Trial Outcomes & Findings for (CB-01-02/04) Extension Study of Budesonide Multi-Matrix System (MMX) 6 mg in Maintenance Of Remission In Patients With Ulcerative Colitis. (NCT NCT00801723)

NCT ID: NCT00801723

Last Updated: 2020-08-31

Results Overview

Clinical remission was defined as the combined absence of recurrence of rectal bleeding and absence of increased stool frequency.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

123 participants

Primary outcome timeframe

1, 3, 6, 9, and 12 months

Results posted on

2020-08-31

Participant Flow

Participant milestones

Participant milestones
Measure
2: Placebo
One placebo tablet self-administered by the patients with a glass of water, in the morning after breakfast. Placebo Tablet: Placebo Tablet once daily.
1: Budesonide MMX® 6 mg
One Budesonide-MMX® 6 mg tablet self-administered by the patients with a glass of water, in the morning after breakfast. Budesonide MMX 6 mg Tablet: Budesonide MMX 6 mg Tablet once daily.
Overall Study
STARTED
61
62
Overall Study
COMPLETED
25
27
Overall Study
NOT COMPLETED
36
35

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

(CB-01-02/04) Extension Study of Budesonide Multi-Matrix System (MMX) 6 mg in Maintenance Of Remission In Patients With Ulcerative Colitis.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
2: Placebo
n=61 Participants
One placebo tablet self-administered by the patients with a glass of water, in the morning after breakfast. Placebo Tablet: Placebo Tablet once daily.
1: Budesonide MMX® 6 mg
n=62 Participants
One Budesonide-MMX® 6 mg tablet self-administered by the patients with a glass of water, in the morning after breakfast. Budesonide MMX 6 mg Tablet: Budesonide MMX 6 mg Tablet once daily.
Total
n=123 Participants
Total of all reporting groups
Age, Continuous
42.0 years
STANDARD_DEVIATION 11.77 • n=99 Participants
42.9 years
STANDARD_DEVIATION 12.65 • n=107 Participants
42.5 years
STANDARD_DEVIATION 12.21 • n=206 Participants
Sex: Female, Male
Female
28 Participants
n=99 Participants
26 Participants
n=107 Participants
54 Participants
n=206 Participants
Sex: Female, Male
Male
33 Participants
n=99 Participants
36 Participants
n=107 Participants
69 Participants
n=206 Participants

PRIMARY outcome

Timeframe: 1, 3, 6, 9, and 12 months

Population: Number of participants with sufficient diary data to enable determination of clinical remission status at the indicated visit.

Clinical remission was defined as the combined absence of recurrence of rectal bleeding and absence of increased stool frequency.

Outcome measures

Outcome measures
Measure
2: Placebo
n=32 Participants
One placebo tablet self-administered by the patients with a glass of water, in the morning after breakfast. Placebo Tablet: Placebo Tablet once daily.
1: Budesonide MMX® 6 mg
n=39 Participants
One Budesonide-MMX® 6 mg tablet self-administered by the patients with a glass of water, in the morning after breakfast. Budesonide MMX 6 mg Tablet: Budesonide MMX 6 mg Tablet once daily.
Percentage of Participants Achieving Clinical Remission
1 month
76.7 percentage of participants
88.2 percentage of participants
Percentage of Participants Achieving Clinical Remission
3 months
92.0 percentage of participants
96.8 percentage of participants
Percentage of Participants Achieving Clinical Remission
6 months
76.2 percentage of participants
80.0 percentage of participants
Percentage of Participants Achieving Clinical Remission
9 months
86.7 percentage of participants
95.0 percentage of participants
Percentage of Participants Achieving Clinical Remission
12 months
84.6 percentage of participants
93.3 percentage of participants

SECONDARY outcome

Timeframe: 12 months

Population: Participants with sufficient diary data to enable determination of clinical relapse status.

Clinical relapse was defined as the recurrence of rectal bleeding and/or an abnormal stool frequency \[≥ 1-2 stools/day above normal for the participant. Clinical remission/relapse status was based on participant diary entries prior to each scheduled visit.

