Trial Outcomes & Findings for Tipifarnib and Etoposide in Treating Older Patients With Newly Diagnosed, Previously Untreated Acute Myeloid Leukemia (NCT NCT00602771)

NCT ID: NCT00602771

Last Updated: 2014-10-09

Results Overview

Bone marrow showing less than 5% myeloblasts with normal maturation of all cell lines, an ANC of at least 1000/mcL and a platelet count of 100,000 mcL, absence of blast in peripheral blood, absence of identifiable leukemic cells in the bone marrow, clearance of disease-associated cytogenetic abnormalities, and clearance of any previously existing extramedullary disease. A CR must be confirmed 4 to 6 weeks after the initial documentation. If possible, at least one bone marrow biopsy should be performed to confirm the CR.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

84 participants

Primary outcome timeframe

6 months

Results posted on

2014-10-09

Participant Flow

January 2008 and December 2009,

5 patients signed consent, but were deemed screen failures and did not begin study treatment

Participant milestones

Participant milestones
Measure
Arm I
Patients receive 600 mg of oral tipifarnib twice daily on days 1-14 and 100 mg of oral etoposide once daily on days 1-3 and 8-10.
Arm II (Closed to Accrual as of November 2008)
Patients receive 400 mg of oral tipifarnib twice daily on days 1-14 and 200 mg of oral etoposide once daily on days 1-3 and 8-10.
Overall Study
STARTED
63
21
Overall Study
COMPLETED
62
21
Overall Study
NOT COMPLETED
1
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Tipifarnib and Etoposide in Treating Older Patients With Newly Diagnosed, Previously Untreated Acute Myeloid Leukemia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Arm I
n=63 Participants
Patients receive 600 mg of oral tipifarnib twice daily on days 1-14 and 100 mg of oral etoposide once daily on days 1-3 and 8-10.
Arm II (Closed to Accrual as of November 2008)
n=21 Participants
Patients receive 400 mg of oral tipifarnib twice daily on days 1-14 and 200 mg of oral etoposide once daily on days 1-3 and 8-10.
Total
n=84 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=39 Participants
0 Participants
n=41 Participants
0 Participants
n=35 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=39 Participants
0 Participants
n=41 Participants
0 Participants
n=35 Participants
Age, Categorical
>=65 years
63 Participants
n=39 Participants
21 Participants
n=41 Participants
84 Participants
n=35 Participants
Age, Continuous
76 years
STANDARD_DEVIATION 20 • n=39 Participants
78 years
STANDARD_DEVIATION 19 • n=41 Participants
76 years
STANDARD_DEVIATION 20 • n=35 Participants
Sex: Female, Male
Female
24 Participants
n=39 Participants
7 Participants
n=41 Participants
31 Participants
n=35 Participants
Sex: Female, Male
Male
39 Participants
n=39 Participants
14 Participants
n=41 Participants
53 Participants
n=35 Participants
Region of Enrollment
United States
63 participants
n=39 Participants
21 participants
n=41 Participants
84 participants
n=35 Participants

PRIMARY outcome

Timeframe: 6 months

Bone marrow showing less than 5% myeloblasts with normal maturation of all cell lines, an ANC of at least 1000/mcL and a platelet count of 100,000 mcL, absence of blast in peripheral blood, absence of identifiable leukemic cells in the bone marrow, clearance of disease-associated cytogenetic abnormalities, and clearance of any previously existing extramedullary disease. A CR must be confirmed 4 to 6 weeks after the initial documentation. If possible, at least one bone marrow biopsy should be performed to confirm the CR.

Outcome measures

Outcome measures
Measure
Arm I
n=15 Participants
Patients receive 600 mg of oral tipifarnib twice daily on days 1-14 and 100 mg of oral etoposide once daily on days 1-3 and 8-10.
Arm II (Closed to Accrual as of November 2008)
n=6 Participants
Patients receive 400 mg of oral tipifarnib twice daily on days 1-14 and 200 mg of oral etoposide once daily on days 1-3 and 8-10.
Complete Response
0 participants
0 participants

Adverse Events

Arm I

Serious events: 5 serious events
Other events: 18 other events
Deaths: 0 deaths

Arm II (Closed to Accrual as of November 2008)

Serious events: 8 serious events
Other events: 6 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Arm I
n=63 participants at risk
Patients receive 600 mg of oral tipifarnib twice daily on days 1-14 and 100 mg of oral etoposide once daily on days 1-3 and 8-10.
Arm II (Closed to Accrual as of November 2008)
n=21 participants at risk
Patients receive 400 mg of oral tipifarnib twice daily on days 1-14 and 200 mg of oral etoposide once daily on days 1-3 and 8-10.
General disorders
non-hematologic toxicities
6.3%
4/63 • Number of events 4
33.3%
7/21 • Number of events 7
Infections and infestations
Infections
7.9%
5/63 • Number of events 5
38.1%
8/21 • Number of events 8

Other adverse events

Other adverse events
Measure
Arm I
n=63 participants at risk
Patients receive 600 mg of oral tipifarnib twice daily on days 1-14 and 100 mg of oral etoposide once daily on days 1-3 and 8-10.
Arm II (Closed to Accrual as of November 2008)
n=21 participants at risk
Patients receive 400 mg of oral tipifarnib twice daily on days 1-14 and 200 mg of oral etoposide once daily on days 1-3 and 8-10.
Nervous system disorders
Dose reduction
28.6%
18/63 • Number of events 18
28.6%
6/21 • Number of events 6

Additional Information

Judith Karp, MD

SKCCC

Phone: 410-502-7726

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60