Trial Outcomes & Findings for Trial of High Dose Lenalidomide in Patients With MDS and AML With Trilineage Dysplasia (NCT NCT00867308)

NCT ID: NCT00867308

Last Updated: 2018-10-17

Results Overview

Number of participants with a complete or partial response according to International Working Group 2006 criteria.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

32 participants

Primary outcome timeframe

15 weeks

Results posted on

2018-10-17

Participant Flow

2 participants on the 15mg arm and 3 participants on the 50mg arm were screen failures.

Participant milestones

Participant milestones
Measure
Lenalidomide 15 mg
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 15 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Lenalidomide 50 mg
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 50 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Overall Study
STARTED
9
18
Overall Study
COMPLETED
0
0
Overall Study
NOT COMPLETED
9
18

Reasons for withdrawal

Reasons for withdrawal
Measure
Lenalidomide 15 mg
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 15 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Lenalidomide 50 mg
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 50 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Overall Study
Death
1
0
Overall Study
Adverse Event
1
4
Overall Study
Lack of Efficacy
6
12
Overall Study
Withdrawal by Subject
1
2

Baseline Characteristics

Race and Ethnicity were not collected from any participant.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Lenalidomide 15 mg
n=9 Participants
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 15 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Lenalidomide 50 mg
n=18 Participants
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 50 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Total
n=27 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=9 Participants
0 Participants
n=18 Participants
0 Participants
n=27 Participants
Age, Categorical
Between 18 and 65 years
3 Participants
n=9 Participants
4 Participants
n=18 Participants
7 Participants
n=27 Participants
Age, Categorical
>=65 years
6 Participants
n=9 Participants
14 Participants
n=18 Participants
20 Participants
n=27 Participants
Age, Continuous
77 years
n=9 Participants
70 years
n=18 Participants
72 years
n=27 Participants
Sex: Female, Male
Female
1 Participants
n=9 Participants
4 Participants
n=18 Participants
5 Participants
n=27 Participants
Sex: Female, Male
Male
8 Participants
n=9 Participants
14 Participants
n=18 Participants
22 Participants
n=27 Participants
Race and Ethnicity Not Collected
0 Participants
Race and Ethnicity were not collected from any participant.

PRIMARY outcome

Timeframe: 15 weeks

Number of participants with a complete or partial response according to International Working Group 2006 criteria.

Outcome measures

Outcome measures
Measure
Lenalidomide 15 mg
n=9 Participants
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 15 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Lenalidomide 50 mg
n=18 Participants
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 50 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Response Rate
Complete response
0 Participants
0 Participants
Response Rate
Partial response
0 Participants
2 Participants

SECONDARY outcome

Timeframe: Up to 8 months

Number of participants who experienced at least one grade 3-4 non-hematological toxicity by CTCAE 3.0 that was attributed to lenalidomide.

Outcome measures

Outcome measures
Measure
Lenalidomide 15 mg
n=9 Participants
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 15 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Lenalidomide 50 mg
n=18 Participants
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 50 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Grade 3-4 Toxicity
6 Participants
12 Participants

Adverse Events

Lenalidomide 15 mg

Serious events: 3 serious events
Other events: 7 other events
Deaths: 3 deaths

Lenalidomide 50 mg

Serious events: 9 serious events
Other events: 13 other events
Deaths: 2 deaths

Serious adverse events

Serious adverse events
Measure
Lenalidomide 15 mg
n=9 participants at risk
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 15 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Lenalidomide 50 mg
n=18 participants at risk
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 50 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Renal and urinary disorders
Acute kidney injury
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Nervous system disorders
Weakness - leg
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
0.00%
0/18 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Clostridium difficile infection
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Endocarditis
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
0.00%
0/18 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Epistaxis
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
0.00%
0/18 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Febrile neutropenia
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Fungal pneumonia
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Cardiac disorders
Hypotension
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Respiratory, thoracic and mediastinal disorders
Hypoxia
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Meningitis
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
0.00%
0/18 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Pericarditis
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Pneumonia
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
16.7%
3/18 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.

