Trial Outcomes & Findings for Trial of Paclitaxel, Bevacizumab, and Enzastaurin Versus Paclitaxel, Bevacizumab and Placebo for Breast Cancer (NCT NCT00536939)

NCT ID: NCT00536939

Last Updated: 2020-09-24

Results Overview

PFS was defined as the time from the date of study enrollment to the first date of objectively determined progressive disease (PD) or death from any cause. PD was determined using Response Evaluation Criteria In Solid Tumors (RECIST version 1.0). PD is ≥20% increase in the sum of the longest diameter (LD) of target lesions taking as references the smallest sum LD recorded since the treatment started or the appearance of 1 or more new lesions. For participants not known to have died and who did not have PD, PFS was censored at the date of the last progression-free assessment. For participants who received subsequent systemic anticancer therapy (after discontinuation from the study treatment) prior to disease progression or death, PFS was censored at the date of last progression-free assessment prior to the initiation of post-discontinuation systemic anticancer therapy. No participant completed a full cycle of therapy and thus no formal analysis was performed.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

2 participants

Primary outcome timeframe

Baseline to measured PD (up to 15 days)

Results posted on

2020-09-24

Participant Flow

This study consisted of a safety lead-in prior to randomization. The study was terminated prior to completion of safety lead-in period.

Participant milestones

Participant milestones
Measure
Enzastaurin + Bevacizumab + Paclitaxel
Safety Lead-in Period: Enzastaurin 1125 milligrams (mg) loading dose (total nine 125-mg tablets: 3 tablets, 3 times daily) administered orally, only on Day 1 of Cycle 1, followed by 500 mg (four 125-mg tablets) administered orally, once daily in a 28-day cycle plus bevacizumab 10 milligrams per kilogram (mg/kg) administered intravenously on Days 1 and 15 of every 28-day cycle plus paclitaxel 90 milligrams per square meter (mg/m\^2) administered intravenously on Days 1, 8 and 15 of every 28-day cycle. Participants were to receive enzastaurin, bevacizumab and paclitaxel for 2 cycles (1 cycle = 28 days). Randomization Period: Participants were to receive the same treatment as administered during the safety lead-in period. Treatment was to continue until there was evidence of disease progression or intolerable toxicity.
Bevacizumab + Paclitaxel + Placebo
Safety lead-in Period: No treatment Randomization Period: Participants were to receive bevacizumab 10 mg/kg administered intravenously on Days 1 and 15 of every 28-day cycle plus paclitaxel 90 mg/m\^2 administered intravenously on Days 1, 8 and 15 of every 28-day cycle plus placebo loading dose administered orally (total 9 tablets: 3 tablets, 3 times daily) only on Day 1 of Cycle 1, followed by oral administration once daily in a 28-day cycle. Treatment was to continue until there was disease progression or intolerable toxicity.
Overall Study
STARTED
2
0
Overall Study
Entered Safety lead-in
2
0
Overall Study
Randomized
0
0
Overall Study
COMPLETED
0
0
Overall Study
NOT COMPLETED
2
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Enzastaurin + Bevacizumab + Paclitaxel
Safety Lead-in Period: Enzastaurin 1125 milligrams (mg) loading dose (total nine 125-mg tablets: 3 tablets, 3 times daily) administered orally, only on Day 1 of Cycle 1, followed by 500 mg (four 125-mg tablets) administered orally, once daily in a 28-day cycle plus bevacizumab 10 milligrams per kilogram (mg/kg) administered intravenously on Days 1 and 15 of every 28-day cycle plus paclitaxel 90 milligrams per square meter (mg/m\^2) administered intravenously on Days 1, 8 and 15 of every 28-day cycle. Participants were to receive enzastaurin, bevacizumab and paclitaxel for 2 cycles (1 cycle = 28 days). Randomization Period: Participants were to receive the same treatment as administered during the safety lead-in period. Treatment was to continue until there was evidence of disease progression or intolerable toxicity.
Bevacizumab + Paclitaxel + Placebo
Safety lead-in Period: No treatment Randomization Period: Participants were to receive bevacizumab 10 mg/kg administered intravenously on Days 1 and 15 of every 28-day cycle plus paclitaxel 90 mg/m\^2 administered intravenously on Days 1, 8 and 15 of every 28-day cycle plus placebo loading dose administered orally (total 9 tablets: 3 tablets, 3 times daily) only on Day 1 of Cycle 1, followed by oral administration once daily in a 28-day cycle. Treatment was to continue until there was disease progression or intolerable toxicity.
Overall Study
Withdrawal by Subject
1
0
Overall Study
Other Complicating Disease
1
0

Baseline Characteristics

Trial of Paclitaxel, Bevacizumab, and Enzastaurin Versus Paclitaxel, Bevacizumab and Placebo for Breast Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Enzastaurin + Bevacizumab + Paclitaxel
n=2 Participants
Safety Lead-in Period: Enzastaurin 1125 milligrams (mg) loading dose (total nine 125-mg tablets: 3 tablets, 3 times daily) administered orally, only on Day 1 of Cycle 1, followed by 500 mg (four 125-mg tablets) administered orally, once daily in a 28-day cycle plus bevacizumab 10 milligrams per kilogram (mg/kg) administered intravenously on Days 1 and 15 of every 28-day cycle plus paclitaxel 90 milligrams per square meter (mg/m\^2) administered intravenously on Days 1, 8 and 15 of every 28-day cycle. Participants were to receive enzastaurin, bevacizumab and paclitaxel for 2 cycles (1 cycle = 28 days). Randomization Period: Participants were to receive the same treatment as administered during the safety lead-in period. Treatment was to continue until there was evidence of disease progression or intolerable toxicity.
Age, Continuous
56.5 years
STANDARD_DEVIATION 16.26 • n=99 Participants
Sex: Female, Male
Female
2 Participants
n=99 Participants
Sex: Female, Male
Male
0 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
2 Participants
n=99 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=99 Participants
Race/Ethnicity, Customized
White
2 Participants
n=99 Participants
Region of Enrollment
United States
2 Participants
n=99 Participants

PRIMARY outcome

Timeframe: Baseline to measured PD (up to 15 days)

Population: No participant completed a full cycle of therapy and data were not collected for this Outcome Measure.

