Trial Outcomes & Findings for SPD503 (Guanfacine Hydrochloride) in ADHD Plus Oppositional Symptoms (NCT NCT00367835)

NCT ID: NCT00367835

Last Updated: 2021-06-14

Results Overview

The oppositional subscale of the CPRS-R:L contains 10 items designed to reflect criteria for oppositional defiance disorder (ODD). Each item is scored on a range from 0 (not true at all) to 3 (very much true) with total scores ranging from 0 to 30. Higher scores are reflective of more severe symptoms.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

217 participants

Primary outcome timeframe

Baseline and up to 8 weeks

Results posted on

2021-06-14

Participant Flow

217 subjects were randomized (138 to SPD503 and 79 to placebo). However, only 214 subjects received at least one dose of study medication (136 for SPD503 and 78 for placebo). Therefore, 214 subjects constitute the safety population.

Participant milestones

Participant milestones
Measure
SPD503
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
Overall Study
STARTED
138
79
Overall Study
COMPLETED
109
48
Overall Study
NOT COMPLETED
29
31

Reasons for withdrawal

Reasons for withdrawal
Measure
SPD503
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
Overall Study
Adverse Event
14
1
Overall Study
Protocol Violation
1
7
Overall Study
Withdrawal by Subject
7
6
Overall Study
Lost to Follow-up
1
4
Overall Study
Lack of Efficacy
3
12
Overall Study
Subject in juvenile detention center
1
0
Overall Study
refused blood collection
1
0
Overall Study
Did not respond to calls
1
0
Overall Study
History of lead poisoning
0
1

Baseline Characteristics

SPD503 (Guanfacine Hydrochloride) in ADHD Plus Oppositional Symptoms

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
SPD503
n=138 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=79 Participants
Total
n=217 Participants
Total of all reporting groups
Age, Categorical
<=18 years
138 Participants
n=99 Participants
79 Participants
n=107 Participants
217 Participants
n=206 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Continuous
9.4 years
STANDARD_DEVIATION 1.73 • n=99 Participants
9.3 years
STANDARD_DEVIATION 2.04 • n=107 Participants
9.4 years
STANDARD_DEVIATION 1.84 • n=206 Participants
Sex: Female, Male
Female
50 Participants
n=99 Participants
19 Participants
n=107 Participants
69 Participants
n=206 Participants
Sex: Female, Male
Male
88 Participants
n=99 Participants
60 Participants
n=107 Participants
148 Participants
n=206 Participants
Region of Enrollment
United States
138 Participants
n=99 Participants
79 Participants
n=107 Participants
217 Participants
n=206 Participants

PRIMARY outcome

Timeframe: Baseline and up to 8 weeks

Population: Full Analysis Set (FAS) defined as all randomized subjects who received at least one dose of any investigational product during this study and with a baseline and at least one post-baseline efficacy measurement.

The oppositional subscale of the CPRS-R:L contains 10 items designed to reflect criteria for oppositional defiance disorder (ODD). Each item is scored on a range from 0 (not true at all) to 3 (very much true) with total scores ranging from 0 to 30. Higher scores are reflective of more severe symptoms.

Outcome measures

Outcome measures
Measure
SPD503
n=130 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=75 Participants
Change From Baseline in the Oppositional Subscale of the Conners' Parent Rating Scale-Revised Long Form (CPRS-R:L) Score at Up to 8 Weeks
-10.8 Units on a scale
Standard Deviation 7.23
-7.0 Units on a scale
Standard Deviation 7.63

SECONDARY outcome

Timeframe: Baseline and up to 8 weeks

Population: FAS

The ADHD-RS-IV consists of 18 items scored on a 4-point scale ranging from 0 (no symptoms) to 3 (severe symptoms) with total score ranging from 0 to 54.

Outcome measures

Outcome measures
Measure
SPD503
n=130 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=75 Participants
Change From Baseline in Attention Deficit Hyperactivity Disorder Rating Scale (ADHD-RS-IV) Total Score at Up to 8 Weeks
-23.8 Units on a scale
Standard Deviation 14.43
-11.4 Units on a scale
Standard Deviation 12.65

SECONDARY outcome

Timeframe: up to 8 weeks

Population: FAS

CGI-S assesses the severity of the subject's condition on a 7-point scale ranging from 1 (normal, not at all ill) to 7 (among the most extremely ill)

Outcome measures

Outcome measures
Measure
SPD503
n=130 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=75 Participants
Assessment of Clinical Global Impression-Severity of Illness (CGI-S)
6 (Severely ill)
4 Participants
5 Participants
Assessment of Clinical Global Impression-Severity of Illness (CGI-S)
7 (Among the most extremely ill)
0 Participants
0 Participants
Assessment of Clinical Global Impression-Severity of Illness (CGI-S)
1 (Normal, not at all ill)
25 Participants
3 Participants
Assessment of Clinical Global Impression-Severity of Illness (CGI-S)
2 (Borderline mentally ill)
33 Participants
6 Participants
Assessment of Clinical Global Impression-Severity of Illness (CGI-S)
3 (Mildly ill)
29 Participants
15 Participants
Assessment of Clinical Global Impression-Severity of Illness (CGI-S)
4 (Moderately ill)
26 Participants
24 Participants
Assessment of Clinical Global Impression-Severity of Illness (CGI-S)
5 (Markedly ill)
13 Participants
22 Participants

SECONDARY outcome

Timeframe: up to 8 weeks

Population: FAS

CGI-I consists of a 7-point scale ranging from 1 (very much improved) to 7 (very much worse). Improvement is defined as a score of 1 (very much improved) or 2 (much improved) on the scale.