Outcome measures

Outcome measures
Measure
2: Placebo
n=32 Participants
One placebo tablet self-administered by the patients with a glass of water, in the morning after breakfast. Placebo Tablet: Placebo Tablet once daily.
1: Budesonide MMX® 6 mg
n=39 Participants
One Budesonide-MMX® 6 mg tablet self-administered by the patients with a glass of water, in the morning after breakfast. Budesonide MMX 6 mg Tablet: Budesonide MMX 6 mg Tablet once daily.
Percentage of Participants With Clinical Relapse
19 Participants
12 Participants

SECONDARY outcome

Timeframe: 12 months

Population: Participants with sufficient index score data to enable determination of endoscopic relapse status.

Endoscopic relapse was defined as an increase of ≥ 2 points in the Endoscopic Index score from the value calculated at baseline. The score is comprised of four components (granulated scattering reflected light, vascular pattern, vulnerability of mucosa, and mucosal damage). Scores range from 0 to 12, and higher scores indicate more severe (worse) endoscopic findings.

Outcome measures

Outcome measures
Measure
2: Placebo
n=32 Participants
One placebo tablet self-administered by the patients with a glass of water, in the morning after breakfast. Placebo Tablet: Placebo Tablet once daily.
1: Budesonide MMX® 6 mg
n=39 Participants
One Budesonide-MMX® 6 mg tablet self-administered by the patients with a glass of water, in the morning after breakfast. Budesonide MMX 6 mg Tablet: Budesonide MMX 6 mg Tablet once daily.
Percentage of Participants With Endoscopic Relapse
16 Participants
27 Participants

Adverse Events

2: Placebo

Serious events: 1 serious events
Other events: 30 other events
Deaths: 0 deaths

1: Budesonide MMX® 6 mg

Serious events: 1 serious events
Other events: 34 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
2: Placebo
n=61 participants at risk
One placebo tablet self-administered by the patients with a glass of water, in the morning after breakfast. Placebo Tablet: Placebo Tablet once daily.
1: Budesonide MMX® 6 mg
n=62 participants at risk
One Budesonide-MMX® 6 mg tablet self-administered by the patients with a glass of water, in the morning after breakfast. Budesonide MMX 6 mg Tablet: Budesonide MMX 6 mg Tablet once daily.
Infections and infestations
Lobar pneumonia
1.6%
1/61 • 12 months
0.00%
0/62 • 12 months
Vascular disorders
Hypertension
0.00%
0/61 • 12 months
1.6%
1/62 • 12 months

Other adverse events

Other adverse events
Measure
2: Placebo
n=61 participants at risk
One placebo tablet self-administered by the patients with a glass of water, in the morning after breakfast. Placebo Tablet: Placebo Tablet once daily.
1: Budesonide MMX® 6 mg
n=62 participants at risk
One Budesonide-MMX® 6 mg tablet self-administered by the patients with a glass of water, in the morning after breakfast. Budesonide MMX 6 mg Tablet: Budesonide MMX 6 mg Tablet once daily.
Gastrointestinal disorders
Colitis ulcerative
26.2%
16/61 • 12 months
17.7%
11/62 • 12 months
Gastrointestinal disorders
Abdominal pain
8.2%
5/61 • 12 months
9.7%
6/62 • 12 months
Nervous system disorders
Headache
3.3%
2/61 • 12 months
6.5%
4/62 • 12 months
Musculoskeletal and connective tissue disorders
Osteopenia
8.2%
5/61 • 12 months
1.6%
1/62 • 12 months
Gastrointestinal disorders
Frequent bowel movements
1.6%
1/61 • 12 months
6.5%
4/62 • 12 months
Blood and lymphatic system disorders
Haematochezia
1.6%
1/61 • 12 months
6.5%
4/62 • 12 months
Gastrointestinal disorders
Constipation
0.00%
0/61 • 12 months
6.5%
4/62 • 12 months

Additional Information

Study Director

Bausch Health

Results disclosure agreements

  • Principal investigator is a sponsor employee Contact sponsor directly for details.
  • Publication restrictions are in place

Restriction type: OTHER