Trial Outcomes & Findings for Temsirolimus (Torisel®) and Erlotinib (Tarceva®) in Platinum-Refractory/Ineligible, Advanced, Squamous Cell Carcinoma (NCT NCT01009203)

NCT ID: NCT01009203

Last Updated: 2015-08-10

Results Overview

The time from treatment initiation to disease progression or death by any cause. Progression is evaluated according to modified Response Evaluation Criteria in Solid Tumors (RECIST) (version 1.0). Target lesions are assessed by computerized tomography (CT) or magnetic resonance imaging (MRI): Progressive Disease (PD), 20% increase in the sum of the longest diameter of target lesions, or unequivocal progression of existing non-target lesion, the appearance of new lesions, death due to disease without prior objective documentation of progression, or global deterioration in health status attributable to disease requiring a change in therapy without objective evidence of progression.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

13 participants

Primary outcome timeframe

3 years

Results posted on

2015-08-10

Participant Flow

Dates of recruitment period: December, 2009 - March, 2011

Participant milestones

Participant milestones
Measure
Erlotinib and Temsirolimus
Erlotinib at 150 mg by mouth daily + Temsirolimus at 15 mg intravenously weekly. Each cycle is comprised of 28 days.
Overall Study
STARTED
13
Overall Study
Received Treatment
12
Overall Study
COMPLETED
6
Overall Study
NOT COMPLETED
7

Reasons for withdrawal

Reasons for withdrawal
Measure
Erlotinib and Temsirolimus
Erlotinib at 150 mg by mouth daily + Temsirolimus at 15 mg intravenously weekly. Each cycle is comprised of 28 days.
Overall Study
Withdrawal by Subject
1
Overall Study
Adverse Event
5
Overall Study
Treatment-unrelated death
1

Baseline Characteristics

Temsirolimus (Torisel®) and Erlotinib (Tarceva®) in Platinum-Refractory/Ineligible, Advanced, Squamous Cell Carcinoma

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Erlotinib and Temsirolimus
n=13 Participants
Erlotinib at 150 mg by mouth daily + Temsirolimus at 15 mg intravenously weekly. Each cycle is comprised of 28 days.
Age, Continuous
61.5 years
n=99 Participants
Sex: Female, Male
Female
1 Participants
n=99 Participants
Sex: Female, Male
Male
12 Participants
n=99 Participants

PRIMARY outcome

Timeframe: 3 years

The time from treatment initiation to disease progression or death by any cause. Progression is evaluated according to modified Response Evaluation Criteria in Solid Tumors (RECIST) (version 1.0). Target lesions are assessed by computerized tomography (CT) or magnetic resonance imaging (MRI): Progressive Disease (PD), 20% increase in the sum of the longest diameter of target lesions, or unequivocal progression of existing non-target lesion, the appearance of new lesions, death due to disease without prior objective documentation of progression, or global deterioration in health status attributable to disease requiring a change in therapy without objective evidence of progression.

Outcome measures

Outcome measures
Measure
Erlotinib and Temsirolimus
n=12 Participants
Erlotinib at 150 mg by mouth daily + Temsirolimus at 15 mg intravenously weekly. Each cycle is comprised of 28 days.
Progression Free Survival (PFS)
1.9 Months
Interval 0.6 to 7.4

SECONDARY outcome

Timeframe: 3 years

Population: Participants who received t least one dose of on-study treatment

Toxicities (i.e. Adverse Events) are evaluated prior to each treatment and during any clinical visit. Toxicity will be evaluated per National Cancer Institute Common Terminology Criteria for Adverse Events (CTCAE), version 3.0. The number of patients affected by adverse events of grade 3 or higher will be reported.

Outcome measures

Outcome measures
Measure
Erlotinib and Temsirolimus
n=12 Participants
Erlotinib at 150 mg by mouth daily + Temsirolimus at 15 mg intravenously weekly. Each cycle is comprised of 28 days.
Toxicity Profile
Diarrhea
2 participants
Toxicity Profile
Facial/neck edema
1 participants
Toxicity Profile
Laryngeal edema
1 participants
Toxicity Profile
Asthenia
5 participants
Toxicity Profile
Peritonitis / infection
2 participants
Toxicity Profile
Anorexia
1 participants
Toxicity Profile
Elevated triglycerides
1 participants
Toxicity Profile
Aspiration pneumonia
1 participants
Toxicity Profile
Dyspnea
3 participants
Toxicity Profile
Hypoxia
1 participants

