Trial Outcomes & Findings for Efficacy and Safety of Intravenous Ferric Carboxymaltose (FCM) in Patients With Iron Deficiency Anemia (IDA) (NCT NCT00982007)

NCT ID: NCT00982007

Last Updated: 2018-02-20

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

997 participants

Primary outcome timeframe

Day 35

Results posted on

2018-02-20

Participant Flow

Hospitals and Medical Clinics

Participant milestones

Participant milestones
Measure
Cohort 1 (Group A) - Ferric Carboxymaltose (FCM)
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 1 (Group B) - Ferrous Sulfate
Oral iron Ferrous Sulfate Tablets : 325 mg Ferrous Sulfate tablets taken orally three times a day
Cohort 2 (Group C) - Ferric Carboxymaltose (FCM)
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 2 (Group D) - IV Iron (Standard of Care)
Other IV iron IV Iron (standard of care) : IV standard of care (other IV iron) per the Investigator's discretion
Overall Study
STARTED
250
257
253
251
Overall Study
COMPLETED
246
253
253
245
Overall Study
NOT COMPLETED
4
4
0
6

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Efficacy and Safety of Intravenous Ferric Carboxymaltose (FCM) in Patients With Iron Deficiency Anemia (IDA)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Cohort 1 (Group A) - Ferric Carboxymaltose (FCM)
n=246 Participants
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 1 (Group B) - Ferrous Sulfate
n=253 Participants
Oral iron Ferrous Sulfate Tablets : 325 mg Ferrous Sulfate tablets taken orally three times a day
Cohort 2 (Group C) - Ferric Carboxymaltose (FCM)
n=253 Participants
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 2 (Group D) - IV Iron (Standard of Care)
n=245 Participants
Other IV iron IV Iron (standard of care) : IV standard of care (other IV iron) per the Investigator's discretion
Total
n=997 Participants
Total of all reporting groups
Age, Categorical
<=18 years
2 Participants
n=99 Participants
7 Participants
n=107 Participants
2 Participants
n=206 Participants
3 Participants
n=7 Participants
14 Participants
n=31 Participants
Age, Categorical
Between 18 and 65 years
209 Participants
n=99 Participants
208 Participants
n=107 Participants
216 Participants
n=206 Participants
218 Participants
n=7 Participants
851 Participants
n=31 Participants
Age, Categorical
>=65 years
35 Participants
n=99 Participants
38 Participants
n=107 Participants
35 Participants
n=206 Participants
24 Participants
n=7 Participants
132 Participants
n=31 Participants
Age, Continuous
43.1 years
STANDARD_DEVIATION 17.18 • n=99 Participants
43.5 years
STANDARD_DEVIATION 17.71 • n=107 Participants
43.6 years
STANDARD_DEVIATION 16.88 • n=206 Participants
42.6 years
STANDARD_DEVIATION 15.51 • n=7 Participants
43.2 years
STANDARD_DEVIATION 16.63 • n=31 Participants
Sex: Female, Male
Female
233 Participants
n=99 Participants
238 Participants
n=107 Participants
239 Participants
n=206 Participants
231 Participants
n=7 Participants
941 Participants
n=31 Participants
Sex: Female, Male
Male
13 Participants
n=99 Participants
15 Participants
n=107 Participants
14 Participants
n=206 Participants
14 Participants
n=7 Participants
56 Participants
n=31 Participants
Region of Enrollment
United States
246 participants
n=99 Participants
253 participants
n=107 Participants
253 participants
n=206 Participants
245 participants
n=7 Participants
997 participants
n=31 Participants

PRIMARY outcome

Timeframe: Day 35

Population: Modified Intent-to-Treat Population: Subjects who have received at least 1 dose of randomized study medication and had at least 1 post-baseline hemoglobin assessment

Outcome measures

Outcome measures
Measure
Cohort 1 (Group A) - Ferric Carboxymaltose (FCM)
n=244 Participants
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 1 (Group B) - Ferrous Sulfate
n=251 Participants
Oral iron Ferrous Sulfate Tablets : 325 mg Ferrous Sulfate tablets taken orally three times a day
Cohort 2 (Group C) - Ferric Carboxymaltose (FCM)
n=245 Participants
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 2 (Group D) - IV Iron (Standard of Care)
n=237 Participants
Other IV iron IV Iron (standard of care) : IV standard of care (other IV iron) per the Investigator's discretion
Mean Increase From Baseline to the Highest Observed Hemoglobin Value Between Baseline and Day 35 or Time of Intervention for Patients Taking FCM as Compared to That for Patients Taking Ferrous Sulfate.
1.57 g/dL
Standard Deviation 1.194
0.80 g/dL
Standard Deviation 0.799
2.90 g/dL
Standard Deviation 1.640
2.16 g/dL
Standard Deviation 1.252

Adverse Events

Cohort 1 (Group A) - Ferric Carboxymaltose (FCM)

Serious events: 8 serious events
Other events: 31 other events
Deaths: 0 deaths

Cohort 1 (Group B) - Ferrous Sulfate

Serious events: 10 serious events
Other events: 5 other events
Deaths: 0 deaths

Cohort 2 (Group C) - Ferric Carboxymaltose (FCM)

