Trial Outcomes & Findings for Efficacy and Safety of Desmopressin (Nocturin®) 0.1 mg Tablets in Treatment of Nocturia in Participants With Benign Prostate Syndrome (BPS) (NCT NCT00902265)

NCT ID: NCT00902265

Last Updated: 2011-04-19

Results Overview

The number of nighttime voids was calculated over 48-hours period prior to baseline and week 12 visits. Calculated as Week 12 measure - Baseline measure.

Recruitment status

COMPLETED

Target enrollment

138 participants

Primary outcome timeframe

Baseline, Week 12

Results posted on

2011-04-19

Participant Flow

This was a post marketing, non-randomized surveillance study. The 138 participants were screened from 60 German sites. The study planned for two visits - baseline (week 0 and week 12). Participants could opt for an optional visit between week 0 and week 12 (17 participants did not opt for optional visit).

Participant milestones

Participant milestones
Measure
Desmopressin 0.1 mg
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Overall Study
STARTED
138
Overall Study
Participants Who Received Treatment
137
Overall Study
COMPLETED
132
Overall Study
NOT COMPLETED
6

Reasons for withdrawal

Reasons for withdrawal
Measure
Desmopressin 0.1 mg
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Overall Study
Lost to Follow-up Prior to First Visit
1
Overall Study
Adverse Event
2
Overall Study
Lack of Efficacy
2
Overall Study
Protocol Violation
1

Baseline Characteristics

Efficacy and Safety of Desmopressin (Nocturin®) 0.1 mg Tablets in Treatment of Nocturia in Participants With Benign Prostate Syndrome (BPS)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Desmopressin 0.1 mg
n=137 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Age Continuous
62.6 years
STANDARD_DEVIATION 7.8 • n=39 Participants
Sex: Female, Male
Female
0 Participants
n=39 Participants
Sex: Female, Male
Male
137 Participants
n=39 Participants
Region of Enrollment
Germany
137 participants
n=39 Participants

PRIMARY outcome

Timeframe: Baseline, Week 12

Population: Intent to treat (ITT) population --All participants who received at least one dose of study drug and provided at least one primary efficacy measure (i.e., number of nocturnal voids)

The number of nighttime voids was calculated over 48-hours period prior to baseline and week 12 visits. Calculated as Week 12 measure - Baseline measure.

Outcome measures

Outcome measures
Measure
Desmopressin 0.1 mg
n=132 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Overall Mean Change From Baseline in Mean Number of Nighttime Voids at Week 12
-2.01 Number of nocturnal voids
Standard Deviation 1.13

SECONDARY outcome

Timeframe: Baseline, Week 12

Population: Intent to treat (ITT) population --All participants who received at least one dose of study drug and provided at least one primary efficacy measure (i.e., number of nocturnal voids)

The ratio of nighttime urine volume to 24-hour urine volume is calculated as the urine volume (volume of all voids after going to bed plus the first morning void) / 24-hour urine volume. Ratios are calculated at baseline and week 12 and difference between the two time points is reported here.

Outcome measures

Outcome measures
Measure
Desmopressin 0.1 mg
n=114 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Mean Change From Baseline in Ratio of Nighttime Urine Volume to 24-hour Urine Volume at Week 12
-14.0 ratio
Standard Deviation 11.9

SECONDARY outcome

Timeframe: Baseline, Week 12

Population: Intent to treat (ITT) population --All participants who received at least one dose of study drug and provided at least one primary efficacy measure (i.e., number of nocturnal voids)

Initial period of undisturbed sleep is calculated as the number of hours between falling asleep and waking for the first time during the night to void. Change is calculated at Week 12 - baseline.

Outcome measures

Outcome measures
Measure
Desmopressin 0.1 mg
n=124 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Mean Change From Baseline in Initial Period of Undisturbed Sleep at Week 12
1.69 Hours
Standard Deviation 1.16

SECONDARY outcome

Timeframe: Baseline, Week 12

Population: Intent to treat (ITT) population --All participants who received at least one dose of study drug and provided at least one primary efficacy measure (i.e., number of nocturnal voids)

The International Prostate Symptoms Score (IPSS) is a self-administered 8 item questionnaire designed to assess urination frequency and Quality of Life (QOL). The first 7 items are summed into a total score and question urination frequency. They are scaled 0-5, with higher numbers indicating greater severity of symptoms. The last question (item 8) concerns QOL and is scaled 0-6 where higher numbers indicate lower quality of life due to symptoms. The total scale across all questions is 0-41, with higher scores representing worse symptoms.