SECONDARY outcome

Timeframe: 3 years

Population: Participants evaluable for response

Tumor response is evaluated according to Response Evaluation Criteria in Solid Tumors (RECIST) (version 1.0). Target lesions are assessed by computerized tomography (CT) or magnetic resonance imaging (MRI:) Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions. Overall response rate (ORR) is the sum of the percentages of patients achieving complete and partial responses

Outcome measures

Outcome measures
Measure
Erlotinib and Temsirolimus
n=9 Participants
Erlotinib at 150 mg by mouth daily + Temsirolimus at 15 mg intravenously weekly. Each cycle is comprised of 28 days.
Overall Response Rate (ORR)
Complete response (CR)
0 percentage of evaluable participants
Overall Response Rate (ORR)
Partial response (PR)
11.1 percentage of evaluable participants
Overall Response Rate (ORR)
Overall response rate (CR + PR)
11.1 percentage of evaluable participants

SECONDARY outcome

Timeframe: 3 years

The time from treatment initiation to death by any cause

Outcome measures

Outcome measures
Measure
Erlotinib and Temsirolimus
n=12 Participants
Erlotinib at 150 mg by mouth daily + Temsirolimus at 15 mg intravenously weekly. Each cycle is comprised of 28 days.
Overall Survival (OS)
4 months
Interval 0.6 to 20.2

Adverse Events

Erlotinib and Temsirolimus

Serious events: 4 serious events
Other events: 12 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Erlotinib and Temsirolimus
n=12 participants at risk
Erlotinib at 150 mg by mouth daily + Temsirolimus at 15 mg intravenously weekly. Each cycle is comprised of 28 days.
Infections and infestations
Device related infection
8.3%
1/12 • Number of events 1 • 3 years
Nervous system disorders
Cerebrovascular Ischemia
8.3%
1/12 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Adult respiratory distress syndrome
8.3%
1/12 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Dyspnea (Shortness of breath)
8.3%
1/12 • Number of events 1 • 3 years
General disorders
Death
8.3%
1/12 • Number of events 1 • 3 years

