Trial Outcomes & Findings for Effect of Guanfacine Extended-Release on Attention Deficit Hyperactivity Disorder (ADHD)-Associated Insomnia (NCT NCT01156051)

NCT ID: NCT01156051

Last Updated: 2014-08-11

Results Overview

Change in objective measures of sleep, using polysomnography

Recruitment status

TERMINATED

Study phase

PHASE4

Target enrollment

29 participants

Primary outcome timeframe

Baseline to last observation carried forward (after at least one week of dose stability)

Results posted on

2014-08-11

Participant Flow

From 2010 to 2012, children were referred primarily from the outpatient practice affiliated with a community based hospital dedicated to the evaluation and management of children with special needs. Four patients were referred from community pediatricians who commonly refer to the practice.

Medications for ADHD, that would affect sleep/alertness, or that had psychoactive properties were discontinued prior to polysomnography. Of the 35 who entered screening, 29 were enrolled. Children were disquialified for not meeting diagnostic criteria or for having disqualifying conditions (e.g., depression, heart pathology).

Participant milestones

Participant milestones
Measure
Treatment Group
Children who received (double blinded, randomized) guanfacine extended release tablets in a flexible dosing protocol, with doses ranging from 1mg to 4mg administered once daily in the morning.
Control
Children who received a matching placebo tablet administered once daily in the morning in a flexible dosing protocol, with tablets identical to guanfacine extended release from 1mg to 4mg.
Overall Study
STARTED
12
17
Overall Study
COMPLETED
11
16
Overall Study
NOT COMPLETED
1
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Treatment Group
Children who received (double blinded, randomized) guanfacine extended release tablets in a flexible dosing protocol, with doses ranging from 1mg to 4mg administered once daily in the morning.
Control
Children who received a matching placebo tablet administered once daily in the morning in a flexible dosing protocol, with tablets identical to guanfacine extended release from 1mg to 4mg.
Overall Study
Lost to Follow-up
1
0
Overall Study
patient not compliant with protocol
0
1

Baseline Characteristics

Effect of Guanfacine Extended-Release on Attention Deficit Hyperactivity Disorder (ADHD)-Associated Insomnia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Guanfacine Extended-Release Tablets
n=11 Participants
Guanfacine Extended-Release Tablets 1mg, 2mg, 3mg, and 4mg Guanfacine extended-release tablets: Guanfacine extended-release tablets were started at 1mg and then increased at weekly intervals to 2mg, 3mg, or 4mg as needed and as tolerated
Placebo Comparator
n=16 Participants
Placebo control Placebo comparator: Placebo tablets identical to the experimental arm guanfacine extended-release tablets 1mg were started and then increased at weekly intervals to 2mg, 3mg, or 4mg as needed and as tolerated
Total
n=27 Participants
Total of all reporting groups
Age, Continuous
9.1 years
STANDARD_DEVIATION 1.8 • n=99 Participants
8.8 years
STANDARD_DEVIATION 1.9 • n=107 Participants
8.9 years
STANDARD_DEVIATION 1.9 • n=206 Participants
Sex: Female, Male
Female
2 Participants
n=99 Participants
8 Participants
n=107 Participants
10 Participants
n=206 Participants
Sex: Female, Male
Male
9 Participants
n=99 Participants
8 Participants
n=107 Participants
17 Participants
n=206 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=99 Participants
2 Participants
n=107 Participants
2 Participants
n=206 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
11 Participants
n=99 Participants
14 Participants
n=107 Participants
25 Participants
n=206 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Race/Ethnicity, Customized
White
10 participants
n=99 Participants
12 participants
n=107 Participants
22 participants
n=206 Participants
Race/Ethnicity, Customized
African-American
1 participants
n=99 Participants
4 participants
n=107 Participants
5 participants
n=206 Participants
Region of Enrollment
United States
11 participants
n=99 Participants
16 participants
n=107 Participants
27 participants
n=206 Participants

PRIMARY outcome

Timeframe: Baseline to last observation carried forward (after at least one week of dose stability)

Population: 29 children were enrolled, one (treatment) was lost to follow up an one (placebo) was discontinued due to noncompliance with protocol.