Outcome measures

Outcome measures
Measure
Desmopressin 0.1 mg
n=131 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Mean Change From Baseline of Total International Prostate Symptom Score (IPSS) at Week 12
-4.86 Units on a scale
Standard Deviation 4.22

SECONDARY outcome

Timeframe: Baseline, Week 12

Population: Intent to treat (ITT) population --All participants who received at least one dose of study drug and provided at least one primary efficacy measure (i.e., number of nocturnal voids).

The International Prostate Symptoms Score (IPSS) is a self-administered 8 item questionnaire designed to assess urination frequency and Quality of Life (QOL). The last question (item 8) concerns Quality of Life (QOL) and is scaled 0-6 where higher numbers indicate lower quality of life due to symptoms. Higher scores represent worse Quality of Life (QoL).

Outcome measures

Outcome measures
Measure
Desmopressin 0.1 mg
n=117 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Mean Change From Baseline International Prostate Symptom Score (IPSS) Quality of Life Score at Week 12
-1.56 Units on a scale
Standard Deviation 1.05

SECONDARY outcome

Timeframe: Baseline, Week 12

Population: Intent to treat (ITT) population --All participants who received at least one dose of study drug and provided at least one primary efficacy measure (i.e., number of nocturnal voids).

The LSEQ is a self-administered 10-item visual analog scale questionnaire designed to assess sleep quality. The 10 individual items are scored 1 to 100, with the total score ranging from 0 - 1,000. Higher numbers indicate lower sleep quality.

Outcome measures

Outcome measures
Measure
Desmopressin 0.1 mg
n=129 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Mean Change From Baseline in Total Score in Leeds Sleep Evaluation Questionnaire (LSEQ) at Week 12
-15.1 Units on a scale
Standard Deviation 12.1

SECONDARY outcome

Timeframe: Baseline, Week 12

Population: Intent to treat (ITT) population --All participants who received at least one dose of study drug and provided at least one primary efficacy measure (i.e., number of nocturnal voids).

The ICIQ-N is a self-administered 4-item questionnaire designed to assess the frequency and bother of daytime and nighttime urination. In questions 1 and 2 participants were asked to estimate the frequency of both daytime voiding (all voids before going to bed excluding the first morning void) and rate the degree of bother of daytime urination on a scale ranging from 0 (not at all) to 10 (a great deal). Higher numbers indicate lower Quality of Life (QoL).

Outcome measures

Outcome measures
Measure
Desmopressin 0.1 mg
n=127 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Change From Baseline in Degree of Bother Due to Frequency of Daytime Voiding Assessed by The International Consultation on Incontinence Modular Questionnaire - Nocturia (ICIQ-N)
-2.25 Units on a scale
Standard Deviation 2.25

SECONDARY outcome

Timeframe: Baseline, Week 12

Population: Intent to treat (ITT) population --All participants who received at least one dose of study drug and provided at least one primary efficacy measure (i.e., number of nocturnal voids).

The ICIQ-N is a self-administered 4-item questionnaire designed to assess the frequency and bother of daytime and nighttime urination. In questions 3 and 4, participants were asked to estimate the frequency of nighttime voiding (number of voids after going to bed plus the first morning void) and rate the degree of bother of nighttime urination on a scale ranging from 0 (not at all) to 10 (a great deal). Higher numbers indicate lower Quality of Life (QOL).

Outcome measures

Outcome measures
Measure
Desmopressin 0.1 mg
n=129 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Change From Baseline in Degree of Bother Due to Frequency of Nighttime Voiding Assessed by The International Consultation on Incontinence Modular Questionnaire - Nocturia (ICIQ-N)at Week 12
-4.00 Units on a scale
Standard Deviation 2.49

SECONDARY outcome

Timeframe: Week 1 to Week 12

Population: Safety Population, consisting of participants who took at least one dose of desmopressin

Outcome measures

Outcome measures
Measure
Desmopressin 0.1 mg
n=137 Participants
Participants with benign prostate syndrome suffering from nocturia associated with nocturnal polyuria. Drug given by prescription.
Participants With Treatment Emergent Adverse Events (AEs)
All Adverse Events
3 Participants
Participants With Treatment Emergent Adverse Events (AEs)
Deaths
0 Participants
Participants With Treatment Emergent Adverse Events (AEs)
Serious Adverse Events
0 Participants
Participants With Treatment Emergent Adverse Events (AEs)
AEs Leading to Discontinuation
2 Participants

Adverse Events

Desmopressin 0.1 mg

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Clinical Development Support

Ferring Pharmaceuticals

Results disclosure agreements

  • Principal investigator is a sponsor employee PI gives Ferring a draft manuscript 30 days before submission for the final form for to any journal for review and comments. Ferring can ask that confidential information be removed.
  • Publication restrictions are in place

Restriction type: OTHER