Outcome measures

Outcome measures
Measure
SPD503
n=130 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=75 Participants
Number of Participants With Improvement on Clinical Global Impression-Improvement (CGI-I)
93 Participants
24 Participants

SECONDARY outcome

Timeframe: Baseline and up to 8 weeks

Population: FAS

Each item on the NYPRS-S is scored from a range of 0 (not at all) to 3 (very much) with total scores ranging from 0 to 120. Higher scores are reflective of increased disease severity.

Outcome measures

Outcome measures
Measure
SPD503
n=130 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=75 Participants
Change From Baseline in the 40-Item Conduct Problem Scale of the New York Parent's Rating Scale-School-aged (NYPRS-S) Score at Up to 8 Weeks
-15.6 units on a scale
Standard Deviation 12.86
-10.3 units on a scale
Standard Deviation 13.25

SECONDARY outcome

Timeframe: Baseline and up to 8 weeks

Population: FAS

The response to each of the 36 items on the PSI/SF is converted to a five-point scale from 1 (strongly agree) to 5 (strongly disagree) with total scores ranging from 36 to 180. A higher score is reflective of less stress for the parents.

Outcome measures

Outcome measures
Measure
SPD503
n=109 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=57 Participants
Change From Baseline in the Parent Stress Index-Short Form (PSI/SF) Score at Up to 8 Weeks
17.3 Units on a scale
Standard Deviation 19.76
7.2 Units on a scale
Standard Deviation 18.29

SECONDARY outcome

Timeframe: up to 8 weeks

Population: FAS

The Medication Satisfaction Survey (MSS) consists of 11 questions each being answered with one of six responses (strongly agree, agree, somewhat agree, somewhat disagree, disagree, strongly disagree). Overall satisfaction with their child taking the study medication, Question #11, with a response of "strongly agree" or "agree".

Outcome measures

Outcome measures
Measure
SPD503
n=129 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=69 Participants
Number of Participants With Overall Satisfaction on the Medication Satisfaction Survey (MSS)
84 Participants
21 Participants

SECONDARY outcome

Timeframe: Baseline and up to 8 weeks

Population: Safety population defined as all randomized subjects who received at least one dose of any investigational product during this study.

QTcF is the QT interval using Fridericia's correction formula. QT interval is a measure of time between the start of the Q wave and the end of the T wave and is dependent on the heart rate (e.g., the faster the heart rate, the shorter the QT interval). The QT interval has to be corrected in order to aid interpretation.

Outcome measures

Outcome measures
Measure
SPD503
n=107 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=58 Participants
Change From Baseline in Electrocardiogram Results (QTcF Interval) at Up to 8 Weeks
5.2 msec
Standard Deviation 15.74
2.1 msec
Standard Deviation 17.41

SECONDARY outcome

Timeframe: Baseline and up to 8 weeks

Population: Safety population

Outcome measures

Outcome measures
Measure
SPD503
n=130 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=75 Participants
Change From Baseline in Pulse Rate at Up to 8 Weeks
-4.3 beats/min
Standard Deviation 11.89
0.7 beats/min
Standard Deviation 11.44

SECONDARY outcome

Timeframe: Baseline and up to 8 weeks

Population: Safety population

Outcome measures

Outcome measures
Measure
SPD503
n=130 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=75 Participants
Change From Baseline in Systolic Blood Pressure at Up to 8 Weeks
-2.6 mmHg
Standard Deviation 10.27
0.7 mmHg
Standard Deviation 8.18

SECONDARY outcome

Timeframe: Baseline and up to 8 weeks

Population: Safety population

Outcome measures

Outcome measures
Measure
SPD503
n=130 Participants
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=75 Participants
Change From Baseline in Diastolic Blood Pressure at Up to 8 Weeks
-1.3 mmHg
Standard Deviation 8.48
0.9 mmHg
Standard Deviation 7.38

Adverse Events

SPD503

Serious events: 0 serious events
Other events: 115 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 47 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
SPD503
n=136 participants at risk
Subjects will receive either 1, 2, 3, or 4 mg/day oral doses of SPD503 (Guanfacine hydrochloride)
Placebo
n=78 participants at risk
Nervous system disorders
Somnolence
50.7%
69/136
6.4%
5/78
Nervous system disorders
Headache
22.1%
30/136
17.9%
14/78
Nervous system disorders
Sedation
13.2%
18/136
1.3%
1/78
Nervous system disorders
Dizziness
5.1%
7/136
3.8%
3/78
Gastrointestinal disorders
Abdominal pain upper
11.8%
16/136
2.6%
2/78
Gastrointestinal disorders
Vomiting
7.4%
10/136
6.4%
5/78
Gastrointestinal disorders
Nausea
2.9%
4/136
6.4%
5/78
General disorders
Fatigue
11.0%
15/136
5.1%
4/78
Psychiatric disorders
Irritability
8.1%
11/136
2.6%
2/78
Psychiatric disorders
Affect lability
1.5%
2/136
5.1%
4/78
Investigations
Blood pressure diastolic decreased
5.9%
8/136
1.3%
1/78
Infections and infestations
Upper respiratory tract infection
4.4%
6/136
5.1%
4/78
Respiratory, thoracic and mediastinal disorders
Pharyngolaryngeal pain
3.7%
5/136
5.1%
4/78

Additional Information

Study Director

Shire

Phone: +1 866 842 5335

Results disclosure agreements

  • Principal investigator is a sponsor employee If a multicenter publication is not submitted within twelve (12) months after conclusion, abandonment or termination of the Study at all sites, or after Sponsor confirms there shall be no multicenter Study publication, the Institution and/or such Principal Investigator may publish the results from the Institution site individually
  • Publication restrictions are in place

Restriction type: OTHER