Trial Outcomes & Findings for Effects of Methylphenidate on Cellular Abnormalities in Children With Attention Deficit Hyperactivity Disorder (ADHD) (NCT NCT00409708)

NCT ID: NCT00409708

Last Updated: 2011-05-17

Results Overview

The number of chromosomal aberrations per 100 cells excluding gaps at Baseline (n=33, n=32) and at Week 12 (n=33, n=32) was counted in blood samples cultured for 48 hours using a standard protocol. The types of abnormalities included translocations (reciprocal and non-reciprocal), insertions, dicentrics, fragments, inversions, chromatid exchanges (quadriradials and triradials), breaks, and other unusual observations, eg, aneuploidy, tetraploidy or endoreduplication.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

142 participants

Primary outcome timeframe

baseline and at end of treatment (Week 12)

Results posted on

2011-05-17

Participant Flow

Participant milestones

Participant milestones
Measure
Ritalin LA Plus Behavior Therapy
10-60 mg/day
Behavior Therapy
0 mg/day Ritalin LA
Treatment
STARTED
53
56
Treatment
COMPLETED
38
39
Treatment
NOT COMPLETED
15
17
Washout
STARTED
38
39
Washout
COMPLETED
17
29
Washout
NOT COMPLETED
21
10

Reasons for withdrawal

Reasons for withdrawal
Measure
Ritalin LA Plus Behavior Therapy
10-60 mg/day
Behavior Therapy
0 mg/day Ritalin LA
Treatment
Abnormal test procedure result(s)
1
0
Treatment
Lack of Efficacy
0
1
Treatment
Protocol Violation
6
2
Treatment
Withdrawal by Subject
3
8
Treatment
Lost to Follow-up
0
6
Treatment
Administrative problems
5
0
Washout
Lack of Efficacy
9
1
Washout
Protocol Violation
0
1
Washout
Withdrawal by Subject
11
5
Washout
Lost to Follow-up
1
3

Baseline Characteristics

Effects of Methylphenidate on Cellular Abnormalities in Children With Attention Deficit Hyperactivity Disorder (ADHD)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Ritalin LA Plus Behavior Therapy
n=52 Participants
10-60 mg/day
Behavior Therapy
n=52 Participants
0 mg/day Ritalin LA
Total
n=104 Participants
Total of all reporting groups
Age, Categorical
<=18 years
52 Participants
n=99 Participants
52 Participants
n=107 Participants
104 Participants
n=206 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age Continuous
8.3 years
STANDARD_DEVIATION 1.75 • n=99 Participants
8.5 years
STANDARD_DEVIATION 1.91 • n=107 Participants
8.4 years
STANDARD_DEVIATION 1.83 • n=206 Participants
Sex: Female, Male
Female
21 Participants
n=99 Participants
17 Participants
n=107 Participants
38 Participants
n=206 Participants
Sex: Female, Male
Male
31 Participants
n=99 Participants
35 Participants
n=107 Participants
66 Participants
n=206 Participants

PRIMARY outcome

Timeframe: baseline and at end of treatment (Week 12)

Population: Per-Protocol-1 (PP1) population: The PP1 population consisted of all patients who were randomized and provided cytogenetic data for at least one of the primary endpoints at baseline and at the Week 12 evaluation.

The number of chromosomal aberrations per 100 cells excluding gaps at Baseline (n=33, n=32) and at Week 12 (n=33, n=32) was counted in blood samples cultured for 48 hours using a standard protocol. The types of abnormalities included translocations (reciprocal and non-reciprocal), insertions, dicentrics, fragments, inversions, chromatid exchanges (quadriradials and triradials), breaks, and other unusual observations, eg, aneuploidy, tetraploidy or endoreduplication.

