Phase II Study of KPS-0373 in Patients With Spinocerebellar Degeneration (SCD)

Study to Evaluate Multiple Ascending Dose and Multi-Dose of DT-216 in Adult Patients With Friedreich Ataxia

NCT05573698 ·Status: COMPLETED ·Phase: PHASE1

Study of Safety and Dosing Effect on SMN Levels of Valproic Acid (VPA) in Patients With Spinal Muscular Atrophy

NCT00374075 ·Status: COMPLETED ·Phase: PHASE1

Safety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3

NCT02227823 ·Status: COMPLETED ·Phase: PHASE2

A Multiple Ascending Dose Study of DT-216P2 in Patients With Friedreich's Ataxia

NCT06874010 ·Status: RECRUITING ·Phase: PHASE1/PHASE2

A Pharmacokinetics and Safety Study of BIIB132 in Adults With Spinocerebellar Ataxia 3

NCT05160558 ·Status: TERMINATED ·Phase: PHASE1

Trial in Adult Participants With Spinocerebellar Ataxia (SCA)

NCT02960893 ·Status: COMPLETED ·Phase: PHASE2/PHASE3

Efficacy of EGb761 in Patients Suffering From Friedreich Ataxia

NCT00824512 ·Status: COMPLETED ·Phase: PHASE2

A Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy

NCT03779334 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE2

Troriluzole in Adult Participants With Spinocerebellar Ataxia

NCT03701399 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE3

A Phase 2 RCT Study of CX-8998 for Essential Tremor

NCT03101241 ·Status: COMPLETED ·Phase: PHASE2

Safety and Tolerability of Lithium in Spinocerebellar Ataxia 2 (SCA2)

NCT00998634 ·Status: COMPLETED ·Phase: PHASE2

Safety Study of SPARC1104

NCT01797185 ·Status: COMPLETED ·Phase: PHASE3

A Clinical Study to Evaluate the Effect of MIN-102 on the Progression of Friedreich's Ataxia in Male and Female Patients

NCT03917225 ·Status: COMPLETED ·Phase: PHASE2

A Single Ascending Dose Study of DT-216P2 in Normal Healthy Participants

NCT06772870 ·Status: NOT_YET_RECRUITING ·Phase: PHASE1

A Study to Assess the Efficacy, Safety and Pharmacokinetics of Nusinersen (ISIS 396443) in Infants With Spinal Muscular Atrophy (SMA)

NCT01839656 ·Status: COMPLETED ·Phase: PHASE2

A Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular Atrophy

NCT05808764 ·Status: RECRUITING ·Phase: PHASE2

Study to Assess the Efficacy, Safety, and Tolerability of Valbenazine for the Treatment of Dyskinesia Due to Cerebral Palsy

NCT05206513 ·Status: COMPLETED ·Phase: PHASE3

NF-κB Inhibition in Amyotrophic Lateral Sclerosis

NCT05031351 ·Status: UNKNOWN ·Phase: PHASE2

Phase IIIb, Open-label, Multi-center Study to Evaluate Safety, Tolerability and Efficacy of OAV101 Administered Intrathecally to Participants With SMA Who Discontinued Treatment With Nusinersen or Risdiplam

NCT05386680 ·Status: COMPLETED ·Phase: PHASE3

Safety and Efficacy of Lithium Carbonate in Patients With Spinocerebellar Ataxia Type 3

NCT01096082 ·Status: COMPLETED ·Phase: PHASE2/PHASE3

Efficacy, Tolerability, and Pharmacokinetics of Multiple Doses of Oral TAK-831 in Adults With Friedreich Ataxia

NCT03214588 ·Status: COMPLETED ·Phase: PHASE2

Study of the Oral Treatment MTR-601 in Cervical Dystonia

NCT06830642 ·Status: SUSPENDED ·Phase: PHASE2

Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam

NCT05156320 ·Status: COMPLETED ·Phase: PHASE3

Valproate and Levocarnitine in Children With Spinal Muscular Atrophy

NCT01671384 ·Status: UNKNOWN ·Phase: PHASE3

Valproic Acid in Ambulant Adults With Spinal Muscular Atrophy

NCT00481013 ·Status: COMPLETED ·Phase: PHASE2