PFS was defined as the time from the date of study enrollment to the first date of objectively determined progressive disease (PD) or death from any cause. PD was determined using Response Evaluation Criteria In Solid Tumors (RECIST version 1.0). PD is ≥20% increase in the sum of the longest diameter (LD) of target lesions taking as references the smallest sum LD recorded since the treatment started or the appearance of 1 or more new lesions. For participants not known to have died and who did not have PD, PFS was censored at the date of the last progression-free assessment. For participants who received subsequent systemic anticancer therapy (after discontinuation from the study treatment) prior to disease progression or death, PFS was censored at the date of last progression-free assessment prior to the initiation of post-discontinuation systemic anticancer therapy. No participant completed a full cycle of therapy and thus no formal analysis was performed.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline to measured Progressive disease (up to 15 days)

Population: No participant completed a full cycle of therapy and data were not collected for this Outcome Measure.

ORR was defined as the percentage of participants with a confirmed complete response (CR) or partial response (PR), assessed according to the Response Evaluation Criteria In Solid Tumors (RECIST version 1.0). CR was defined as the disappearance of all tumor lesions; PR was defined as either ≥30% decrease in the sum of the longest diameter (LD) of target lesions taking as reference the baseline sum LDs or complete disappearance of target lesions, with persistence (but not worsening) of 1 or more non-target lesions. In either case of PR, no new lesions should have appeared. The percentage of participants with ORR was calculated as a total number of participants with CR or PR from the start of study treatment until disease progression or recurrence divided by the total number of participants treated, then multiplied by 100. No participant completed a full cycle of therapy and thus no formal analysis was performed.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline to study completion (Day 15) plus 30-day safety follow-up

Population: All enrolled participants.

A summary of SAEs and all other non-serious AEs, regardless of causality, is located in the Reported Adverse Event module.

Outcome measures

Outcome measures
Measure
Enzastaurin + Bevacizumab + Paclitaxel
n=2 Participants
Safety Lead-in Period: Enzastaurin 1125 milligrams (mg) loading dose (total nine 125-mg tablets: 3 tablets, 3 times daily) administered orally, only on Day 1 of Cycle 1, followed by 500 mg (four 125-mg tablets) administered orally, once daily in a 28-day cycle plus bevacizumab 10 milligrams per kilogram (mg/kg) administered intravenously on Days 1 and 15 of every 28-day cycle plus paclitaxel 90 milligrams per square meter (mg/m\^2) administered intravenously on Days 1, 8 and 15 of every 28-day cycle. Participants were to receive enzastaurin, bevacizumab and paclitaxel for 2 cycles (1 cycle = 28 days). Randomization Period: Participants were to receive the same treatment as administered during the safety lead-in period. Treatment was to continue until there was evidence of disease progression or intolerable toxicity.
Number of Participants With Adverse Events (AEs) or Any Serious AEs (SAEs)
Adverse Events (AEs)
2 Participants
Number of Participants With Adverse Events (AEs) or Any Serious AEs (SAEs)
Serious Adverse Events (SAEs)
0 Participants

Adverse Events

Enzastaurin + Bevacizumab + Paclitaxel

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Enzastaurin + Bevacizumab + Paclitaxel
n=2 participants at risk
Safety Lead-in Period: Enzastaurin 1125 milligrams (mg) loading dose (total nine 125-mg tablets: 3 tablets, 3 times daily) administered orally, only on Day 1 of Cycle 1, followed by 500 mg (four 125-mg tablets) administered orally, once daily in a 28-day cycle plus bevacizumab 10 milligrams per kilogram (mg/kg) administered intravenously on Days 1 and 15 of every 28-day cycle plus paclitaxel 90 milligrams per square meter (mg/m\^2) administered intravenously on Days 1, 8 and 15 of every 28-day cycle. Participants were to receive enzastaurin, bevacizumab and paclitaxel for 2 cycles (1 cycle = 28 days). Randomization Period: Participants were to receive the same treatment as administered during the safety lead-in period. Treatment was to continue until there was evidence of disease progression or intolerable toxicity.
Blood and lymphatic system disorders
Leukopenia
50.0%
1/2 • Number of events 2
Gastrointestinal disorders
Nausea
50.0%
1/2 • Number of events 1
General disorders
Oedema peripheral
50.0%
1/2 • Number of events 1
General disorders
Pain
50.0%
1/2 • Number of events 2
Infections and infestations
Infection
50.0%
1/2 • Number of events 1
Investigations
Haemoglobin decreased
50.0%
1/2 • Number of events 1
Investigations
Neutrophil count decreased
50.0%
1/2 • Number of events 1
Musculoskeletal and connective tissue disorders
Musculoskeletal disorder
50.0%
1/2 • Number of events 1
Nervous system disorders
Headache
50.0%
1/2 • Number of events 1

Additional Information

Chief Medical Officer

Eli Lilly and Company

Phone: 800-545-5979

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: GT60