Trial Outcomes & Findings for Cyproheptadine in Preventing Weight Loss in Children Receiving Chemotherapy for Cancer (NCT NCT01132547)

NCT ID: NCT01132547

Last Updated: 2015-07-02

Results Overview

Recruitment status

TERMINATED

Study phase

PHASE3

Target enrollment

22 participants

Primary outcome timeframe

8 weeks

Results posted on

2015-07-02

Participant Flow

Participant milestones

Participant milestones
Measure
Arm I Cyproheptadine Hydrochloride
Patients receive oral cyproheptadine hydrochloride twice daily for 8 weeks. cyproheptadine hydrochloride: Given orally
Arm II Placebo
Patients receive an oral placebo twice daily for 8 weeks. placebo: Given orally
Overall Study
STARTED
9
13
Overall Study
COMPLETED
5
12
Overall Study
NOT COMPLETED
4
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Arm I Cyproheptadine Hydrochloride
Patients receive oral cyproheptadine hydrochloride twice daily for 8 weeks. cyproheptadine hydrochloride: Given orally
Arm II Placebo
Patients receive an oral placebo twice daily for 8 weeks. placebo: Given orally
Overall Study
Withdrawal by Subject
3
1
Overall Study
Death
1
0

Baseline Characteristics

Cyproheptadine in Preventing Weight Loss in Children Receiving Chemotherapy for Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Arm I Cyproheptadine Hydrochloride
n=9 Participants
Patients receive oral cyproheptadine hydrochloride twice daily for 8 weeks. cyproheptadine hydrochloride: Given orally
Arm II Placebo
n=13 Participants
Patients receive an oral placebo twice daily for 8 weeks. placebo: Given orally
Total
n=22 Participants
Total of all reporting groups
Age, Continuous
10.2 years
STANDARD_DEVIATION 5.7 • n=99 Participants
12.0 years
STANDARD_DEVIATION 4.7 • n=107 Participants
11.2 years
STANDARD_DEVIATION 5.1 • n=206 Participants
Sex: Female, Male
Female
3 Participants
n=99 Participants
10 Participants
n=107 Participants
13 Participants
n=206 Participants
Sex: Female, Male
Male
6 Participants
n=99 Participants
3 Participants
n=107 Participants
9 Participants
n=206 Participants
Region of Enrollment
United States
9 participants
n=99 Participants
13 participants
n=107 Participants
22 participants
n=206 Participants

PRIMARY outcome

Timeframe: 8 weeks

Population: LOCF

Outcome measures

Outcome measures
Measure
Arm I Cyproheptadine Hydrochloride
n=9 Participants
Patients receive oral cyproheptadine hydrochloride twice daily for 8 weeks. cyproheptadine hydrochloride: Given orally
Arm II Placebo
n=13 Participants
Patients receive an oral placebo twice daily for 8 weeks. placebo: Given orally
Participant With Weight Loss ≥ 5% at the 8- Week Assessment When Compared to Baseline
0 participants
2 participants

PRIMARY outcome

Timeframe: Baseline and 8 weeks

Population: Completers =

Change from Baseline in Weight Z score

Outcome measures

Outcome measures
Measure
Arm I Cyproheptadine Hydrochloride
n=5 Participants
Patients receive oral cyproheptadine hydrochloride twice daily for 8 weeks. cyproheptadine hydrochloride: Given orally
Arm II Placebo
n=12 Participants
Patients receive an oral placebo twice daily for 8 weeks. placebo: Given orally
Severity of Weight Loss
0.12 Z score
Standard Deviation 1.15
-0.02 Z score
Standard Deviation 0.30

SECONDARY outcome

Timeframe: Baseline and 8 weeks

Population: Completers

Change from Baseline in Weight

Outcome measures

Outcome measures
Measure
Arm I Cyproheptadine Hydrochloride
n=5 Participants
Patients receive oral cyproheptadine hydrochloride twice daily for 8 weeks. cyproheptadine hydrochloride: Given orally
Arm II Placebo
n=12 Participants
Patients receive an oral placebo twice daily for 8 weeks. placebo: Given orally
Pattern of Weight in the Study Population
0.18 Kilograms
Standard Deviation 0.79
-0.32 Kilograms
Standard Deviation 3.13

Adverse Events

Arm I Cyproheptadine Hydrochloride

Serious events: 3 serious events
Other events: 4 other events
Deaths: 0 deaths

Arm II Placebo

Serious events: 0 serious events
Other events: 4 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Arm I Cyproheptadine Hydrochloride
n=9 participants at risk
Patients receive oral cyproheptadine hydrochloride twice daily for 8 weeks. cyproheptadine hydrochloride: Given orally
Arm II Placebo
n=13 participants at risk
Patients receive an oral placebo twice daily for 8 weeks. placebo: Given orally
Nervous system disorders
Intracranial hemorrhage
11.1%
1/9 • Number of events 1
0.00%
0/13
Investigations
Platelet count decrease
22.2%
2/9 • Number of events 2
0.00%
0/13
Blood and lymphatic system disorders
Febrile Neutropenia
22.2%
2/9 • Number of events 3
0.00%
0/13
Investigations
Neutrophil count decrease
11.1%
1/9 • Number of events 2
0.00%
0/13

Other adverse events

Other adverse events
Measure
Arm I Cyproheptadine Hydrochloride
n=9 participants at risk
Patients receive oral cyproheptadine hydrochloride twice daily for 8 weeks. cyproheptadine hydrochloride: Given orally
Arm II Placebo
n=13 participants at risk
Patients receive an oral placebo twice daily for 8 weeks. placebo: Given orally
Blood and lymphatic system disorders
Anemia
22.2%
2/9 • Number of events 4
0.00%
0/13
Blood and lymphatic system disorders
Febrile neutropenia
11.1%
1/9 • Number of events 1
0.00%
0/13
Gastrointestinal disorders
Abdominal pain
11.1%
1/9 • Number of events 1
7.7%
1/13 • Number of events 1
Musculoskeletal and connective tissue disorders
Pain in extremity
11.1%
1/9 • Number of events 1
0.00%
0/13
Nervous system disorders
Headache
11.1%
1/9 • Number of events 1
7.7%
1/13 • Number of events 1
Skin and subcutaneous tissue disorders
Skin and Subcutaneous tissue disorders other
22.2%
2/9 • Number of events 2
7.7%
1/13 • Number of events 1
Immune system disorders
Allergic reaction
11.1%
1/9 • Number of events 1
0.00%
0/13
Gastrointestinal disorders
Constipation
0.00%
0/9
7.7%
1/13 • Number of events 1
General disorders
Fever
22.2%
2/9 • Number of events 3
0.00%
0/13
Vascular disorders
Hypertension
11.1%
1/9 • Number of events 1
0.00%
0/13
Psychiatric disorders
Insomnia
0.00%
0/9
7.7%
1/13 • Number of events 1
Nervous system disorders
Somnolence
0.00%
0/9
7.7%
1/13 • Number of events 1
Gastrointestinal disorders
Mucositis oral
11.1%
1/9 • Number of events 1
0.00%
0/13
Gastrointestinal disorders
Nausea
0.00%
0/9
7.7%
1/13 • Number of events 1
General disorders
Pain
11.1%
1/9 • Number of events 1
0.00%
0/13
Cardiac disorders
Tachycardia NOS
0.00%
0/9
7.7%
1/13 • Number of events 1

Additional Information

Angelina Fink, Research Base Administrator

SunCoast CCOP Research Base at the University of South Florida

Phone: 813-396-9245

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place