg.
Telmisartan
n=26 Participants
Telmisartan 40 mg up-titrated to 80mg
Atenolol Placebo
n=14 Participants
Participants randomized to receive Atenolol placebo
Telmisartan Placebo
n=27 Participants
Participants randomized to receive Telmisartan placebo
Total
n=85 Participants
Total of all reporting groups
Age, Continuous
43.4 years
STANDARD_DEVIATION 12.8 • n=39 Participants
47 years
STANDARD_DEVIATION 12.2 • n=41 Participants
49.1 years
STANDARD_DEVIATION 13.6 • n=35 Participants
49.1 years
STANDARD_DEVIATION 11.2 • n=31 Participants
47.3 years
STANDARD_DEVIATION 12.3 • n=146 Participants
Sex: Female, Male
Female
5 Participants
n=39 Participants
7 Participants
n=41 Participants
8 Participants
n=35 Participants
7 Participants
n=31 Participants
27 Participants
n=146 Participants
Sex: Female, Male
Male
13 Participants
n=39 Participants
19 Participants
n=41 Participants
6 Participants
n=35 Participants
20 Participants
n=31 Participants
58 Participants
n=146 Participants
Race/Ethnicity, Customized
South Asian
0 Participants
n=39 Participants
0 Participants
n=41 Participants
0 Participants
n=35 Participants
0 Participants
n=31 Participants
0 Participants
n=146 Participants
Race/Ethnicity, Customized
Asian
2 Participants
n=39 Participants
1 Participants
n=41 Participants
1 Participants
n=35 Participants
0 Participants
n=31 Participants
4 Participants
n=146 Participants
Race/Ethnicity, Customized
Black African
0 Participants
n=39 Participants
0 Participants
n=41 Participants
0 Participants
n=35 Participants
1 Participants
n=31 Participants
1 Participants
n=146 Participants
Race/Ethnicity, Customized
European
15 Participants
n=39 Participants
23 Participants
n=41 Participants
12 Participants
n=35 Participants
26 Participants
n=31 Participants
76 Participants
n=146 Participants
Race/Ethnicity, Customized
Native North American
0 Participants
n=39 Participants
0 Participants
n=41 Participants
0 Participants
n=35 Participants
0 Participants
n=31 Participants
0 Participants
n=146 Participants
Race/Ethnicity, Customized
Other
1 Participants
n=39 Participants
2 Participants
n=41 Participants
1 Participants
n=35 Participants
0 Participants
n=31 Participants
4 Participants
n=146 Participants

PRIMARY outcome

Timeframe: The difference between baseline measures (2012-2013) and Year 3 measure (2015-2016)

Population: Intention to treat analysis method followed: patients completed final visit over the phone where aortic root size cannot be measured; patients refused a final visit, or patient's information was received through a third party. Patients missing primary outcome measures still followed for other analyses.

The primary analyses include the evaluation of the effects of monotherapy (atenolol vs. placebo, telmisartan vs. placebo) on the change in aortic root size measured at 3 years. Change is measured in centimeters squared (final measurement - baseline measurement). Original outcome measure time frame was scheduled for 5 years, however due to poor study participant and site recruitment study was closed early and final outcome measures taken at approximately 3 years.

Outcome measures

Outcome measures
Measure
Atenolol
n=16 Participants
Atenolol 25 mg up-titrated to 100 mg.
Telmisartan
n=23 Participants
Telmisartan 40 mg up-titrated to 80mg
Atenolol Placebo
n=13 Participants
Participants randomized to receive atenolol placebo
Telmisartan Placebo
n=25 Participants
Participants randomized to receive telmisartan placebo
Change From Baseline in Ascending Aorta Size, as Evaluated by MRI
.6 centimeters squared
Standard Deviation 1.4
.4 centimeters squared
Standard Deviation 1.3
.7 centimeters squared
Standard Deviation .8
1 centimeters squared
Standard Deviation 1.6

SECONDARY outcome

Timeframe: The difference between baseline measures (2012-2013) and Year 3 measure (2015-2016)

Population: Discrepancy exists between participant flow numbers and patients analyzed for the following reasons: patients completed final visit over the phone where aortic root size cannot be measured; patients refused a final visit, patient's information was received through a third party. Pt's not removed as they are still included in other analyses

Rate of change in ascending aorta size evaluated by transthoracic echocardiography (ECHO) at 3 years. Change is measured in centimeters squared (final measurement - baseline measurement). Time frame was scheduled for 5 years, however due to poor study participant and site recruitment study was closed early and final outcome measures taken at approximately 3 years.

Outcome measures

Outcome measures
Measure
Atenolol
n=17 Participants
Atenolol 25 mg up-titrated to 100 mg.
Telmisartan
n=21 Participants
Telmisartan 40 mg up-titrated to 80mg
Atenolol Placebo
n=12 Participants
Participants randomized to receive atenolol placebo
Telmisartan Placebo
n=23 Participants
Participants randomized to receive telmisartan placebo
Rate of Change in Ascending Aorta Size Evaluated by Transthoracic Echocardiography (TEE)
-.9 centimetres squared
Standard Deviation 3.2
-.2 centimetres squared
Standard Deviation 4.5
-1.6 centimetres squared
Standard Deviation 4.3
.3 centimetres squared
Standard Deviation 2.8

Adverse Events

Atenolol

Serious events: 0 serious events
Other events: 10 other events
Deaths: 0 deaths

Telmisartan

Serious events: 2 serious events
Other events: 13 other events
Deaths: 0 deaths

Atenolol Placebo

Serious events: 1 serious events
Other events: 10 other events
Deaths: 0 deaths

Telmisartan Placebo

Serious events: 2 serious events
Other events: 18 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Atenolol
n=18 participants at risk
Atenolol 25 mg up-titrated to 100 mg.
Telmisartan
n=26 participants at risk
Telmisartan 40 mg up-titrated to 80mg
Atenolol Placebo
n=14 participants at risk
Participants randomized to receive atenolol placebo
Telmisartan Placebo
n=27 participants at risk
Participants randomized to receive telmisartan placebo
General disorders
Unexpected Serious Adverse Event
0.00%
0/18
7.7%
2/26
7.1%
1/14
7.4%
2/27

Other adverse events

Other adverse events
Measure
Atenolol
n=18 participants at risk
Atenolol 25 mg up-titrated to 100 mg.
Telmisartan
n=26 participants at risk
Telmisartan 40 mg up-titrated to 80mg
Atenolol Placebo
n=14 participants at risk
Participants randomized to receive atenolol placebo
Telmisartan Placebo
n=27 participants at risk
Participants randomized to receive telmisartan placebo
Cardiac disorders
Chest Pain
16.7%
3/18
11.5%
3/26
7.1%
1/14
7.4%
2/27
Cardiac disorders
Shortness of Breath
16.7%
3/18
3.8%
1/26
7.1%
1/14
14.8%
4/27
Vascular disorders
Dizziness
16.7%
3/18
23.1%
6/26
28.6%
4/14
14.8%
4/27
Vascular disorders
Syncope
0.00%
0/18
0.00%
0/26
0.00%
0/14
3.7%
1/27
Investigations
Other
5.6%
1/18
11.5%
3/26
28.6%
4/14
25.9%
7/27

Additional Information

Dr. Tara McCready, Program Director

Population Health Research Institute

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place