Other adverse events

Other adverse events
Measure
Erlotinib and Temsirolimus
n=12 participants at risk
Erlotinib at 150 mg by mouth daily + Temsirolimus at 15 mg intravenously weekly. Each cycle is comprised of 28 days.
General disorders
Rhinitis (Runny nose)
8.3%
1/12 • Number of events 2 • 3 years
Blood and lymphatic system disorders
Leukocytes decreased
8.3%
1/12 • Number of events 1 • 3 years
Blood and lymphatic system disorders
Lymphopenia (Decreased lymphocytes)
8.3%
1/12 • Number of events 1 • 3 years
Blood and lymphatic system disorders
Neutrophils decreased
16.7%
2/12 • Number of events 2 • 3 years
Blood and lymphatic system disorders
Platelets decreased
25.0%
3/12 • Number of events 4 • 3 years
Cardiac disorders
Hypotension (Low blood pressure)
8.3%
1/12 • Number of events 1 • 3 years
General disorders
Fatigue
83.3%
10/12 • Number of events 20 • 3 years
General disorders
Fever
16.7%
2/12 • Number of events 3 • 3 years
General disorders
Weight loss
8.3%
1/12 • Number of events 1 • 3 years
Skin and subcutaneous tissue disorders
Acne
8.3%
1/12 • Number of events 1 • 3 years
Skin and subcutaneous tissue disorders
Dermatology/Skin - Other
8.3%
1/12 • Number of events 1 • 3 years
Skin and subcutaneous tissue disorders
Fibrosis
8.3%
1/12 • Number of events 1 • 3 years
Skin and subcutaneous tissue disorders
Induration (Hardening of the skin)
8.3%
1/12 • Number of events 1 • 3 years
Skin and subcutaneous tissue disorders
Pruritus (Itching)
8.3%
1/12 • Number of events 1 • 3 years
Skin and subcutaneous tissue disorders
Rash
58.3%
7/12 • Number of events 16 • 3 years
Skin and subcutaneous tissue disorders
Wound complication, non-infectious
8.3%
1/12 • Number of events 2 • 3 years
Endocrine disorders
Hypothyroidism (Low thyroid function)
8.3%
1/12 • Number of events 1 • 3 years
Gastrointestinal disorders
Anorexia (Loss of appetite)
16.7%
2/12 • Number of events 3 • 3 years
Gastrointestinal disorders
Constipation
25.0%
3/12 • Number of events 5 • 3 years
Gastrointestinal disorders
Dehydration
8.3%
1/12 • Number of events 1 • 3 years
Gastrointestinal disorders
Diarrhea
50.0%
6/12 • Number of events 10 • 3 years
Gastrointestinal disorders
Dry mouth
8.3%
1/12 • Number of events 1 • 3 years
Gastrointestinal disorders
Dyspepsia (Heartburn)
8.3%
1/12 • Number of events 1 • 3 years
Gastrointestinal disorders
Dysphagia (Difficulty swallowing)
8.3%
1/12 • Number of events 1 • 3 years
Gastrointestinal disorders
Mucositis oral (Inflammation of the mouth)
16.7%
2/12 • Number of events 3 • 3 years
Gastrointestinal disorders
Nausea
41.7%
5/12 • Number of events 8 • 3 years
Gastrointestinal disorders
Taste alteration
16.7%
2/12 • Number of events 2 • 3 years
Gastrointestinal disorders
Vomiting
16.7%
2/12 • Number of events 2 • 3 years
Infections and infestations
Gingival infection (Gum infection)
25.0%
3/12 • Number of events 3 • 3 years
General disorders
Edema limbs
16.7%
2/12 • Number of events 2 • 3 years
General disorders
Edema: head and neck
33.3%
4/12 • Number of events 10 • 3 years
Investigations
Alkaline phosphatase increased
8.3%
1/12 • Number of events 1 • 3 years
Investigations
Hemoglobin decreased
16.7%
2/12 • Number of events 2 • 3 years
Investigations
Hypercholesterolemia (High cholesterol levels)
16.7%
2/12 • Number of events 2 • 3 years
Investigations
Hyperglycemia (High blood sugar levels)
25.0%
3/12 • Number of events 3 • 3 years
Investigations
Hypertriglyceridemia (High triglyceride levels)
16.7%
2/12 • Number of events 2 • 3 years
Investigations
Hypoalbuminemia (Low albumin levels)
16.7%
2/12 • Number of events 2 • 3 years
Investigations
Hypocalcemia (Low calcium levels)
16.7%
2/12 • Number of events 2 • 3 years
Investigations
Hypokalemia (Low potassium levels)
33.3%
4/12 • Number of events 6 • 3 years
Investigations
Hypomagnesemia (Low magnesium levels)
25.0%
3/12 • Number of events 3 • 3 years
Investigations
Hyponatremia (Low sodium levels)
8.3%
1/12 • Number of events 1 • 3 years
Investigations
Hypophosphatemia (Low phosphate levels)
16.7%
2/12 • Number of events 3 • 3 years
Musculoskeletal and connective tissue disorders
Myalgia (Muscle pain)
8.3%
1/12 • Number of events 1 • 3 years
Musculoskeletal and connective tissue disorders
Pelvic soft tissue necrosis
8.3%
1/12 • Number of events 1 • 3 years
Psychiatric disorders
Depression
8.3%
1/12 • Number of events 1 • 3 years
Nervous system disorders
Headache
8.3%
1/12 • Number of events 1 • 3 years
Nervous system disorders
Syncope (Sudden loss of consciousness)
8.3%
1/12 • Number of events 2 • 3 years
General disorders
Ear, nose and throat examination abnormal
50.0%
6/12 • Number of events 11 • 3 years
General disorders
Patient odor
8.3%
1/12 • Number of events 1 • 3 years
General disorders
Joint pain
8.3%
1/12 • Number of events 1 • 3 years
General disorders
Neck pain
8.3%
1/12 • Number of events 1 • 3 years
General disorders
Oral pain
8.3%
1/12 • Number of events 1 • 3 years
General disorders
Pain in extremity
8.3%
1/12 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Bronchial obstruction
8.3%
1/12 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Cough
8.3%
1/12 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Dyspnea (Shortness of breath)
16.7%
2/12 • Number of events 5 • 3 years
Respiratory, thoracic and mediastinal disorders
Pleural effusion (Fluid collection in lung lining)
8.3%
1/12 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Pneumothorax (Lung collapse)
8.3%
1/12 • Number of events 1 • 3 years
Vascular disorders
Vascular access complication (Clotting)
8.3%
1/12 • Number of events 1 • 3 years

Additional Information

Julie E. Bauman, MD

University of Pittsburgh Medical Center

Phone: 4126486507

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place