Trial Outcomes & Findings for Efficacy and Tolerability of an Intra-Nasal Testosterone Product (NCT NCT00975650)

NCT ID: NCT00975650

Last Updated: 2018-08-13

Results Overview

The primary objective of this study was to determine the efficacy of Nasobol in the treatment of hypogonadal men requiring testosterone replacement therapy. Efficacy was determined by establishing a pharmacokinetic profile for serum testosterone levels following Nasobol treatment or that of the active control, Androderm®.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

57 participants

Primary outcome timeframe

0.0 (trough), 0.50, 1.0, 1.5, 2.0, 3.0, 6.0, 9.0, 10.0, 10.5, 11.0, 11.5, 12.0, 13.0, 16.0, 19.0, 22.0, and 24.0 hours.

Results posted on

2018-08-13

Participant Flow

Participant milestones

Participant milestones
Measure
Sequence 1
Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days; Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days; Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days; Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days;
Sequence 2
Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days; Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days; Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days; Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Sequence 3
Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days; Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days; Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days; Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days
Sequence 4
Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days; Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days; Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days; Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Period 1
STARTED
13
16
14
14
Period 1
COMPLETED
13
16
14
14
Period 1
NOT COMPLETED
0
0
0
0
Period 2
STARTED
13
16
14
14
Period 2
COMPLETED
12
14
14
14
Period 2
NOT COMPLETED
1
2
0
0
Period 3
STARTED
12
14
14
14
Period 3
COMPLETED
12
14
14
14
Period 3
NOT COMPLETED
0
0
0
0
Period 4
STARTED
12
14
14
14
Period 4
COMPLETED
12
14
14
14
Period 4
NOT COMPLETED
0
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Efficacy and Tolerability of an Intra-Nasal Testosterone Product

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
All Subjects
n=57 Participants
All Subjects who were dosed.
Age, Continuous
52.0 years
STANDARD_DEVIATION 12.0 • n=99 Participants
Sex: Female, Male
Female
0 Participants
n=99 Participants
Sex: Female, Male
Male
57 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
19 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
38 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=99 Participants
Race (NIH/OMB)
Asian
0 Participants
n=99 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=99 Participants
Race (NIH/OMB)
Black or African American
4 Participants
n=99 Participants
Race (NIH/OMB)
White
53 Participants
n=99 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=99 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
Region of Enrollment
United States
57 Participants
n=99 Participants

PRIMARY outcome

Timeframe: 0.0 (trough), 0.50, 1.0, 1.5, 2.0, 3.0, 6.0, 9.0, 10.0, 10.5, 11.0, 11.5, 12.0, 13.0, 16.0, 19.0, 22.0, and 24.0 hours.

Population: Number of participants includes participants who completed the corresponding treatment and had sufficient plasma concentration data to calculate the PK parameter.

The primary objective of this study was to determine the efficacy of Nasobol in the treatment of hypogonadal men requiring testosterone replacement therapy. Efficacy was determined by establishing a pharmacokinetic profile for serum testosterone levels following Nasobol treatment or that of the active control, Androderm®.

Outcome measures

Outcome measures
Measure
Treatment A
n=52 Participants
Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment B
n=55 Participants
Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment C
n=52 Participants
Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment D
n=54 Participants
Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days
Serum Testosterone Ln-Cmax
6.25 ng/dL
Standard Deviation 0.37
6.41 ng/dL
Standard Deviation 0.35
6.54 ng/dL
Standard Deviation 0.36
6.36 ng/dL
Standard Deviation 0.37

PRIMARY outcome

Timeframe: 0.0 (trough), 0.50, 1.0, 1.5, 2.0, 3.0, 6.0, 9.0, 10.0, 10.5, 11.0, 11.5, 12.0, 13.0, 16.0, 19.0, 22.0, and 24.0 hours.

Population: Number of participants includes participants who completed the corresponding treatment and had sufficient plasma concentration data to calculate the PK parameter.

Outcome measures

Outcome measures
Measure
Treatment A
n=52 Participants
Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment B
n=55 Participants
Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment C
n=52 Participants
Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment D
n=54 Participants
Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days
Serum Testosterone Ln-AUCt
8.80 ng.h/dL
Standard Deviation 0.26
8.90 ng.h/dL
Standard Deviation 0.27
8.95 ng.h/dL
Standard Deviation 0.29
9.09 ng.h/dL
Standard Deviation 0.29

PRIMARY outcome

Timeframe: 0.0 (trough), 0.50, 1.0, 1.5, 2.0, 3.0, 6.0, 9.0, 10.0, 10.5, 11.0, 11.5, 12.0, 13.0, 16.0, 19.0, 22.0, and 24.0 hours.

Population: Number of participants includes participants who completed the corresponding treatment and had sufficient plasma concentration data to calculate the PK parameter.