Change in objective measures of sleep, using polysomnography

Outcome measures

Outcome measures
Measure
Guanfacine Extended-Release Tablets
n=11 Participants
Guanfacine Extended-Release Tablets 1mg, 2mg, 3mg, and 4mg Guanfacine extended-release tablets: Guanfacine extended-release tablets will be started at 1mg and then increased at weekly intervals to 2mg, 3mg, or 4mg as needed and as tolerated
Placebo Comparator
n=16 Participants
Placebo control Placebo comparator: Placebo tablets identical to the experimental arm guanfacine extended-release tablets 1mg, 2mg, 3mg, 4mg, but without the active ingredient (guanfacine).
Change in Polysomnographic Total Sleep Time (TST)
-57.32 minutes
Standard Deviation 89.17
31.32 minutes
Standard Deviation 59.54

SECONDARY outcome

Timeframe: Baseline to last observation carried forward (after at least one week of dose stability)

Population: 29 children enrolled, but two were discontinued before termination data was available: one (treatment) was lost to follow up and one (placebo) was noncompliant with the protocol.

Change in baseline to treatment ADHD-Rating Scale IV (Investigator-interview ) total. This scale quantitates ADHD symptoms based on DSM-IV criteria with a minimum score of 0 and a maximum score of 54 (higher scores suggesting more ADHD symptoms). The total score is a sum of the 9 items on the ADHD Rating Scale IV inattention score and the 9 items on the ADHD Rating Scale IV hyperactivity-impulsivity score (scores for each 0-27).

Outcome measures

Outcome measures
Measure
Guanfacine Extended-Release Tablets
n=11 Participants
Guanfacine Extended-Release Tablets 1mg, 2mg, 3mg, and 4mg Guanfacine extended-release tablets: Guanfacine extended-release tablets will be started at 1mg and then increased at weekly intervals to 2mg, 3mg, or 4mg as needed and as tolerated
Placebo Comparator
n=16 Participants
Placebo control Placebo comparator: Placebo tablets identical to the experimental arm guanfacine extended-release tablets 1mg, 2mg, 3mg, 4mg, but without the active ingredient (guanfacine).
Change in Baseline to Treatment ADHD-Rating Scale IV Total Score
-18.27 units on a scale
Standard Deviation 11.31
-1.69 units on a scale
Standard Deviation 9.16

SECONDARY outcome

Timeframe: Baseline to last observation carried forward (after at least one week of dose stability)

Population: 29 children were enrolled; two were disqualified: one (treatment) was lost to follow-up,and one (placebo) was noncompliant with the protocol.

Change in an objective measure of sleep onset, using polysomnography.

Outcome measures

Outcome measures
Measure
Guanfacine Extended-Release Tablets
n=11 Participants
Guanfacine Extended-Release Tablets 1mg, 2mg, 3mg, and 4mg Guanfacine extended-release tablets: Guanfacine extended-release tablets will be started at 1mg and then increased at weekly intervals to 2mg, 3mg, or 4mg as needed and as tolerated
Placebo Comparator
n=16 Participants
Placebo control Placebo comparator: Placebo tablets identical to the experimental arm guanfacine extended-release tablets 1mg, 2mg, 3mg, 4mg, but without the active ingredient (guanfacine).
Change in Baseline to Treatment Latency to Persistent Sleep (LPS)
10.54 minutes
Standard Deviation 88.44
-19.94 minutes
Standard Deviation 54.12

SECONDARY outcome

Timeframe: Baseline to last observation carried forward (after at least one week of dose stability)

Population: 29 children were enrolled; two were disqualified: one (treatment) was lost to follow-up,and one (placebo) was noncompliant with the protocol.

