Trial Outcomes & Findings for Study of Asthma Phenotypes and Pharmacogenomic Interactions by Race-Ethnicity (SAPPHIRE) (NCT NCT01142947)

NCT ID: NCT01142947

Last Updated: 2019-04-02

Results Overview

Patients will be treated with 6 weeks of inhaled beclomethasone diproprionate (BD) treatment and the change in Asthma Control Test (ACT) quantified. The composite ACT score measured at each time point ranged from 5-25 (with higher scores reflective of better asthma control). Therefore, the absolute change in ACT score from before to after treatment could range from -20 to +20.

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

362 participants

Primary outcome timeframe

6 weeks

Results posted on

2019-04-02

Participant Flow

362 self-reported African American enrolled in 6-week treatment with inhaled beclomethasone dipropionate; 291 returned at the end of treatment; 262 with measurable medication adherence; 244 with genome-wide genotype data.

Participant milestones

Participant milestones
Measure
Beclomethasone Dipropionate (BD)
Patients who meet eligibility criteria will be treated with 6 weeks of beclomethasone dipropionate to assess change in asthma control. This change will be the phenotype used in discovery for the genetic association study. There is no placebo group. beclomethasone dipropionate: 160 mcg twice a day (320 mcg per day total)
Overall Study
STARTED
362
Overall Study
COMPLETED
244
Overall Study
NOT COMPLETED
118

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Some individuals did not have the genome wide genotype data needed to assess genetic ancestry.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Beclomethasone Dipropionate (BD)
n=362 Participants
Patients who meet eligibility criteria will be treated with 6 weeks of beclomethasone dipropionate to assess change in pulmonary function and asthma control. These change will be used as phenotypes in a genetic association study. There is no placebo group. beclomethasone dipropionate: 160 mcg twice a day (320 mcg per day total)
Age, Continuous
32.2 years
STANDARD_DEVIATION 13.0 • n=362 Participants
Sex: Female, Male
Female
216 Participants
n=362 Participants
Sex: Female, Male
Male
146 Participants
n=362 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=362 Participants
Race (NIH/OMB)
Asian
0 Participants
n=362 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=362 Participants
Race (NIH/OMB)
Black or African American
362 Participants
n=362 Participants
Race (NIH/OMB)
White
0 Participants
n=362 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=362 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=362 Participants
Proportion of African Genetic Ancestry
80.6 % African Ancestry (within individuals)
STANDARD_DEVIATION 8.7 • n=330 Participants • Some individuals did not have the genome wide genotype data needed to assess genetic ancestry.
Body Mass Index
32.4 kilograms per meters squared
STANDARD_DEVIATION 9.5 • n=362 Participants
Smoking Status
Never Smoker
315 Participants
n=355 Participants • Smoking status missing on seven individuals
Smoking Status
Past Smoker
37 Participants
n=355 Participants • Smoking status missing on seven individuals
Smoking Status
Current Smoker
3 Participants
n=355 Participants • Smoking status missing on seven individuals
Initial Asthma Control Test Score
17.8 Composite Score
STANDARD_DEVIATION 5.0 • n=354 Participants • Initial ACT score missing in 8 individuals
Percent of Predicted Forced Expiratory Volume at 1 Second
73.0 % of the predicted FEV1
STANDARD_DEVIATION 12.6 • n=362 Participants

PRIMARY outcome

Timeframe: 6 weeks

Patients will be treated with 6 weeks of inhaled beclomethasone diproprionate (BD) treatment and the change in Asthma Control Test (ACT) quantified. The composite ACT score measured at each time point ranged from 5-25 (with higher scores reflective of better asthma control). Therefore, the absolute change in ACT score from before to after treatment could range from -20 to +20.

Outcome measures

Outcome measures
Measure
Beclomethasone Dipropionate (BD)
n=244 Participants
Patients who meet eligibility criteria will be treated with 6 weeks of beclomethasone dipropionate to assess change in pulmonary function and asthma control. These change will be used as phenotypes in a genetic association study. There is no placebo group. beclomethasone dipropionate: 160 mcg twice a day (320 mcg per day total)
Change in Asthma Control Test Score
3.32 change in composite score
Standard Deviation 4.47

Adverse Events

Beclomethasone Dipropionate (BD)

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

L. Keoki Williams, MD, MPH

Center for Individualized and Genomic Medicine Research, Henry Ford Health System

Phone: 313-874-5454

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place