Trial Outcomes & Findings for Comparison of the Safety and Efficacy of Intravenous Iron Versus Oral Iron in the Treatment of Anemia Secondary to Heavy Uterine Bleeding (NCT NCT00395993)

NCT ID: NCT00395993

Last Updated: 2018-02-20

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

456 participants

Primary outcome timeframe

Any time between baseline and the end of study or time to intervention

Results posted on

2018-02-20

Participant Flow

Hospitals and medical clinics

Participant milestones

Participant milestones
Measure
Ferric Carboxymaltose (FCM)
Maximum of 1,000 mg of iron as IV FCM given at weekly intervals until the individual's calculated cumulative dose has been reached or a maximum of 2,500 mg has been administered
Oral Iron Tablets
325 mg tablets TID on Days 0 through Day 42
Overall Study
STARTED
246
231
Overall Study
COMPLETED
211
212
Overall Study
NOT COMPLETED
35
19

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Comparison of the Safety and Efficacy of Intravenous Iron Versus Oral Iron in the Treatment of Anemia Secondary to Heavy Uterine Bleeding

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Ferric Carboxymaltose (FCM)
n=230 Participants
Maximum of 1,000 mg of iron as IV FCM given at weekly intervals until the individual's calculated cumulative dose has been reached or a maximum of 2,500 mg has been administered
Oral Iron Tablets
n=226 Participants
325 mg tablets TID on Days 0 through Day 42
Total
n=456 Participants
Total of all reporting groups
Age, Categorical
<=18 years
2 Participants
n=99 Participants
0 Participants
n=107 Participants
2 Participants
n=206 Participants
Age, Categorical
Between 18 and 65 years
228 Participants
n=99 Participants
226 Participants
n=107 Participants
454 Participants
n=206 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Continuous
38.7 years
STANDARD_DEVIATION 7.49 • n=99 Participants
39.5 years
STANDARD_DEVIATION 7.63 • n=107 Participants
39.1 years
STANDARD_DEVIATION 7.54 • n=206 Participants
Sex: Female, Male
Female
230 Participants
n=99 Participants
226 Participants
n=107 Participants
456 Participants
n=206 Participants
Sex: Female, Male
Male
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Region of Enrollment
United States
230 participants
n=99 Participants
226 participants
n=107 Participants
456 participants
n=206 Participants

PRIMARY outcome

Timeframe: Any time between baseline and the end of study or time to intervention

Population: Modified Intent-to-Treat Population defined as subjects from the Safety Population who received at least 1 dose of study medication, had average baseline hemoglobin, TSAT, and ferritin levels, had heavy uterine bleeding, and had at least 1 post-baseline hemoglobin assessment.

Outcome measures

Outcome measures
Measure
Ferric Carboxymaltose (FCM)
n=228 Participants
Maximum of 1,000 mg of iron as IV FCM given at weekly intervals until the individual's calculated cumulative dose has been reached or a maximum of 2,500 mg has been administered
Oral Iron Tablets
n=225 Participants
325 mg tablets TID on Days 0 through Day 42
Number of Subjects Achieving 'Clinical Success'. Clinical Success is Defined as an Increase in Hemoglobin of ≥ 2.0 g/dL
187 participants
139 participants

Adverse Events

Ferric Carboxymaltose (FCM)

Serious events: 3 serious events
Other events: 120 other events
Deaths: 0 deaths

Oral Iron Tablets

Serious events: 3 serious events
Other events: 133 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Ferric Carboxymaltose (FCM)
n=230 participants at risk
Maximum of 1,000 mg of iron as IV FCM given at weekly intervals until the individual's calculated cumulative dose has been reached or a maximum of 2,500 mg has been administered
Oral Iron Tablets
n=226 participants at risk
325 mg tablets TID on Days 0 through Day 42
Reproductive system and breast disorders
Uterine hemorrhage
0.43%
1/230 • 11 months
0.44%
1/226 • 11 months
Nervous system disorders
Transient ischemic attack
0.00%
0/230 • 11 months
0.44%
1/226 • 11 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Uterine leiomyoma
0.00%
0/230 • 11 months
0.44%
1/226 • 11 months
General disorders
Chest pain
0.43%
1/230 • 11 months
0.00%
0/226 • 11 months
Infections and infestations
Pelvic inflammatory disease
0.43%
1/230 • 11 months
0.00%
0/226 • 11 months
Gastrointestinal disorders
Abdominal pain
0.00%
0/230 • 11 months
0.44%
1/226 • 11 months

Other adverse events

Other adverse events
Measure
Ferric Carboxymaltose (FCM)
n=230 participants at risk
Maximum of 1,000 mg of iron as IV FCM given at weekly intervals until the individual's calculated cumulative dose has been reached or a maximum of 2,500 mg has been administered
Oral Iron Tablets
n=226 participants at risk
325 mg tablets TID on Days 0 through Day 42
Gastrointestinal disorders
Constipation
3.5%
8/230 • 11 months
15.5%
35/226 • 11 months
Gastrointestinal disorders
Diarrhea
3.5%
8/230 • 11 months
5.8%
13/226 • 11 months
Gastrointestinal disorders
Abdominal pain
5.2%
12/230 • 11 months
2.7%
6/226 • 11 months
Gastrointestinal disorders
Nausea
5.2%
12/230 • 11 months
14.6%
33/226 • 11 months
General disorders
Fatigue
5.7%
13/230 • 11 months
2.2%
5/226 • 11 months
Infections and infestations
Nasopharyngitis
3.0%
7/230 • 11 months
6.2%
14/226 • 11 months
Renal and urinary disorders
Blood phosphorus decreased
11.3%
26/230 • 11 months
0.00%
0/226 • 11 months
Nervous system disorders
Headache
14.8%
34/230 • 11 months
11.9%
27/226 • 11 months

Additional Information

Mark A. Falone, MD

Luitpold Pharmaceuticals, Inc.

Phone: 610-650-4200

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60