Outcome measures

Outcome measures
Measure
Ritalin LA Plus Behavior Therapy
n=36 Participants
10-60 mg/day
Behavior Therapy
n=35 Participants
0 mg/day Ritalin LA
The Number of Chromosomal Aberrations Per 100 Cells Excluding Gaps at Baseline and at the End of Treatment i.e Day 84 (Week 12)
Baseline
1.05 number of abnormalities
Standard Deviation 1.246
0.75 number of abnormalities
Standard Deviation 1.008
The Number of Chromosomal Aberrations Per 100 Cells Excluding Gaps at Baseline and at the End of Treatment i.e Day 84 (Week 12)
At the end of treatment i.e. week12: Mean
0.53 number of abnormalities
Standard Deviation 1.132
0.41 number of abnormalities
Standard Deviation 0.665

PRIMARY outcome

Timeframe: baseline and at end of treatment (Week 12)

The number of micronuclei per 1000 binucleated cells was measured at Baseline ( n=34 , n=29 ) and at the end of treatment, Week 12 (n =34, n= 29), in blood cultured for 48 hours using a standard protocol.

Outcome measures

Outcome measures
Measure
Ritalin LA Plus Behavior Therapy
n=36 Participants
10-60 mg/day
Behavior Therapy
n=35 Participants
0 mg/day Ritalin LA
The Number of Micronuclei Per 1000 Binucleated Cells Endpoints at Baseline and at the End of Treatment i.e Day 84 (Week 12)
At Baseline
5.76 number of micronuclei per 1000 binucleat
Standard Deviation 2.336
5.71 number of micronuclei per 1000 binucleat
Standard Deviation 4.535
The Number of Micronuclei Per 1000 Binucleated Cells Endpoints at Baseline and at the End of Treatment i.e Day 84 (Week 12)
At the end of treatment i.e. Week 12
3.63 number of micronuclei per 1000 binucleat
Standard Deviation 2.053
4.19 number of micronuclei per 1000 binucleat
Standard Deviation 2.737

SECONDARY outcome

Timeframe: baseline and at end of treatment (Week 12)

Population: Per-Protocol-2 population: The PP2 population consisted of all subjects who were randomized and provided at least one post-baseline efficacy assessment.

Blood collected at baseline (n=20, n=14) and at the end of treatment, Week 12, (n= 20, n= 14) was cultured for 48 hours using a standard protocol. Giemsa staining and/or fluorescent in situ hybridization (FISH) chromosome painting was done on the cells in metaphase and the number of chromatoid exchanges per cell was recorded by blinded raters.

Outcome measures

Outcome measures
Measure
Ritalin LA Plus Behavior Therapy
n=38 Participants
10-60 mg/day
Behavior Therapy
n=37 Participants
0 mg/day Ritalin LA
Number of Sister Chromatoid Exchanges Per Cell
Baseline
7.807 number of sister chromatoid exchanges
Standard Deviation 0.9228
7.533 number of sister chromatoid exchanges
Standard Deviation 1.2160
Number of Sister Chromatoid Exchanges Per Cell
At the end of treatment i.e. Week12
7.213 number of sister chromatoid exchanges
Standard Deviation 1.0408
7.303 number of sister chromatoid exchanges
Standard Deviation 0.6165

SECONDARY outcome

Timeframe: End of treatment (Week 12)

Since no cytogenetic effects were observed, blood samples were not analyzed for pharmacokinetics/pharmacodynamics.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline to end of treatment (Week 12)

Population: Per-Protocol-2 (PP2) Population: The PP2 population consisted of all subjects who were randomized and provided at least one post-baseline efficacy assessment.

Parents completed the Conners' ADHD/DSM-IV Scale for Parents (CADS-P) consisting of the ADHD Index (12 items) and the Diagnostic and Statistical Manual of Mental Disorders, Fourth Edition (DSM-IV)( 18 items). Parents rated their child's behavior of the previous week from a list of common problems. When asked "How much of a problem has this been in the last week?" parents selected 0 = none, not at all, seldom, or very infrequently; 3 = very much true, or it occurs very often or frequently; or 1 or 2 for ratings in between. A score of 50 is considered normal and more than 70 markedly atypical.

Outcome measures

Outcome measures
Measure
Ritalin LA Plus Behavior Therapy
n=38 Participants
10-60 mg/day
Behavior Therapy
n=37 Participants
0 mg/day Ritalin LA
Change From Baseline to End of Treatment (Week 12) on the Conners' ADHD/DSM-IV Scale for Parents (CADS-P)
-17.0 Units on a rating scale
Standard Deviation 11.23
-7.0 Units on a rating scale
Standard Deviation 9.97

SECONDARY outcome

Timeframe: From baseline to the end of treatment (Week 12)

Population: Per-Protocol-2 (PP2) Population: The PP2 population consisted of all subjects who were randomized and provided at least one post-baseline efficacy assessment.

