Trial Outcomes & Findings for Divalproex Sodium vs. Placebo in Childhood/Adolescent Autism (NCT NCT00211757)

NCT ID: NCT00211757

Last Updated: 2024-10-28

Results Overview

The CGI-I is a 7-point improvement scale. Ratings of 1 or 2 (responders) indicate a substantial reduction in symptoms. A rating of 3 (minimally improved) on the CGI is defined as a slight symptomatic improvement that is not deemed clinically significant; patients with such an improvement were not considered responders. Two versions of this test were used, one focused on irritability (primary outcome measure) and a general version CGI-I-autism focused on all symptoms including core symptom domains. The CGI-I irritability took into consideration the scores from the ABC-Irritability subscale, the OAS-M aggression and irritability subscales and information from open-ended questioning related to the degree of interference, nature, and range of behavioral problems at school and at home

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

27 participants

Primary outcome timeframe

Baseline to end of study (week 15)

Results posted on

2024-10-28

Participant Flow

Participant milestones

Participant milestones
Measure
Placebo
Subjects in this arm will receive a placebo comparative to the study drug divalproex sodium. Placebo: Placebo comparator.
Divalproex Sodium
Subjects will receive the study drug, divalproex sodium. Divalproex sodium: Study drug.
Overall Study
STARTED
11
16
Overall Study
COMPLETED
10
14
Overall Study
NOT COMPLETED
1
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Placebo
Subjects in this arm will receive a placebo comparative to the study drug divalproex sodium. Placebo: Placebo comparator.
Divalproex Sodium
Subjects will receive the study drug, divalproex sodium. Divalproex sodium: Study drug.
Overall Study
Withdrawal by Subject
1
1
Overall Study
Lack of Efficacy
0
1

Baseline Characteristics

Divalproex Sodium vs. Placebo in Childhood/Adolescent Autism

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo
n=11 Participants
Subjects in this arm will receive a placebo comparative to the study drug divalproex sodium. Placebo: Placebo comparator.
Divalporex Sodium
n=16 Participants
Subjects will receive the study drug, divalproex sodium. Divalproex sodium: Study drug.
Total
n=27 Participants
Total of all reporting groups
Age, Categorical
<=18 years
11 Participants
n=99 Participants
16 Participants
n=107 Participants
27 Participants
n=206 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Sex: Female, Male
Female
1 Participants
n=99 Participants
3 Participants
n=107 Participants
4 Participants
n=206 Participants
Sex: Female, Male
Male
10 Participants
n=99 Participants
13 Participants
n=107 Participants
23 Participants
n=206 Participants
Diagnosis
Autistic Disorder
9 Participants
n=99 Participants
14 Participants
n=107 Participants
23 Participants
n=206 Participants
Diagnosis
Asperger's Syndrome
2 Participants
n=99 Participants
2 Participants
n=107 Participants
4 Participants
n=206 Participants

PRIMARY outcome

Timeframe: Baseline to end of study (week 15)

The CGI-I is a 7-point improvement scale. Ratings of 1 or 2 (responders) indicate a substantial reduction in symptoms. A rating of 3 (minimally improved) on the CGI is defined as a slight symptomatic improvement that is not deemed clinically significant; patients with such an improvement were not considered responders. Two versions of this test were used, one focused on irritability (primary outcome measure) and a general version CGI-I-autism focused on all symptoms including core symptom domains. The CGI-I irritability took into consideration the scores from the ABC-Irritability subscale, the OAS-M aggression and irritability subscales and information from open-ended questioning related to the degree of interference, nature, and range of behavioral problems at school and at home

Outcome measures

Outcome measures
Measure
Placebo
n=11 Participants
Subjects in this arm will receive a placebo comparative to the study drug divalproex sodium. Placebo: Placebo comparator.
Divalproex Sodium
n=16 Participants
Subjects will receive the study drug, divalproex sodium. Divalproex sodium: Study drug.
Number of Participants Reporting Improvement on the Clinical Global Impression
1 Participants
10 Participants

PRIMARY outcome

Timeframe: Baseline and End of Study (week 15)

The Aberrant Behavior Checklist is designed to objectively identify five behavior sub scales through observation by the primary caregiver: irritability, lethargy, stereotypy, hyperactivity, and inappropriate speech. The ABC was filled out by parents on a scale from 0-3 for each category. (0 being not a problem, 3 being severe problem). Scores from all sub scales were added (scoring 0-45 for Irritability subscale, 0-48 for Lethargy subscale, 0-21 for stereotypy scale, 0-48 for hyperactivity sub-scale, and 0-12 for inappropriate speech sub-scale) to obtain an overall score with a an overall scoring range of 0-174. Higher scores were indicative of worsening symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=11 Participants
Subjects in this arm will receive a placebo comparative to the study drug divalproex sodium. Placebo: Placebo comparator.
Divalproex Sodium
n=16 Participants
Subjects will receive the study drug, divalproex sodium. Divalproex sodium: Study drug.
Change in Aberrant Behaviors as Measured by the Aberrant Behavior Checklist Scores
baseline
22 score on a scale
Standard Deviation 7.81
20.3 score on a scale
Standard Deviation 7.36
Change in Aberrant Behaviors as Measured by the Aberrant Behavior Checklist Scores
Week 15
14.5 score on a scale
Standard Deviation 6.67
17.7 score on a scale
Standard Deviation 7.94

Adverse Events

Placebo

Serious events: 0 serious events
Other events: 8 other events
Deaths: 0 deaths

Divalproex Sodium

Serious events: 0 serious events
Other events: 7 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Placebo
n=11 participants at risk
Subjects in this arm will receive a placebo comparative to the study drug divalproex sodium. Placebo: Placebo comparator.
Divalproex Sodium
n=16 participants at risk
Subjects will receive the study drug, divalproex sodium. Divalproex sodium: Study drug.
General disorders
Insomnia
18.2%
2/11 • 6 weeks on treatment
12.5%
2/16 • 6 weeks on treatment
Skin and subcutaneous tissue disorders
Rash
0.00%
0/11 • 6 weeks on treatment
12.5%
2/16 • 6 weeks on treatment
Metabolism and nutrition disorders
Weight gian
9.1%
1/11 • 6 weeks on treatment
6.2%
1/16 • 6 weeks on treatment
General disorders
headache
0.00%
0/11 • 6 weeks on treatment
6.2%
1/16 • 6 weeks on treatment
General disorders
polyuria
0.00%
0/11 • 6 weeks on treatment
12.5%
2/16 • 6 weeks on treatment
General disorders
agitation
9.1%
1/11 • 6 weeks on treatment
12.5%
2/16 • 6 weeks on treatment
Immune system disorders
Infection
27.3%
3/11 • 6 weeks on treatment
12.5%
2/16 • 6 weeks on treatment
General disorders
Hypersomnolence
27.3%
3/11 • 6 weeks on treatment
0.00%
0/16 • 6 weeks on treatment

Additional Information

Dr. Eric Hollander

Montefiore Medical Center

Phone: 718-920-4287

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place