Outcome measures

Outcome measures
Measure
Treatment A
n=52 Participants
Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment B
n=55 Participants
Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment C
n=52 Participants
Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment D
n=54 Participants
Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days
Serum Testosterone Cavg
287.10 ng/dL
Standard Deviation 76.42
316.64 ng/dL
Standard Deviation 88.93
336.11 ng/dL
Standard Deviation 100.76
384.62 ng/dL
Standard Deviation 102.97

PRIMARY outcome

Timeframe: 0.0 (trough), 0.50, 1.0, 1.5, 2.0, 3.0, 6.0, 9.0, 10.0, 10.5, 11.0, 11.5, 12.0, 13.0, 16.0, 19.0, 22.0, and 24.0 hours.

Population: Number of participants includes participants who completed the corresponding treatment and had sufficient plasma concentration data to calculate the PK parameter.

Outcome measures

Outcome measures
Measure
Treatment A
n=52 Participants
Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment B
n=55 Participants
Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment C
n=52 Participants
Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment D
n=54 Participants
Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days
Serum Dihydrotestosterone Ln-Cmax
3.54 ng/dL
Standard Deviation 0.38
3.67 ng/dL
Standard Deviation 0.44
3.80 ng/dL
Standard Deviation 0.41
3.44 ng/dL
Standard Deviation 0.35

PRIMARY outcome

Timeframe: 0.0 (trough), 0.50, 1.0, 1.5, 2.0, 3.0, 6.0, 9.0, 10.0, 10.5, 11.0, 11.5, 12.0, 13.0, 16.0, 19.0, 22.0, and 24.0 hours.

Population: Number of participants includes participants who completed the corresponding treatment and had sufficient plasma concentration data to calculate the PK parameter.

Outcome measures

Outcome measures
Measure
Treatment A
n=52 Participants
Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment B
n=55 Participants
Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment C
n=52 Participants
Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment D
n=54 Participants
Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days
Serum Dihydrotestosterone Ln-AUCt
6.34 ng.h/dL
Standard Deviation 0.38
6.47 ng.h/dL
Standard Deviation 0.41
6.52 ng.h/dL
Standard Deviation 0.45
6.33 ng.h/dL
Standard Deviation 0.34

PRIMARY outcome

Timeframe: 0.0 (trough), 0.50, 1.0, 1.5, 2.0, 3.0, 6.0, 9.0, 10.0, 10.5, 11.0, 11.5, 12.0, 13.0, 16.0, 19.0, 22.0, and 24.0 hours.

Population: Number of participants includes participants who completed the corresponding treatment and had sufficient plasma concentration data to calculate the PK parameter.

Outcome measures

Outcome measures
Measure
Treatment A
n=52 Participants
Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment B
n=55 Participants
Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment C
n=52 Participants
Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment D
n=54 Participants
Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days
Serum Dihydrotestosterone Cavg
25.24 ng/dL
Standard Deviation 8.51
28.97 ng/dL
Standard Deviation 11.41
30.79 ng/dL
Standard Deviation 12.50
24.69 ng/dL
Standard Deviation 8.46

PRIMARY outcome

Timeframe: Each period is 7 days

Population: Number of participants includes participants who completed the corresponding treatment and had sufficient plasma concentration data to calculate the PK parameter.

The percentage of subjects with a Cavg within the reference range of 300 to 1050 ng/dL and 25.5 to 97.8 ng/dL for testosterone and dihydotestosterone.

Outcome measures

Outcome measures
Measure
Treatment A
n=52 Participants
Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment B
n=55 Participants
Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment C
n=52 Participants
Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment D
n=54 Participants
Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days
Percentage of Subjects With Cavg Within the Reference Range
Dihydrotestosterone
24 Participants
31 Participants
34 Participants
22 Participants
Percentage of Subjects With Cavg Within the Reference Range
Testosterone
19 Participants
27 Participants
27 Participants
42 Participants

Adverse Events

Treatment A

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Treatment B

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

Treatment C

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Treatment D

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Treatment A
n=57 participants at risk
Treatment A: 8.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment B
n=56 participants at risk
Treatment B: 11.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment C
n=54 participants at risk
Treatment C: 14.0 mg Nasobol® (2 syringes), b.i.d. for 7 days
Treatment D
n=55 participants at risk
Treatment D: 5.0 mg Androderm® (Positive Control)-Patch, q.d. for 7 days
Respiratory, thoracic and mediastinal disorders
Nasal dryness
1.8%
1/57
5.4%
3/56
0.00%
0/54
0.00%
0/55
Gastrointestinal disorders
Nausea
3.5%
2/57
0.00%
0/56
0.00%
0/54
1.8%
1/55
General disorders
Application Site Rash
0.00%
0/57
0.00%
0/56
0.00%
0/54
3.6%
2/55
Nervous system disorders
Headache
1.8%
1/57
3.6%
2/56
0.00%
0/54
1.8%
1/55
Psychiatric disorders
Anxiety
1.8%
1/57
1.8%
1/56
0.00%
0/54
3.6%
2/55

Additional Information

Dr. Nathan Bryson, Vice President, Scientific Affairs

Acerus Pharmaceuticals Corporation

Phone: 1-416-679-0776

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place