The Clinical Global Impression scale (CGI-I) is a clinician-rated instrument designed to assess the overall change of illness relative to baseline. The CGI-I consists of 7 ratings as follows: 1 = very much improved, 2 = much improved, 3 = minimally improved, 4 = no change, 5 = minimally worse, 6 = much worse, and 7 = very much worse. CGI-I assessments are relative to the patient's status at the Baseline visit.

Outcome measures

Outcome measures
Measure
Ritalin LA Plus Behavior Therapy
n=38 Participants
10-60 mg/day
Behavior Therapy
n=37 Participants
0 mg/day Ritalin LA
Change From Baseline to the End of Treatment (Week 12) on the Global Improvement Rating of the Clinical Global Impression Scale (CGI-I)
1.9 Units on a rating scale
Standard Deviation 0.81
3.0 Units on a rating scale
Standard Deviation 0.97

SECONDARY outcome

Timeframe: From baseline to the end of treatment (Week 12)

Population: Per-Protocol-2 (PP2) Population: The PP2 population consisted of all subjects who were randomized and provided at least one post-baseline efficacy assessment.

The Clinical Global Impression scale (CGI-S) is a clinician-rated instrument designed to assess the severity of illness. The CGI-S rating indicates illness severity at each time-point on a scale as follows: 1 = normal, not at all ill; 2 = borderline mentally ill; 3 = mildly ill; 4 = moderately ill; 5 = markedly ill; 6 = severely ill; and 7 = extremely ill. CGI-S assessments are relative to the patient's status at the Baseline visit.

Outcome measures

Outcome measures
Measure
Ritalin LA Plus Behavior Therapy
n=38 Participants
10-60 mg/day
Behavior Therapy
n=37 Participants
0 mg/day Ritalin LA
Change From Baseline to the End of Treatment (Week 12) on the Severity of Illness Rating of the Clinical Global Impression Scale (CGI-S)
-1.9 Units on a rating scale
Standard Deviation 0.98
-0.6 Units on a rating scale
Standard Deviation 1.01

Adverse Events

Ritalin+Behavior

Serious events: 0 serious events
Other events: 28 other events
Deaths: 0 deaths

Behavior

Serious events: 0 serious events
Other events: 13 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Ritalin+Behavior
n=52 participants at risk
Ritalin+Behavior
Behavior
n=52 participants at risk
Behavior
Gastrointestinal disorders
Abdominal Pain Upper
9.6%
5/52
3.8%
2/52
Gastrointestinal disorders
Vomiting
9.6%
5/52
1.9%
1/52
General disorders
Fatigue
7.7%
4/52
0.00%
0/52
General disorders
Pyrexia
3.8%
2/52
5.8%
3/52
Infections and infestations
Nasopharyngitis
7.7%
4/52
7.7%
4/52
Infections and infestations
Upper Respiratory Tract Infection
11.5%
6/52
9.6%
5/52
Metabolism and nutrition disorders
Decreased Appetite
19.2%
10/52
0.00%
0/52
Nervous system disorders
Headache
13.5%
7/52
1.9%
1/52
Psychiatric disorders
Initial Insomnia
5.8%
3/52
0.00%
0/52
Psychiatric disorders
Insomnia
9.6%
5/52
0.00%
0/52
Psychiatric disorders
Tearfulness
5.8%
3/52
0.00%
0/52
Respiratory, thoracic and mediastinal disorders
Cough
7.7%
4/52
1.9%
1/52

Additional Information

Study Director

Novartis Pharmaceuticals

Phone: 862 778-8300

Results disclosure agreements

  • Principal investigator is a sponsor employee The terms and conditions of Novartis' agreements with its investigators may vary. However, Novartis does not prohibit any investigator from publishing. Any publications from a single-site are postponed until the publication of the pooled data (i.e., data from all sites) in the clinical trial.
  • Publication restrictions are in place

Restriction type: OTHER