Other adverse events

Other adverse events
Measure
Lenalidomide 15 mg
n=9 participants at risk
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 15 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Lenalidomide 50 mg
n=18 participants at risk
Patients diagnosed with high risk Myelodysplastic syndrome (MDS), regardless of 5q deletion status, will receive lenalidomide 50 mg per day orally, on days 1-28 of a 42 day cycle for 2 cycles. At this point, patients meeting protocol specified response criteria will proceed to Continuing Therapy on a reduced dose of lenalidomide until progression. Patients not achieving response will receive 2 additional cycles of treatment, whereupon response will again be assessed. Patients achieving response at this point will proceed to Continuing Therapy as described. Patients without evidence of response after 4 cycles will be taken off-study.
Investigations
Anemia
22.2%
2/9 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
0.00%
0/18 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Anorexia
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
22.2%
4/18 • Number of events 4 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Musculoskeletal and connective tissue disorders
Arthralgia
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Cardiac disorders
Atrial fibrillation
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Blood and lymphatic system disorders
Bleeding
33.3%
3/9 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
16.7%
3/18 • Number of events 5 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Blood and lymphatic system disorders
Bruising
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
16.7%
3/18 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Nervous system disorders
Confusion
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Gastrointestinal disorders
Constipation
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
33.3%
6/18 • Number of events 8 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Cough
33.3%
3/9 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
22.2%
4/18 • Number of events 4 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Gastrointestinal disorders
Diarrhea
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
22.2%
4/18 • Number of events 7 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Respiratory, thoracic and mediastinal disorders
Dyspnea
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
16.7%
3/18 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Cardiac disorders
Edema
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
38.9%
7/18 • Number of events 10 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Blood and lymphatic system disorders
Epistaxis
44.4%
4/9 • Number of events 5 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
16.7%
3/18 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Fatigue
55.6%
5/9 • Number of events 5 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
44.4%
8/18 • Number of events 12 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Febrile neutropenia
33.3%
3/9 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Fever
11.1%
1/9 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Nervous system disorders
Hallucination
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Headache
11.1%
1/9 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Renal and urinary disorders
Hematuria
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Hoarseness
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Investigations
Hyperbilirubinemia
22.2%
2/9 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Investigations
Hypokalemia
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Investigations
Hyponatremia
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
0.00%
0/18 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Investigations
Leukopenia
22.2%
2/9 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
0.00%
0/18 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Cardiac disorders
Lightheadedness
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Myalgia
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
33.3%
6/18 • Number of events 11 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Gastrointestinal disorders
Nausea
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Nervous system disorders
Neuropathy
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Pain - back
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Pain - chest
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
General disorders
Pain - tooth
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Skin and subcutaneous tissue disorders
Pruritis
11.1%
1/9 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
44.4%
8/18 • Number of events 13 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Skin and subcutaneous tissue disorders
Rash
33.3%
3/9 • Number of events 5 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
33.3%
6/18 • Number of events 9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Gastrointestinal disorders
Stomatitis
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
16.7%
3/18 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Investigations
Thrombocytopenia
33.3%
3/9 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
0.00%
0/18 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Infections and infestations
Thrush
11.1%
1/9 • Number of events 1 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
5.6%
1/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Gastrointestinal disorders
Vomiting
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
16.7%
3/18 • Number of events 3 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Nervous system disorders
Weakness
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
33.3%
6/18 • Number of events 6 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Skin and subcutaneous tissue disorders
Xerosis
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
Gastrointestinal disorders
Xerostomia
0.00%
0/9 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.
11.1%
2/18 • Number of events 2 • Up to 8 months
Due to significant cytopenias in all participants at presentation and throughout the trial, hematologic toxicity was only reported where bone marrow aplasia lasted for \>3 weeks from last dose of lenalidomide with a bone marrow cellularity of \<5% without evidence of leukemia. Adverse events were collected weekly throughout the trial.

Additional Information

Amy DeZern, MD

Johns Hopkins University

Phone: 4105027208

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place