Study About the Evolution of Severe Late Onset Pompe Disease Patient With Pulmonary Dysfunction and Receiving Myozyme®
NCT00731081 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 8
Last updated 2014-02-06
Summary
To describe severe late onset patients with pompe disease receiving Myozyme®
Conditions
- Pompe Disease (Late-Onset)
- Glycogen Storage Disease Type II (GSD II)
- Glycogenesis 2 Acid Maltase Deficiency
Sponsors & Collaborators
-
Genzyme, a Sanofi Company
lead INDUSTRY
Principal Investigators
-
Medical Monitor · Genzyme, a Sanofi Company
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2007-03-31
- Primary Completion
- 2009-05-31
- Completion
- 2009-05-31
Countries
- France
Study Locations
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