Polysomnographic parameter of sleep assessing how many minutes of wakefulness occurred after sleep onset and before full morning awakening.

Outcome measures

Outcome measures
Measure
Guanfacine Extended-Release Tablets
n=11 Participants
Guanfacine Extended-Release Tablets 1mg, 2mg, 3mg, and 4mg Guanfacine extended-release tablets: Guanfacine extended-release tablets will be started at 1mg and then increased at weekly intervals to 2mg, 3mg, or 4mg as needed and as tolerated
Placebo Comparator
n=16 Participants
Placebo control Placebo comparator: Placebo tablets identical to the experimental arm guanfacine extended-release tablets 1mg, 2mg, 3mg, 4mg, but without the active ingredient (guanfacine).
Change in Baseline to Treatment Minutes of Wake Time After Sleep Onset (WASO)
21.80 minutes
Standard Deviation 18.51
-3.90 minutes
Standard Deviation 17.20

Adverse Events

Guanfacine Extended-Release Tablets

Serious events: 0 serious events
Other events: 9 other events
Deaths: 0 deaths

Placebo Comparator

Serious events: 0 serious events
Other events: 11 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Guanfacine Extended-Release Tablets
n=12 participants at risk
Guanfacine Extended-Release Tablets 1mg, 2mg, 3mg, and 4mg Guanfacine extended-release tablets: Guanfacine extended-release tablets will be started at 1mg and then increased at weekly intervals to 2mg, 3mg, or 4mg as needed and as tolerated
Placebo Comparator
n=17 participants at risk
Placebo control Placebo comparator: Placebo tablets identical to the experimental arm guanfacine extended-release tablets 1mg, 2mg, 3mg, 4mg, but without the active ingredient (guanfacine).
Nervous system disorders
somnolence / sedation
66.7%
8/12 • Number of events 8
5.9%
1/17 • Number of events 1
Nervous system disorders
headache
33.3%
4/12 • Number of events 4
11.8%
2/17 • Number of events 2
Gastrointestinal disorders
stomachache / abdominal pain
8.3%
1/12 • Number of events 1
11.8%
2/17 • Number of events 2
Gastrointestinal disorders
acute gastroenteritis
8.3%
1/12 • Number of events 1
11.8%
2/17 • Number of events 2
Metabolism and nutrition disorders
decreased appetite
0.00%
0/12
5.9%
1/17 • Number of events 1
Gastrointestinal disorders
inguinal hernia
0.00%
0/12
5.9%
1/17 • Number of events 1
Infections and infestations
febrile illness
8.3%
1/12 • Number of events 1
0.00%
0/17
Infections and infestations
upper respiratory infection
25.0%
3/12 • Number of events 3
17.6%
3/17 • Number of events 3
Respiratory, thoracic and mediastinal disorders
exacerbation of allergic rhinitis
8.3%
1/12 • Number of events 1
29.4%
5/17 • Number of events 5
Respiratory, thoracic and mediastinal disorders
exacerbation of asthma
0.00%
0/12
5.9%
1/17 • Number of events 1
Respiratory, thoracic and mediastinal disorders
cough
8.3%
1/12 • Number of events 1
0.00%
0/17
Renal and urinary disorders
enuresis
8.3%
1/12 • Number of events 1
0.00%
0/17
Nervous system disorders
dizziness
8.3%
1/12 • Number of events 1
0.00%
0/17
Musculoskeletal and connective tissue disorders
musculoskeletal chest pain
8.3%
1/12 • Number of events 1
0.00%
0/17
General disorders
oral pain due to loose teeth
8.3%
1/12 • Number of events 1
0.00%
0/17
Skin and subcutaneous tissue disorders
dermatitis
8.3%
1/12 • Number of events 1
11.8%
2/17 • Number of events 2
Psychiatric disorders
stuttering
0.00%
0/12
5.9%
1/17 • Number of events 1

Additional Information

Thomas A Rugino MD

Children's Specialized Hospital

Phone: 732-797-3826

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place