Serious events: 17 serious events
Other events: 26 other events
Deaths: 0 deaths

Cohort 2 (Group D) - IV Iron (Standard of Care)

Serious events: 16 serious events
Other events: 10 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Cohort 1 (Group A) - Ferric Carboxymaltose (FCM)
n=246 participants at risk
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 1 (Group B) - Ferrous Sulfate
n=253 participants at risk
Oral iron Ferrous Sulfate Tablets : 325 mg Ferrous Sulfate tablets taken orally three times a day
Cohort 2 (Group C) - Ferric Carboxymaltose (FCM)
n=253 participants at risk
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 2 (Group D) - IV Iron (Standard of Care)
n=245 participants at risk
Other IV iron IV Iron (standard of care) : IV standard of care (other IV iron) per the Investigator's discretion
Blood and lymphatic system disorders
Anemia
0.41%
1/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.79%
2/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Cardiac disorders
Acute myocardial infarction
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Cardiac disorders
Angina pectoris
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Cardiac disorders
Atrial fibrillation
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Congenital, familial and genetic disorders
Cystic fibrosis
0.41%
1/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Gastrointestinal disorders
Colitis
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Gastrointestinal disorders
Gastrointestinal hemorrhage
0.41%
1/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Gastrointestinal disorders
Small intestinal obstruction
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Gastrointestinal disorders
Volvulus
0.41%
1/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
General disorders
Chest pain
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
General disorders
Death
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
General disorders
Fatigue
0.41%
1/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Hepatobiliary disorders
Bile duct stone
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Hepatobiliary disorders
Cholecystitis
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Hepatobiliary disorders
Cholelithiasis
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Immune system disorders
Hypersensitivity
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
1.2%
3/245 • 1 year and 6 months
Infections and infestations
Bacteremia
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Infections and infestations
Herpes zoster
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Infections and infestations
Mastitis
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Infections and infestations
Pneumonia
0.41%
1/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Infections and infestations
Septic shock
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Injury, poisoning and procedural complications
Accidental overdose
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Injury, poisoning and procedural complications
Drug toxicity
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Metabolism and nutrition disorders
Hyperkalemia
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Musculoskeletal and connective tissue disorders
Muscle spasms
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Colon cancer
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Lung neoplasm malignant
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Uterine cancer
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Uterine leiomyoma
0.41%
1/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Nervous system disorders
Carpal tunnel syndrome
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Nervous system disorders
Cerebrovascular accident
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Nervous system disorders
Paresthesia
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Nervous system disorders
Transient ischemic attack
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Pregnancy, puerperium and perinatal conditions
Abortion spontaneous
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Psychiatric disorders
Depression
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Psychiatric disorders
Suicidal ideation
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Psychiatric disorders
Suicide attempt
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Renal and urinary disorders
Renal failure acute
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Reproductive system and breast disorders
Menorrhagia
0.41%
1/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.79%
2/253 • 1 year and 6 months
0.82%
2/245 • 1 year and 6 months
Reproductive system and breast disorders
Pelvic pain
0.41%
1/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months
Reproductive system and breast disorders
Uterine disorder
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Reproductive system and breast disorders
Uterine hemorrhage
0.00%
0/246 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Reproductive system and breast disorders
Vaginal hemorrhage
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Respiratory, thoracic and mediastinal disorders
Acute respiratory failure
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.41%
1/245 • 1 year and 6 months
Respiratory, thoracic and mediastinal disorders
Pulmonary hypertension
0.00%
0/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
0.40%
1/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months

Other adverse events

Other adverse events
Measure
Cohort 1 (Group A) - Ferric Carboxymaltose (FCM)
n=246 participants at risk
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 1 (Group B) - Ferrous Sulfate
n=253 participants at risk
Oral iron Ferrous Sulfate Tablets : 325 mg Ferrous Sulfate tablets taken orally three times a day
Cohort 2 (Group C) - Ferric Carboxymaltose (FCM)
n=253 participants at risk
Intravenous (IV) iron Ferric Carboxymaltose (FCM) : A total maximum cumulative dose of 1500 mg administered on Days 0 and 7.
Cohort 2 (Group D) - IV Iron (Standard of Care)
n=245 participants at risk
Other IV iron IV Iron (standard of care) : IV standard of care (other IV iron) per the Investigator's discretion
Gastrointestinal disorders
Nausea
8.1%
20/246 • 1 year and 6 months
2.0%
5/253 • 1 year and 6 months
4.0%
10/253 • 1 year and 6 months
4.1%
10/245 • 1 year and 6 months
Metabolism and nutrition disorders
Hypophosphatemia
4.5%
11/246 • 1 year and 6 months
0.00%
0/253 • 1 year and 6 months
6.3%
16/253 • 1 year and 6 months
0.00%
0/245 • 1 year and 6 months

Additional Information

Mark A. Falone

Luitpold Pharmaceuticals, Inc.

Phone: 610-650-4200

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60